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Clinical Trials on Mitochondrial Diseases in United Kingdom
Total 146895 results
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Larimar Therapeutics, Inc.CompletedFriedreich AtaxiaUnited States
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The Cleveland ClinicBristol-Myers Squibb; National Institute of Allergy and Infectious Diseases... and other collaboratorsTerminatedHIV Infection | Mitochondrial DysfunctionUnited States
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Design Therapeutics, Inc.CompletedFriedreich AtaxiaUnited States
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Larimar Therapeutics, Inc.Veristat, Inc.; Metrum Research Group, LLCCompletedFriedreich AtaxiaUnited States
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Massachusetts General HospitalCompletedFabry Disease | Mitochondrial Disease | Small Fiber Neuropathy | Ehlers Danlos SyndromeUnited States
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University of South FloridaPfizer; Friedreich's Ataxia Research AllianceTerminatedFriedreich's AtaxiaUnited States
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Imperial College LondonEnrolling by invitationCardiovascular Diseases | Diabetes | Respiratory Disease | Non-Alcoholic Fatty Liver DiseaseUnited Kingdom
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PTC TherapeuticsActive, not recruitingFriedreich AtaxiaUnited States
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Children's Hospital of PhiladelphiaFriedreich's Ataxia Research Alliance; Stealth BioTherapeutics Inc.Active, not recruitingFriedreich AtaxiaUnited States
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Metro International Biotech, LLCChildren's Hospital of PhiladelphiaCompleted
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National Institute of Neurological Disorders and...Completed
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University of South FloridaFriedreich's Ataxia Research Alliance; Edison Pharmaceuticals IncCompleted
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University of South FloridaUnknownFriedreich's AtaxiaUnited States
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Penwest Pharmaceuticals Co.CompletedFriedreich's AtaxiaUnited States
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National Institute of Neurological Disorders and...Completed
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaUnited States
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Retrotope, Inc.CompletedFriedreich's AtaxiaUnited States
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Jerry Vockley, MD, PhDUltragenyx Pharmaceutical IncNo longer availableBarth Syndrome | Mitochondrial Trifunctional Protein Deficiency | Very Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency | Carnitine Palmitoyltransferase Deficiencies (CPT1, CPT2) | Long-chain Hydroxyacyl-CoA Dehydrogenase Deficiency | Glycogen Storage Disorders | Pyruvate Carboxylase Deficiency... and other conditionsUnited States
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Design TherapeuticsCompleted
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Larimar Therapeutics, Inc.Clinilabs, Inc.CompletedHealthy Volunteers | Friedreich AtaxiaUnited States
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Larimar Therapeutics, Inc.Veristat, Inc.; Metrum Research Group, LLCCompletedFriedreich AtaxiaUnited States
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Weill Medical College of Cornell UniversityRecruitingFriedreich's AtaxiaUnited States
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University of PittsburghFriedreich's Ataxia Research AllianceCompleted
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Byron LamNational Eye Institute (NEI)Active, not recruitingLeber's Hereditary Optic NeuropathyUnited States
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PTC TherapeuticsAxio Research. LLCCompleted
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Children's Hospital of PhiladelphiaUniversity of California, Los Angeles; University of FloridaCompleted
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PTC TherapeuticsCompletedFriedreich's AtaxiaUnited States
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University of MinnesotaFriedreich's Ataxia Research Alliance; Bob Allison Ataxia Research CenterCompletedFriedreich AtaxiaUnited States
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Stealth BioTherapeutics Inc.CompletedLeber's Hereditary Optic NeuropathyUnited States
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaUnited States
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Horizon Pharma Ireland, Ltd., Dublin IrelandFriedreich's Ataxia Research AllianceCompletedFriedreich's AtaxiaUnited States
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Horizon Pharma Ireland, Ltd., Dublin IrelandFriedreich's Ataxia Research AllianceCompletedFriedreich's AtaxiaUnited States
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Edison Pharmaceuticals IncNo longer availableLeber's Hereditary Optic NeuropathyUnited States
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National Eye Institute (NEI)CompletedMacular Degeneration | Diabetic Retinopathy | Mitochondria | Hippel-Landau DiseaseUnited States
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The University of Texas Medical Branch, GalvestonWithdrawnGlaucoma | Eye Diseases | Diabetic Retinopathy | Age Related Macular Degeneration | Mitochondrial DNA | Ophthalmic TraumaUnited States
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Horizon Pharma Ireland, Ltd., Dublin IrelandFriedreich's Ataxia Research AllianceCompletedFriedreich's AtaxiaUnited States
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University of California, IrvineWithdrawnDilated Cardiomyopathy | Hypertrophic Cardiomyopathy | Restrictive Cardiomyopathy | Mitochondrial Cardiomyopathy | Noncompaction CardiomyopathyUnited States
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Neurocrine BiosciencesTakedaCompletedFriedreich AtaxiaUnited States
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PTC TherapeuticsCompletedLeigh SyndromeUnited States
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Mannkind CorporationCompleted
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Retrotope, Inc.CompletedFriedreich's AtaxiaUnited States
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Medical College of WisconsinTerminatedLeber's Hereditary Optic Neuropathy (LHON)United States
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Monash UniversityChildren's Hospital of Philadelphia; McGill University; University of Florida; University... and other collaboratorsActive, not recruitingFriedreich AtaxiaUnited States, Canada, Australia, Brazil, Germany
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ShireCompletedFriedreich's AtaxiaUnited States
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Prexton TherapeuticsCompleted
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Neurophth Therapeutics IncRecruitingLeber Hereditary Optic Neuropathy (LHON)China, United States
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Moorfields Eye Hospital NHS Foundation TrustCompletedRetinal Diseases | Vitreous Diseases | Choroidal DiseasesUnited Kingdom
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University of OxfordMerck Sharp & Dohme LLCCompletedCardiovascular Disease | Diabetes Mellitus | Peripheral Arterial Disease | Coronary Heart DiseaseUnited Kingdom
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University of HullRecruitingCoronary Artery Disease | Aortic Valve Disease | Endocarditis | Cardiac Disease | Valve Heart DiseaseUnited Kingdom
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AstraZenecaParexelRecruitingHealthy Subjects | Crohns DiseaseUnited Kingdom