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Clinical Trials on Multiple+Sulfatase+Deficiency+Disease
Total 16986 results
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Genentech, Inc.CompletedDwarfism, Pituitary | Turner Syndrome
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GlaxoSmithKlineTerminatedLiver Diseases | HIV Infection | Thrombocytopenia | Hepatitis C Virus | HBV | NASH - Nonalcoholic Steatohepatitis | Human Immunodeficiency Virus | Chronic Liver Disease | HCV | Non-alcoholic Steatohepatitis | Hepatitis B VirusUnited States, Spain, Taiwan, Italy, Belgium, France, Korea, Republic of, Canada, Russian Federation, Pakistan, Poland, India, Argentina
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University Health Network, TorontoCompletedEffects of Photographic Aids (Photos of Faces) on Patient Recall of Their Clinical Care Team | Effects of Photographic Aids (Photos of Faces) on Clinician-patient Communication | Effects of Photographic Aids (Photos of Faces) on Overall Patient SatisfactionCanada
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National Institute of Respiratory Diseases, MexicoHospital General Dr. Manuel Gea González; National Institute of Medical Sciences... and other collaboratorsNot yet recruitingAcquired Immunodeficiency Syndrome | Cryptococcal Meningitis | Tuberculosis Infection | Histoplasmosis AIDSMexico
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Verinata Health, Inc.CompletedPregnancy | Down Syndrome | Edwards Syndrome | Patau Syndrome | Turners SyndromeUnited States
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Thomas BenfieldRecruitingHIV Infections | Obesity | Renal Insufficiency | Osteoporosis | Hiv | Weight Gain | HIV LipodystrophyDenmark
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Eunice Kennedy Shriver National Institute of Child...CompletedSmith-Lemli-Opitz SyndromeUnited States
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Eunice Kennedy Shriver National Institute of Child...CompletedEstimation of the Carrier Frequency and Incidence of Smith-Lemli-Opitz Syndrome in African AmericansSmith-Lemli-Opitz SyndromeUnited States
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Thomas BenfieldRecruitingCardiovascular Diseases | HIV Infections | Hiv | Weight Change, Body | HIV Lipodystrophy | HIV CardiomyopathyDenmark
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Baxalta now part of ShireCompletedPrimary Immunodeficiency Diseases (PID) | Immune Thrombocytopenic Purpura (ITP) | Kawasaki SyndromeUnited States
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M.D. Anderson Cancer CenterPfizerTerminatedRenal Cell Carcinoma | Von Hippel-Lindau Syndrome | HemangioblastomaUnited States
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BloodworksNational Heart, Lung, and Blood Institute (NHLBI)CompletedHIV Infections | Acquired Immunodeficiency Syndrome | Hemophilia A | Hepatitis, Viral, Human | Blood Disease | Cytomegalovirus Infections | Blood Transfusion
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Food and Drug Administration (FDA)National Eye Institute (NEI)RecruitingAge-Related Macular Degeneration | Retinal Degeneration | Retinitis Pigmentosa | Usher Syndromes | Cone Dystrophy | Rod Dystrophy | Cone Rod Dystrophy | Hydroxychloroquine Retinopathy | Late-Onset Retinal Degeneration | Rod Cone DystrophyUnited States
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Novartis PharmaceuticalsCompletedMyelodysplastic Syndromes | Fanconi Syndrome | Anemia, Aplastic | Beta-thalassemia | Anemia, Diamond-BlackfanUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedMedulloblastoma | Nevoid Basal Cell Carcinoma Syndrome | Desmoplastic/Nodular Medulloblastoma | Medulloblastoma With Extensive NodularityUnited States, Canada, Puerto Rico, Australia
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H. Lee Moffitt Cancer Center and Research InstituteCompletedMyelodysplastic Syndromes | Primary Myelofibrosis | Multiple Myeloma | Hodgkin Lymphoma | Non-Hodgkin's Lymphoma | Chronic Myelomonocytic Leukemia | Chronic Myeloid Leukemia | Acute Leukemia in RemissionUnited States
