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Clinical Trials on Molybdenum Cofactor Deficiency, Type A
Total 988 results
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Centre Hospitalier Universitaire DijonTerminatedPatient With Type 2 Diabetes Treated With Insulin Using a Baseline/Bolus StrategyFrance
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Ain Shams UniversityNot yet recruitingVitamin D Deficiency | Leiomyoma
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St. Jude Children's Research HospitalNational Institute of Allergy and Infectious Diseases (NIAID); The University...Completed
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Peking University People's HospitalWithdrawnRelapse | Prevention | Interferon-A-2B | Hematopietic Stem Cell TransplantationChina
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QIAGEN Gaithersburg, IncCompletedRespiratory Syncytial Virus Infections | Influenza A | Rhinovirus | Influenza B | QIAGEN ResPlex II Advanced Panel | Infection Due to Human Parainfluenza Virus 1 | Parainfluenza Type 2 | Parainfluenza Type 3 | Parainfluenza Type 4 | Human Metapneumovirus A/B | Coxsackie Virus/Echovirus | Adenovirus Types B/C/E | Coronavirus Subtypes 229E and other conditionsUnited States
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Nanfang Hospital of Southern Medical UniversityPeking University People's Hospital; Guangzhou First People's Hospital; Sun Yat-Sen... and other collaboratorsRecruitingCore Binding Factor Acute Myeloid LeukemiaChina
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Alnylam PharmaceuticalsTerminatedZZ Type Alpha-1 Antitrypsin Deficiency Liver DiseaseUnited Kingdom
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National Human Genome Research Institute (NHGRI)RecruitingMetabolic Disease | Purine-Pyrimidine Metabolism | AICDA, OMIM *605257, Immunodeficiency With Hyper-IgM, Type 2; HIGM2 | UNG, OMIM *191525, Hyper-IgM Syndrome 5 | NT5C3A<TAB>, OMIM *606224, Anemia, Hemolytic, Due to UMPH1 Deficiency | UMPS, OMIM *613891, Orotic Aciduria | DHODH, OMIM *126064,... and other conditionsUnited States
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Klinikum St. Georg gGmbHCompletedImpaired Wound Healing | Factor XIII DeficiencyGermany
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West China HospitalUnknownHypothermia | Circulatory Arrest | Type A Aortic DissectionChina
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Pamukkale UniversityBakirkoy Dr. Sadi Konuk Research and Training HospitalCompletedType2 Diabetes | Self Efficacy | Self Management | Cholesterol; Lipidosis | High Density Lipoprotein Deficiency | Motivational Interview | Tele-nursing | LDL - Low Density Lipoprotein Receptor DisorderTurkey
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Owen Drive Surgical Clinic of FayettevilleMedtronic - MITGUnknownEvaluate the Use of a New Mesh Type in Open Inguinal Hernia RepairUnited States
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Rocket Pharmaceuticals Inc.California Institute for Regenerative Medicine (CIRM)CompletedLeukocyte Adhesion Defect - Type ISpain, United States, United Kingdom
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Rocket Pharmaceuticals Inc.WithdrawnLeukocyte Adhesion Defect - Type ISpain
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Columbia UniversityUniversitat Autonoma de Barcelona; Instituto de Salud Carlos III; University... and other collaboratorsActive, not recruitingThymidine Kinase 2 Deficiency | Mitochondrial DNA Depletion Syndrome 2 Myopathic TypeUnited States
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Washington University School of MedicineRecruitingHypertension | Diabetes Mellitus, Type 2 | Vitamin D DeficiencyUnited States
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Amsterdam Molecular TherapeuticsThe Clinical Trial CompanyCompletedFamilial Lipoprotein Lipase DeficiencyCanada
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Niguarda HospitalRecruitingCore Binding Factor Acute Myeloid Leukemia (CBF-AML)Italy
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Casa Sollievo della Sofferenza IRCCSUniversity of BariCompletedRisk Factor, Cardiovascular | Venous Thromboembolism | Blood TypeItaly
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Pompe DiseaseUnited States
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Ultragenyx Pharmaceutical IncTerminatedGlucose Transporter Type 1 Deficiency Syndrome (Glut1 DS)United States, Spain, France, Germany, Italy, United Kingdom
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Amsterdam Molecular TherapeuticsInternational Antiviral Therapy Evaluation CenterUnknownFamilial Lipoprotein Lipase DeficiencyCanada
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Federal State Budgetary Institution, V. A. Almazov...Tameside Hospital NHS Foundation TrustCompletedDiabetic Neuropathies | Vitamin D Deficiency | Diabetes Type 2Russian Federation
