Example: Heart Attack

Clinical Trials on Mucopolysaccharidosis III

Total 41 results

NCT04018755

Active, not recruiting

Open-label Study of Anakinra in MPS III

Conditions: Mucopolysaccharidosis III
NCT01299727

Terminated

Extension of Study HGT-SAN-055 Evaluating Administration of rhHNS in Patients With Sanfilippo Syndrome Type A (MPS IIIA)

Conditions: Sanfilippo Syndrome
NCT01047306

Completed

A Study of Patients With Sanfilippo Syndrome Type A (MPS IIIA)

Conditions: Sanfilippo Syndrome Type A
NCT02037880

Completed

Natural History Studies of Mucopolysaccharidosis III

Conditions: Mucopolysaccharidosis Type IIIA; Mucopolysaccharidosis Type IIIB
NCT04360265

Recruiting

A Long-term Follow-up Study of Patients With MPS IIIA Treated With ABO-102

Conditions: Mucopolysaccharidosis III-A
NCT01509768

Completed

Natural History Study of Patients With Mucopolysaccharidosis Type IIIB (MPS IIIB, Sanfilippo Syndrome Type B)

Conditions: Sanfilippo Syndrome Type B
NCT02618512

Terminated

A Open Label Study in Previously Studied, SBC-103 Treatment Naïve MPS IIIB Subjects to Investigate the Safety, Pharmacokinetics, and Pharmacodynamics/Efficacy of SBC-103 Administered Intravenously

Conditions: Mucopolysaccharidosis III, Type B (MPS IIIB); Sanfilippo B
NCT03811028

Active, not recruiting

A Study to Assess the Safety, Tolerability, and Efficacy of Long-term SOBI003 Treatment in Pediatric MPS IIIA Patients

Conditions: Sanfilippo Syndrome Type A (MPS IIIA)
NCT03423186

Completed

A Study to Assess the Safety and Tolerability of SOBI003 in Pediatric MPS IIIA Patients

Conditions: Sanfilippo Syndrome Type A (MPS IIIA)
NCT02060526

Completed

Randomized, Controlled, Open-label, Multicenter, Safety and Efficacy Study of rhHNS Administration Via an IDDD in Pediatric Patients With Early Stage MPS IIIA Disease

Conditions: Sanfilippo Syndrome
NCT03300453

Completed

Intracerebral Gene Therapy in Children With Sanfilippo Type B Syndrome

Conditions: Sanfilippo Syndrome B
NCT02293382

Completed

A Retrospective Chart Review of Deceased Patients With Mucopolysaccharidosis Type IIIB

Conditions: MPS IIIB (Sanfilippo Syndrome)
NCT02053064

Completed

Long-term Follow-up of Sanfilippo Type A Patients Treated by Intracerebral SAF-301 Gene Therapy

Conditions: Mucopolysaccharidosis Type III A; Sanfilippo Disease Type A
NCT01474343

Completed

Intracerebral Gene Therapy for Sanfilippo Type A Syndrome

Conditions: Mucopolysaccharidosis Type III A; Sanfilippo Disease Type A
NCT02324049

Completed

Safety, Pharmacokinetics, and Pharmacodynamics/Efficacy of SBC-103 in Mucopolysaccharidosis III, Type B (MPS IIIB)

Conditions: Mucopolysaccharidosis IIIB
NCT04088734

Recruiting

Gene Transfer Study of ABO-102 in Patients With Middle and Advanced Phases of MPS IIIA Disease

Conditions: MPS IIIA; Sanfilippo Syndrome; Sanfilippo A; Mucopolysaccharidosis III
NCT02716246

Recruiting

Phase I/II Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH

Conditions: MPS IIIA; Sanfilippo Syndrome; Sanfilippo A; Mucopolysaccharidosis III
NCT02350816

Terminated

An Extension Study to Determine Safety and Efficacy for Pediatric Patients With MPS Type IIIA Disease Who Participated in Study HGT-SAN-093.

Conditions: Sanfilippo Syndrome; Mucopolysaccharidosis (MPS)
NCT03784287

Active, not recruiting

A Treatment Extension Study of Mucopolysaccharidosis Type IIIB

Conditions: Mucopolysaccharidosis Type IIIB; MPS III B
NCT02754076

Completed

A Treatment Study of Mucopolysaccharidosis Type IIIB

Conditions: MPS III B; Mucopolysaccharidosis Type IIIB
NCT01873911

Completed

Neurobehavioral Phenotypes in MPS III

Conditions: Sanfilippo Syndrome Type A; Sanfilippo Syndrome Type B; Hurler Syndrome
NCT01155778

Completed

Safety, Tolerability, Ascending Dose and Dose Frequency Study of rhHNS Via an IDDD in MPS IIIA Patients

Conditions: Mucopolysaccharidosis (MPS)
NCT04201405

Recruiting

Gene Therapy With Modified Autologous Hematopoietic Stem Cells for Patients With Mucopolysaccharidosis Type IIIA

Conditions: Mucopolysaccharidosis Type IIIA
NCT02493998

Completed

A Study of Mucopolysaccharidosis Type IIIB (MPS IIIB)

Conditions: Mucopolysaccharidosis Type IIIB; Mucopolysaccharidosis Type 3 B; MPS III B; MPS 3 B
NCT02090179

Completed

Evaluation of Blood Brain Barrier Integrity and Structural Abnormalities in MPS IIIB Patients Using Multimodal Magnetic Resonance Imaging

Conditions: MPS IIIB (Sanfilippo B Syndrome)