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NeurogesXCompletedHIV Infections | Pain | Diabetes Mellitus | Diabetic Neuropathies | Peripheral Nervous System Diseases | Neuralgia | Herpes Zoster | PolyneuropathiesUnited States
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National Institutes of Health Clinical Center (CC)Enrolling by invitationAdenocarcinoma | Renal Cell Carcinoma | Prostate Cancer | Prostate Neoplasms | Von Hippel Lindau DiseaseUnited States
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NeurogesXTerminatedHIV Infections | Pain | Diabetes Mellitus | Diabetic Neuropathies | Peripheral Nervous System Diseases | Neuralgia | Herpes Zoster | Polyneuropathies
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Golden Jubilee National HospitalUniversity of Glasgow; Royal Infirmary of Edinburgh; Aberdeen Royal Infirmary; Network...Not yet recruitingAortic Valve Insufficiency | Marfan Syndrome | Bicuspid Aortic Valve | Aortic Diseases | Aortic Dissection | Aortic Aneurysm, Thoracic | Ehlers-Danlos Syndrome | Aortic Ectasia | Loeys-Dietz Syndrome
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Karolinska InstitutetRecruitingAcute Kidney Injury | Pulmonary Hypertension | Congenital Diaphragmatic Hernia | Multiple Organ Failure | HyperchloremiaSweden
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Case Comprehensive Cancer CenterCompletedAcute Myeloid Leukemia | Multiple Myeloma | Acute Lymphoblastic Leukemia | Chronic Lymphocytic Leukemia | Non-Hodgkin Lymphoma | Myelodysplastic Syndrome | Chronic Myelogenous Leukemia | Myeloproliferative Neoplasm | Acute Biphenotypic Leukemia | Hodgkins DiseaseUnited States
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InSightecCompleted
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The Cleveland ClinicNational Cancer Institute (NCI)CompletedMelanoma | Sarcoma | Lymphoma | Kidney Cancer | Breast Cancer | Multiple Myeloma | Unspecified Adult Solid Tumor, Protocol SpecificUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedMultiple Myeloma | Chronic Myeloid Leukemia (CML) | Pancreatic Ca | Colon/Rectal Ca | Carcinoma, Non-Small -Cell LungUnited States
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CENTOGENE GmbH RostockWithdrawnHypophosphatemia | Photophobia | Renal Fanconi SyndromeGermany, India, Sri Lanka
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AbbVieCompletedHepatitis C Virus (HCV)China, Korea, Republic of
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Lei LiUnknownLynch Syndrome | Endometrial Cancer | Microsatellite Instability | Circulating Tumor CellChina
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InCor Heart InstituteNovartisCompletedTuberous Sclerosis | Angiomyolipoma | LymphangioleiomyomatosisBrazil
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Virginia Commonwealth UniversityGenzyme, a Sanofi CompanyCompletedAcute Myeloid Leukemia | Leukemia | Multiple Myeloma | Hodgkin Lymphoma | Non-Hodgkin's Lymphoma | Chronic Lymphocytic Leukemia | Myelodysplastic Syndrome | Chronic Myelogenous LeukemiaUnited States
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Children's Hospital Medical Center, CincinnatiNovartis PharmaceuticalsCompletedTuberous Sclerosis | LymphangioleiomyomatosisUnited States
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Children's Hospital Medical Center, CincinnatiThe LAM Foundation; Tuberous Sclerosis AllianceCompletedTuberous Sclerosis | LymphangioleiomyomatosisUnited States
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Assistance Publique - Hôpitaux de ParisNot yet recruiting
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Hacettepe UniversityUnknownCerebral Palsy | Muscular Dystrophies | Traumatic Brain Injury | Autism Spectrum Disorder | Down Syndrome | Disability Physical | Disability, Developmental
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The Chaim Sheba Medical CenterRecruitingFragile X Syndrome | Williams Syndrome | Velocardiofacial SyndromeIsrael
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University of California, San DiegoNational Heart, Lung, and Blood Institute (NHLBI)CompletedObstructive Sleep Apnea | Human Immunodeficiency VirusUnited States