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University of Massachusetts, WorcesterCompletedVitamin D Deficiency | Type 2 Diabetes | Nonalcoholic Fatty Liver DiseaseUnited States
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University of PittsburghRecruitingLysosomal Storage Diseases | Leukodystrophy | Niemann-Pick Diseases | Batten Disease | Gaucher Disease | Krabbe Disease | Alpha-Mannosidosis | Osteopetrosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | GM1 Gangliosidoses | MPS I | MPS II | Vanishing White Matter Disease | Multiple Sulfatase Deficiency... and other conditionsUnited States
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Andrea BranchUnknownHepatocellular Carcinoma | Vitamin D DeficiencyUnited States
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1 | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States, United Kingdom, Spain, Italy, Brazil, Canada, Poland
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Clinical Nutrition Research Centre, SingaporeCompletedDiabetes Mellitus, Type 2 | Cardiovascular Risk FactorSingapore
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1 | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States, Israel, Mexico, Russian Federation, Argentina, Italy
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Federal Research Institute of Pediatric Hematology...CompletedLeukemia, Myeloid, Acute | Opportunistic Infections | Graft vs Host Disease | Precursor T-Cell Lymphoblastic Leukemia-Lymphoma | Bone Marrow Failure Syndromes | Immune Deficiency DiseaseRussian Federation
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Johns Hopkins UniversityTerminatedAtaxia-Telangiectasia (A-T)United States
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First Affiliated Hospital Xi'an Jiaotong UniversityCompleted
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SanofiCompletedSphingomyelin LipidosisItaly, Czechia, Belgium, France, Portugal, Turkey, United States, Argentina, Brazil, Chile, Germany, Romania, Spain
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Instituto Mexicano del Seguro SocialCompletedVitamin D Deficiency | Leiomyoma | Fibroid UterusMexico
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Second Affiliated Hospital of Wenzhou Medical UniversityUnknownVitamin D Deficiency | Gynaecological DiseaseChina
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Joslin Diabetes CenterCompletedType1diabetes | Cardiovascular Risk FactorUnited States
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National Taiwan University HospitalTaipei Veterans General Hospital, TaiwanNot yet recruitingHepatocellular Carcinoma | Vitamin D Deficiency | Perioperative Complication
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Second Affiliated Hospital of Wenzhou Medical UniversityUnknownVitamin D Deficiency | Uterine Fibroids | Gynaecological DiseaseChina
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SanofiApproved for marketing
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisBrazil, France, Italy, United States, Germany, United Kingdom
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Changi General HospitalNot yet recruitingCardiovascular Diseases | Hypercholesterolemia | Lipoprotein Types--Lp System Lp(A) HyperlipoproteinemiaSingapore
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University of New MexicoCompletedRetinitis Pigmentosa | Age Related Macular Degeneration | Congenital Stationary Night Blindness | ColorblindnessUnited States
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Genzyme, a Sanofi CompanyApproved for marketingGlycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe Disease (Late-Onset)United States
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Chile, France, Germany, Italy, Japan, Netherlands, Portugal, Spain, Tunisia, Turkey, United Kingdom
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisUnited States, Belgium, Brazil, France, Germany, Italy, United Kingdom
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Fundación Española de Hematología y HemoterapíaRecruitingNiemann-Pick Diseases | Gaucher Disease | Splenomegaly | Acid SphingoMyelinase Deficiency | ASMDSpain
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Acute Leukemia French AssociationCompletedAcute Myeloblastic Leukemia Core Binding FactorFrance
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St. Justine's HospitalSuspendedType 1 Diabetes | Cardiovascular Risk FactorCanada
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University of Colorado, DenverVA Eastern Colorado Health Care SystemCompletedHealthy | Overweight | Type 2 Diabetes Mellitus | Cardiovascular Risk FactorUnited States
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Jonsson Comprehensive Cancer CenterCalifornia Institute for Regenerative Medicine (CIRM)TerminatedSarcoma | Unresectable Malignant Neoplasm | Locally Advanced Malignant Neoplasm | HLA-A*0201 Positive Cells Present | NY-ESO-1 PositiveUnited States