- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Mitochondrial Diseases in United Kingdom
Total 146859 results
-
Great Ormond Street Hospital for Children NHS Foundation...National Institute for Health Research, United Kingdom; The Freya FoundationRecruitingPyruvate Dehydrogenase Complex Deficiency | Pyruvate Dehydrogenase E1 Alpha Deficiency | Pyruvate Dehydrogenase E1-Beta Deficiency | Pyruvate Dehydrogenase E2 Deficiency | Pyruvate Dehydrogenase Phosphatase DeficiencyUnited Kingdom
-
Santhera PharmaceuticalsCompletedFriedreich's AtaxiaNetherlands, Austria, Germany, United Kingdom
-
Santhera PharmaceuticalsCompletedLeber's Hereditary Optic NeuropathyCanada, Germany, United Kingdom
-
Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University...RecruitingEnd Stage Liver Disease | Mitochondrial Diseases | Acute Liver Failure | Respiratory Chain Deficiencies, Mitochondrial | Disorder of Fatty Acid OxidationUnited States, Canada
-
Woodinville Psychiatric AssociatesCompletedDiabetes Mellitus, Type 2 | Mitochondrial Diseases | Movement Disorders | FibromyalgiaUnited States
-
The Champ FoundationChildren's Hospital of Philadelphia; The Cleveland ClinicRecruitingPearson Syndrome | Single Large Scale Mitochondrial DNA Deletion Syndromes (SLSMDS)United States
-
RWTH Aachen UniversityAssistance Publique - Hôpitaux de ParisWithdrawnFriedreich AtaxiaSpain, Italy, Austria, Germany, United Kingdom, France
-
University of WashingtonAmerican Heart AssociationCompletedHeart Failure,Congestive | Mitochondrial Alteration | Heart Failure New York Heart Association Class IVUnited States
-
University of Colorado, DenverCompletedMitochondrial Diseases | Human Immunodeficiency Virus (HIV)United States
-
Santhera PharmaceuticalsCompletedLeber's Hereditary Optic NeuropathyCanada, Germany, United Kingdom
-
Santhera PharmaceuticalsCompletedFriedreich's AtaxiaNetherlands, Austria, United Kingdom, Belgium, France, Germany
-
Kemin Foods LCDSM Nutritional Products, Inc.Terminated
-
GenSight BiologicsCompletedLeber Hereditary Optic NeuropathyUnited States, France, Italy, United Kingdom, Germany
-
Mead Johnson NutritionWithdrawnCow's Milk Allergy | Intolerance to Extensively Hydrolyzed Formulas | Intolerance to Breast MilkUnited Kingdom
-
Oregon State UniversityTerminatedSedentary Lifestyle | Insulin Resistance | Overweight and Obesity | Metabolic Disease | Mitochondrial MetabolismUnited States
-
Reata, a wholly owned subsidiary of BiogenAbbVie; Friedreich's Ataxia Research AllianceActive, not recruitingFriedreich AtaxiaUnited States, Australia, Austria, Italy, United Kingdom
-
University of Maryland, BaltimoreNational Institute of Nursing Research (NINR)CompletedPain | Physical Activity | Osteoarthritis, Knee | Mitochondrial PathologyUnited States
-
Oregon Health and Science UniversityUniversity of PittsburghCompletedVery Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency | Carnitine Palmitoyltransferase 2 (CPT2) Deficiency | Mitochondrial Trifunctional Protein (TFP) Deficiency | Long-chain 3 hydroxyacylCoA Dehydrogenase (LCHAD) DeficiencyUnited States
-
Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingMELAS or m.3243 A>G Mitochondrial DNA Mutation CarrierUnited States
-
The University of Texas Health Science Center at...National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedInsulin Sensitivity | Multiple Mitochondrial Dysfunctions SyndromeUnited States
-
Oregon Health and Science UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Oregon...TerminatedPeripheral Neuropathy | Mitochondrial Trifunctional Protein DeficiencyUnited States
-
Oregon State UniversityCompletedSedentary Lifestyle | Insulin Resistance | Overweight and Obesity | Metabolic Disease | Mitochondrial MetabolismUnited States
-
Richard FryeAutism Discovery and Treatment FoundationRecruitingEpilepsy | Neurodevelopmental Disorders | Autism Spectrum Disorder | Down Syndrome | Mitochondrial Encephalomyopathies | Pediatric Acute-Onset Neuropsychiatric Syndrome | Cerebral Folate Deficiency | Pediatric Autoimmune Neuropsychiatric Disorder Associated With Streptococcal InfectionUnited States