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University of BirminghamIMPACT (funded by NHS Blood & Transplant, Anthony Nolan and Leukaemia UK)RecruitingAcute Myeloid Leukemia | Myelodysplastic Syndromes | Multiple Myeloma | Hodgkin Lymphoma | Myelofibrosis | Chronic Myelomonocytic Leukemia | Acute Lymphoblastic Leukemia | Non Hodgkin Lymphoma | Chronic Myelogenous LeukemiaUnited Kingdom
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Washington University School of MedicineBioLineRx, Ltd.CompletedMultiple Myeloma | Hodgkin Disease | Non-Hodgkin's Lymphoma | Acute Lymphoblastic Leukemia | Non-Hodgkin Lymphoma | Myelodysplastic Syndrome | Acute Myelogenous Leukemia | Chronic Myelogenous Leukemia | Myeloproliferative Neoplasm | Hodgkin's Disease | Hodgkins DiseaseUnited States
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AbbVieCompletedHepatitis C Virus Infection | Chronic Hepatitis C | Human Immunodeficiency Virus Infection | Compensated Cirrhosis and Non-cirrhotics
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AbbVieCompletedHepatitis C Virus Infection | Chronic Hepatitis C | Human Immunodeficiency Virus Infection | Compensated Cirrhosis and Non-cirrhotics
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Centre Hospitalier Universitaire DijonUnknownHeart Failure | Multiple Sclerosis | Hemophilia | Chronic Respiratory Failure | Horton's Disease | Chronic Coronary Syndrome | AMD and Macular Edema | Malignant HemopathyFrance
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UK Kidney AssociationRecruitingVasculitis | AL Amyloidosis | Tuberous Sclerosis | Fabry Disease | Cystinuria | Focal Segmental Glomerulosclerosis | IgA Nephropathy | Bartter Syndrome | Pure Red Cell Aplasia | Membranous Nephropathy | Atypical Hemolytic Uremic Syndrome | Autosomal Dominant Polycystic Kidney Disease | Cystinosis | Nephronophthisis | BK Nephropathy and other conditionsUnited Kingdom
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Melbourne HealthRecruitingMyelodysplastic Syndromes | Leukemia, Myeloid, Acute | Plasma Cell Myeloma | Non-hodgkin Lymphoma | Leukemia, Lymphoblastic, Acute, L1 | Leukemia, Lymphoblastic, Acute, L2Australia
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Indiana UniversityTerminatedMultiple Myeloma | Myelofibrosis | Chronic Lymphocytic Leukemia | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Mantle-Cell Lymphoma | Chronic Myelogenous Leukemia | Lymphoma, Non-Hodgkin's | Myelodysplasia | Hodgkin's DiseaseUnited States
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Foundation for Professional Development (Pty) LtdNational Institute of Allergy and Infectious Diseases (NIAID); University of... and other collaboratorsRecruitingHIV/AIDS | Pregnancy | Cost-effectiveness | Antenatal Care | Chlamydia Trachomatis | Vaginal Microbiome | Birth Outcomes | Sexually Transmitted Infection | Neisseria Gonorrhoeae | Trichomonas VaginalisSouth Africa
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Memorial Sloan Kettering Cancer CenterPediatric Brain Tumor ConsortiumTerminatedFanconi Anemia | Myelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML)United States
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AbbVieAvailableMultiple Myeloma | Non-Hodgkin's Lymphoma | Amyloidosis | Chronic Lymphocytic Leukemia (CLL) | Acute Myeloid Leukemia (AML) | Acute Lymphoblastic Leukemia (ALL) | Plasma Cell Leukemia
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Gynecologic Oncology GroupNational Cancer Institute (NCI)Not yet recruitingLynch Syndrome | Recurrent Uterine Corpus Carcinoma | Stage I Uterine Corpus Cancer | Stage II Uterine Corpus Cancer | Stage III Uterine Corpus Cancer | Stage IV Uterine Corpus CancerUnited States
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Bayside HealthMonash UniversityRecruitingLymphoma, Non-Hodgkin | Multiple Myeloma | HIV | Chronic Lymphocytic Leukemia | Organ Transplantation | COVID-19 VaccinesAustralia
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Juno Therapeutics, a Subsidiary of CelgeneTerminatedFollicular Lymphoma | Multiple Myeloma | Mantle Cell Lymphoma | Chronic Lymphocytic Leukemia | Non Hodgkin Lymphoma | Diffuse Large B Cell LymphomaUnited States