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Clinical Trials on Mucopolysaccharidosis III
Total 4574 results
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University of FloridaLacerta TherapeuticsCompletedPompe DiseaseUnited States
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)WithdrawnRenal Cell Carcinoma | Stage I Renal Cell Cancer AJCC v8 | Stage II Renal Cell Cancer AJCC v8United States
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University of FloridaBioMarin PharmaceuticalCompleted
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University of FloridaAmicus TherapeuticsCompletedLysosomal Storage Diseases | Glycogen Storage Disease Type II | Pompe DiseaseUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedStage I Childhood Hodgkin Lymphoma | Stage II Childhood Hodgkin Lymphoma | Childhood Lymphocyte Depletion Hodgkin Lymphoma | Childhood Mixed Cellularity Hodgkin Lymphoma | Childhood Nodular Sclerosis Hodgkin Lymphoma | Childhood Favorable Prognosis Hodgkin LymphomaUnited States
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LMU KlinikumGenzyme, a Sanofi CompanyCompletedPompe DiseaseGermany, Taiwan, Italy
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Amicus TherapeuticsCompleted
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National Taiwan University HospitalCompleted
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National Taiwan University HospitalUnknown
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Hospices Civils de LyonUnknown
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type IIUnited States, France, Germany, Israel, Italy, Netherlands, Taiwan
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Fundació Institut de Recerca de l'Hospital de la...Genzyme, a Sanofi CompanyUnknown
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National Taiwan University HospitalCompleted
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Amicus TherapeuticsCompletedGlycogen Storage Disease Type II | Pompe DiseaseUnited States
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Amicus TherapeuticsRecruitingPompe DiseaseUnited States
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Duke UniversitySanofiRecruiting
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Duke UniversityGenzyme, a Sanofi CompanyRecruitingPompe DiseaseUnited States
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University of WashingtonExelixisActive, not recruitingStage I Soft Tissue Sarcoma of the Trunk and Extremities | Stage II Soft Tissue Sarcoma of the Trunk and Extremities | Sarcoma of the Extremity | Stage IA Soft Tissue Sarcoma of the Trunk and Extremities | Stage IB Soft Tissue Sarcoma of the Trunk and ExtremitiesUnited States
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Genzyme, a Sanofi CompanyCompleted
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National Cancer Institute (NCI)CompletedStage I Prostate Adenocarcinoma AJCC v7 | Stage II Prostate Adenocarcinoma AJCC v7United States
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CENTOGENE GmbH RostockWithdrawnLipoprotein Lipase Deficiency | Inborn Error of Lipid Metabolism | Corneal ArcusGermany, India, Sri Lanka
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Roswell Park Cancer InstituteNational Cancer Institute (NCI)TerminatedRecurrent Renal Cell Carcinoma | Stage I Renal Cell Cancer | Stage II Renal Cell CancerUnited States
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Mayo ClinicNational Cancer Institute (NCI)CompletedB-cell Chronic Lymphocytic Leukemia | Refractory Chronic Lymphocytic Leukemia | Stage 0 Chronic Lymphocytic Leukemia | Stage I Chronic Lymphocytic Leukemia | Stage II Chronic Lymphocytic LeukemiaUnited States
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Valerion Therapeutics, LLCTerminatedPompe DiseaseUnited States, United Kingdom
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Boston UniversityInnovations for Poverty ActionCompletedCardiovascular Disease | Breast Cancer | Asthma | Diabetes Type II
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University of FloridaNational Heart, Lung, and Blood Institute (NHLBI)CompletedPompe DiseaseUnited States
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BioMarin PharmaceuticalCompletedPompe DiseaseUnited States, United Kingdom, France, Australia, Germany
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BioMarin PharmaceuticalTerminatedPompe DiseaseUnited States, United Kingdom, Australia, France, Germany, New Zealand
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University of FloridaCompletedPompe DiseaseUnited States
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Centre Hospitalier de CayenneCompleted
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National Taiwan University HospitalUnknown
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Genzyme, a Sanofi CompanyTerminatedPompe DiseaseUnited States
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Pompe DiseaseUnited States
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type IIUnited States, Taiwan, Israel, United Kingdom, France
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National Cancer Institute (NCI)CompletedRecurrent Childhood Medulloblastoma | Recurrent Childhood Ependymoma | Childhood Atypical Teratoid/Rhabdoid Tumor | Childhood Choroid Plexus Tumor | Childhood Craniopharyngioma | Childhood Ependymoblastoma | Childhood Grade I Meningioma | Childhood Grade II Meningioma | Childhood Grade III Meningioma | Childhood High-grade Cerebellar Astrocytoma and other conditionsUnited States
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European Institute of OncologyUniversity of Rome Tor VergataRecruitingLung Cancer | Non-small Cell Lung Cancer Stage I | Non-small Cell Lung Cancer Stage II | Lung Cancer DiagnosisItaly
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Xinhua Hospital, Shanghai Jiao Tong University...Shanghai Vitalgen BioPharma Co., Ltd.RecruitingType II Gaucher DiseaseChina
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Zuyderland Medisch CentrumNot yet recruitingCervical Intraepithelial Neoplasia-II | High Risk Human Papillomavirus
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Universitair Ziekenhuis BrusselMarguerite - Marie Delacroix FoundationNot yet recruitingClassical Lissencephalies and Subcortical Band HeterotopiasBelgium
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Shanghai Zhongshan HospitalShanghai Changzheng HospitalRecruitingChronic Lymphocytic Leukemia Stage A(0) | Chronic Lymphocytic Leukemia Stage A(I) | Chronic Lymphocytic Leukemia Stage A(II) | Chronic Lymphocytic Leukaemia Stage B(I)China
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Serhat Gumrukcu, MD PhDFrida Therapeutics LLCRecruiting
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Masahiro TsuboiEli Lilly and Company; Merck Sharp & Dohme LLCRecruitingNon-small Cell Lung Cancer Stage II | Non-small Cell Lung Cancer Stage IB | Non-small Cell Lung Cancer Stage ⅢAJapan
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Genzyme, a Sanofi CompanyActive, not recruiting
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Amicus TherapeuticsAvailable
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Hopital La RabtaCompletedDiabetes Mellitus, Type 2 | Vitamin D Deficiency | Adrenal Insufficiency | Hypogonadism, Male | Statin Adverse Reaction | Dyslipidemia Associated With Type II Diabetes MellitusTunisia
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Duke UniversityCompleted
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Kinderkrankenhaus auf der BultCompletedType 1 Diabetes | Familial Hypercholesterolemia
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Heart Care FoundationFondazione SISACompletedCoronary Artery DiseaseItaly
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Duke UniversityGenzyme, a Sanofi CompanyCompleted