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Clinical Trials on Morquio A Syndrome in United States
Total 15688 results
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BioMarin PharmaceuticalTerminatedMorquio A Syndrome | MPS IV A | Mucopolysaccharidosis IVAFrance, United Kingdom, Taiwan, United States, Argentina, Netherlands, Canada, Brazil, Germany, Italy
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Greenwood Genetic CenterShriners Hospitals for Children; BioMarin PharmaceuticalCompletedMPS IVA | Maroteaux Lamy Syndrome | MPS VI | Morquio Syndrome AUnited States
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Nadia Ali, PhDBioMarin PharmaceuticalCompletedMorquio A Syndrome | Mucopolysaccharidosis IV AUnited States
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BioMarin PharmaceuticalTerminatedMorquio A Syndrome | MPS IV A | Mucopolysaccharidosis IVAUnited Kingdom
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BioMarin PharmaceuticalCompletedMPS IV AUnited States, Canada, France, United Kingdom, Taiwan, Argentina, Colombia, Japan, Saudi Arabia, Netherlands, Denmark, Korea, Republic of, Brazil, Germany, Portugal, Italy, Qatar
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Nemours Children's ClinicEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingMucopolysaccharidosis IV Type A | Morquio A Syndrome | MPS IVAUnited States
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BioMarin PharmaceuticalCompletedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVATaiwan, United States, Italy, United Kingdom
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BioMarin PharmaceuticalCompletedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IV AUnited States, Canada, France, Taiwan, Argentina, Colombia, Spain, Turkey, Japan, Saudi Arabia, Netherlands, Denmark, Korea, Republic of, Brazil, United Kingdom, Germany, Norway, Portugal, Italy, Qatar
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BioMarin PharmaceuticalTerminatedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited Kingdom, United States, Germany
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Nadia Ali, PhDBioMarin PharmaceuticalCompletedMucopolysaccharidosis IV | Morquio DiseaseUnited States
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BioMarin PharmaceuticalTerminatedMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited States, United Kingdom, Canada, Germany
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Emory UniversityBioMarin PharmaceuticalCompletedMPS - Mucopolysaccharidosis | Morquio DiseaseUnited States
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BioMarin PharmaceuticalICON plcCompletedMucopolysaccharidosis IV Type A | Morquio A Syndrome | MPS IVAUnited States, United Kingdom, Australia, Taiwan, Belgium, Malaysia, Austria, Canada, Portugal, France, Ireland, Czechia, Denmark, Italy, Netherlands, Poland, Puerto Rico
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BioMarin PharmaceuticalApproved for marketingMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited States, Puerto Rico
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Oregon Health and Science UniversityUniversity of Utah; BioMarin PharmaceuticalCompleted
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National Institute of Allergy and Infectious Diseases...PepTcell Limited (t/a SEEK)CompletedMosquito-Borne Infectious DiseasesUnited States
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National Cancer Institute (NCI)CompletedPreviously Treated Myelodysplastic Syndromes | Secondary Myelodysplastic Syndromes | de Novo Myelodysplastic SyndromesUnited States
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedPreviously Treated Myelodysplastic Syndromes | Secondary Myelodysplastic Syndromes | de Novo Myelodysplastic SyndromesUnited States
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Birmingham Women's and Children's NHS Foundation...BioMarin PharmaceuticalWithdrawnMucopolysaccharidosis IV | Morquio A DiseaseUnited Kingdom
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PersImmune, IncUniversity of California, San DiegoUnknown
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Benjamin TomlinsonRecruitingMyelodysplastic Syndromes | MDS/MPN Crossover SyndromesUnited States
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Dana-Farber Cancer InstituteCompletedMyelodysplastic Syndromes (MDS)United States
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Sohail RaoRecruitingSpecimens Are to be Collected From Subjects Who Are Having or Have Had a Fluid or Tissue Removed, a Biopsy or a Blood or Bone Marrow DrawUnited States
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National Institute of Allergy and Infectious Diseases...CompletedMosquito-Borne DiseaseUnited States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedHurler Syndrome | Sanfilippo Syndrome Type A | Sanfilippo Syndrome Type BUnited States
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University of Colorado, DenverActive, not recruitingHigh Grade Myelodysplastic SyndromesUnited States
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University of Wisconsin, MadisonCompleted
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University of California, DavisHelen Keller InternationalCompleted
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The University of Texas Health Science Center,...RecruitingNeuropsychiatric SyndromesUnited States
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Brian JonasNational Cancer Institute (NCI); Celgene; Pharmacyclics LLC.CompletedPreviously Treated Myelodysplastic Syndrome | Myelodysplastic Syndrome | Therapy-Related Myelodysplastic Syndrome | Secondary Myelodysplastic Syndrome | Refractory High Risk Myelodysplastic SyndromeUnited States
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ShireCompletedSanfilippo Syndrome Type AUnited States
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Mayo ClinicCompletedCongenital Myasthenic SyndromeUnited States
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Rockefeller UniversityCompleted
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Wake Forest University Health SciencesNational Cancer Institute (NCI)TerminatedPreviously Treated Myelodysplastic SyndromesUnited States
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National Pediatric Neuroinflammation Organization...CompletedOpsoclonus-myoclonus SyndromeUnited States
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Abramson Cancer Center of the University of PennsylvaniaCompletedA Healthcare Professional, a Patient or Caregiver in the Radiation Oncology Department at the University of PennsylvaniaUnited States
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University of FloridaCompletedSmall Intestinal Bacterial Overgrowth Syndrome (SIBO) | Small Bowel Bacterial Overgrowth Syndrome (SBBOS)United States
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National Pediatric Neuroinflammation Organization...Genentech, Inc.CompletedAtaxia | Myoclonus | Opsoclonus-myoclonus Syndrome | OpsoclonusUnited States
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AkesoRecruitingHigher-risk Myelodysplastic SyndromesUnited States, China
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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Case Comprehensive Cancer CenterRecruitingMyelodysplastic Syndrome (MDS)United States
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Weill Medical College of Cornell UniversityNovartis PharmaceuticalsCompletedMyelodysplastic Syndrome (MDS)United States
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Bristol-Myers SquibbPfizerCompletedN/A - Healthy SubjectsUnited States
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The Champ FoundationChildren's Hospital of Philadelphia; The Cleveland ClinicRecruitingPearson Syndrome | Single Large Scale Mitochondrial DNA Deletion Syndromes (SLSMDS)United States
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SCRI Development Innovations, LLCNovartis PharmaceuticalsTerminated
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New York Institute of TechnologyCompletedN/A Healthy IndividualsUnited States
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Thomas Jefferson UniversityAbbVieRecruitingMyelodysplastic Syndrome | Recurrent Myelodysplastic Syndrome | Refractory Myelodysplastic SyndromeUnited States
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Jasper Therapeutics, Inc.Recruiting
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University of Texas Southwestern Medical CenterChildren's Hospital of PhiladelphiaEnrolling by invitationShort Gut SyndromeUnited States
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DynPort Vaccine Company LLC, A GDIT CompanyCompletedRECOMBINANT BOTULINUM VACCINE A/BUnited States