-
GenSight BiologicsCompletedLeber Hereditary Optic NeuropathyUnited States, France, Italy, Spain, United Kingdom
-
Massachusetts General HospitalNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)UnknownInsulin Resistance | Pediatric Obesity | Mitochondrial DysfunctionUnited States
-
European Friedreich's Ataxia Consortium for Translational...RecruitingFriedreich's AtaxiaAustria, Germany, Italy, Spain, Belgium, Czechia, France, Greece, Ireland, United Kingdom
-
The University of Texas Health Science Center at...National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingType 2 Diabetes | Non-Alcoholic Fatty Liver Disease | Mitochondrial Metabolism DisordersUnited States
-
GenSight BiologicsActive, not recruitingLeber Hereditary Optic NeuropathyBelgium, Spain, United States, France, United Kingdom, Taiwan, Italy
-
Oklahoma Medical Research FoundationUniversity of Wisconsin, Madison; University of Oklahoma; National Institute...RecruitingInsulin Resistance | Chronic Disease | Aging | Insulin Sensitivity | MitochondriaUnited States
-
University of WashingtonNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Emory... and other collaboratorsCompletedCardiovascular Disease | Sarcopenia | Endothelial Dysfunction | Kidney Disease | Muscle Mitochondrial FunctionUnited States
-
Santhera PharmaceuticalsCompletedLeber's Hereditary Optic Neuropathy (LHON)Belgium, Netherlands, France, Germany, Norway, United Kingdom, Italy
-
East Carolina UniversityGlaxoSmithKlineUnknownMitral Valve Regurgitation | Left Atrium Dilatation and Hypertrophy | Mitochondrial Dysfunction in the Heart | Cardiomyocyte Apoptosis | Cardiac InflammationUnited States
-
Friedreich's Ataxia Research AllianceRecruitingFriedreich AtaxiaUnited States, Canada, New Zealand, Australia, France, Austria, Belgium, Brazil, Czechia, Germany, Greece, Ireland, Italy, Spain, United Kingdom, India, Netherlands
-
Edison Pharmaceuticals IncTerminated
-
Santhera PharmaceuticalsCompletedLeber's Hereditary Optic Neuropathy (LHON)United States, United Kingdom, Spain, Poland, Austria, Belgium, Bulgaria, Germany, Italy, Portugal
-
Massachusetts Eye and Ear InfirmaryNational Eye Institute (NEI)Active, not recruitingStroke | Myasthenia Gravis | Traumatic Brain Injury | Chronic Progressive External Ophthalmoplegia | Ptosis, Eyelid | BlepharoptosisUnited States
-
UK Kidney AssociationRecruitingVasculitis | AL Amyloidosis | Tuberous Sclerosis | Fabry Disease | Cystinuria | Focal Segmental Glomerulosclerosis | IgA Nephropathy | Bartter Syndrome | Pure Red Cell Aplasia | Membranous Nephropathy | Atypical Hemolytic Uremic Syndrome | Autosomal Dominant Polycystic Kidney Disease | Cystinosis | Nephronophthisis | BK Nephropathy and other conditionsUnited Kingdom
-
Hugo W. Moser Research Institute at Kennedy Krieger...RecruitingLeukoencephalopathies | Genetic Disease | White Matter Disease | Ataxia, Cerebellar | LBSL | Leukoencephalopathy With Brainstem and Spinal Cord Involvement and Lactate ElevationUnited States
-
Taysha Gene Therapies, Inc.Withdrawn
-
Children's Hospital of PhiladelphiaNational Heart, Lung, and Blood Institute (NHLBI)Recruiting
-
Children's Hospital of PhiladelphiaFriedreich's Ataxia Research AllianceCompleted
-
Children's Hospital of PhiladelphiaFriedreich's Ataxia Research AllianceCompleted
-
Larimar Therapeutics, Inc.Children's Hospital of PhiladelphiaCompletedFriedreich AtaxiaUnited States
-
BiogenNot yet recruiting
-
University of FloridaNational Institutes of Health (NIH); National Center for Advancing Translational... and other collaboratorsRecruiting
-
University of MinnesotaCompleted
-
Children's Hospital of PhiladelphiaFriedreich's Ataxia Research Alliance; Vidara Therapeutics Research LtdCompleted
-
Ralitza GavrilovaCardero Therapeutics, Inc.Completed
-
National Human Genome Research Institute (NHGRI)CompletedFriedreich AtaxiaUnited States
-
National Institute of Neurological Disorders and...CompletedFriedreich AtaxiaUnited States