- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Muscular Dystrophies, Limb-Girdle in United States
Total 529 results
-
Wake Forest University Health SciencesMuscular Dystrophy AssociationCompletedMuscular Dystrophies, Limb-Girdle (GENETICALLY CONFIRMED)United States
-
Linda Pax LowesRecruitingLimb-Girdle Muscular Dystrophy Type 2A | Limb-Girdle Muscular Dystrophy, Type 2EUnited States
-
Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedLimb-Girdle Muscular DystrophyUnited States
-
ML Bio Solutions, Inc.RecruitingLimb-Girdle Muscular Dystrophy Type 2I (LGMD2I)United States, Netherlands, United Kingdom, Denmark, Australia, Italy, Norway
-
Nationwide Children's HospitalMyonexus TherapeuticsRecruitingLimb-Girdle Muscular Dystrophy, Type 2EUnited States
-
Sarepta Therapeutics, Inc.RecruitingLimb-girdle Muscular DystrophyUnited States
-
Sarepta Therapeutics, Inc.Active, not recruiting
-
aTyr Pharma, Inc.CompletedLimb-Girdle Muscular Dystrophies | Facioscapulohumeral Muscular DystrophyUnited States, Denmark, France
-
Virginia Commonwealth UniversityUniversity of Colorado, Denver; Washington University School of Medicine; University... and other collaboratorsRecruitingLimb Girdle Muscular Dystrophy | Calpain-3 Deficiency Limb Girdle Muscular Dystrophy Type 2A | Limb Girdle Muscular Dystrophy Type R1 | LGMD2AUnited States, United Kingdom
-
The Emmes Company, LLCJain Foundation; Coalition to Cure Calpain 3 (C3)Terminated
-
PTC TherapeuticsTerminatedLimb-Girdle Muscular DystrophyUnited States, Norway, Canada, Sweden, Russian Federation, Denmark, France, Germany
-
Cooperative International Neuromuscular Research...Carolinas Medical Center lead study siteCompletedBecker Muscular Dystrophy | Limb-Girdle Muscular Dystrophy, Type 2A (Calpain-3 Deficiency) | Limb-Girdle Muscular Dystrophy, Type 2B (Miyoshi Myopathy, Dysferlin Deficiency) | Limb-Girdle Muscular Dystrophy, Type 2I (FKRP-deficiency)United States
-
University of North Carolina, Chapel HillNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedMuscular Dystrophies | Duchenne Muscular Dystrophy | Becker Muscular Dystrophy | Limb-Girdle Muscular DystrophyUnited States
-
Northwestern UniversityCompletedBecker Muscular Dystrophy | Limb-girdle Muscular DystrophyUnited States
-
Boston Children's HospitalNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingLimb-girdle Muscular Dystrophy | Neuromuscular; Disorder, Hereditary | Duchenne/Becker Muscular DystrophyUnited States
-
Sarepta Therapeutics, Inc.Active, not recruiting
-
Asklepios Biopharmaceutical, Inc.RecruitingMuscular Dystrophy | Limb Girdle Muscular Dystrophy | LGMD2I | LGMD | Limb-Girdle Muscular Dystrophy Type 2 | LGMD2 | FKRP | FKRP Mutation | Fukutin Related ProteinUnited States
-
Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedMuscular DystrophiesUnited States
-
Wyeth is now a wholly owned subsidiary of PfizerCompletedBecker Muscular Dystrophy | Facioscapulohumeral Muscular Dystrophy | Limb-Girdle Muscular DystrophyUnited States
-
Virginia Commonwealth UniversityWashington University School of Medicine; University of Iowa; University of Minnesota and other collaboratorsRecruitingMuscular Dystrophies | Limb Girdle Muscular DystrophyUnited States, United Kingdom
-
GenethonActive, not recruitingLGMD2IDenmark, France, United Kingdom
-
ML Bio Solutions, Inc.Virginia Commonwealth UniversityCompletedMuscular Dystrophies | Limb Girdle Muscular DystrophyUnited States, Denmark
-
Sarepta Therapeutics, Inc.Active, not recruitingLimb-Girdle Muscular Dystrophy, Type 2EUnited States
-
aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular Dystrophy | Limb Girdle Muscular DystrophyUnited States, Denmark, Italy
-
Cooperative International Neuromuscular Research...National Institutes of Health (NIH)CompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | Limb Girdle Muscular DystrophyUnited States
-
Sarepta Therapeutics, Inc.RecruitingLimb-girdle Muscular DystrophyUnited States, Brazil, Belgium, Canada, Germany, Italy, Spain, Sweden, Turkey, United Kingdom
-
Cooperative International Neuromuscular Research...National Institutes of Health (NIH)CompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | Limb Girdle Muscular DystrophyUnited States
-
Cooperative International Neuromuscular Research...United States Department of DefenseCompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | Limb Girdle Muscular DystrophyUnited States, Japan, Canada
-
Atamyo TherapeuticsRecruiting
-
AbiliTech Medical Inc.Richard M. Schulze Family FoundationRecruitingCerebral Palsy | Muscular Dystrophies | Duchenne Muscular Dystrophy | Becker Muscular Dystrophy | Spinal Muscular Atrophy | Limb Girdle Muscular Dystrophy | FSHDUnited States
-
Newcastle-upon-Tyne Hospitals NHS TrustJain FoundationActive, not recruitingDysferlinopathy | LGMD2B Now Classified as LGMDR2 | Miyoshi MyopathyKorea, Republic of, Chile, Spain, United States, Denmark, France, Italy, Japan, United Kingdom
-
Newcastle UniversityLudwig-Maximilians - University of Munich; LGMD2i Research Fund; CureLGMD2iRecruitingLimb Girdle Muscular Dystrophy | Congenital Muscular Dystrophy | LGMDR9 | LGMD2I | Walker-Warburg Syndrome | Muscle-Eye-Brain Disease | FKRP Gene MutationUnited Kingdom
-
ML Bio Solutions, Inc.Active, not recruiting
-
Myotonic Dystrophy FoundationRecruitingMyotonic Dystrophy | Myotonic Dystrophy 1 | Steinert's Disease | Congenital Myotonic Dystrophy | PROMM (Proximal Myotonic Myopathy) | Steinert Disease | Dystrophia Myotonica 1 | Myotonic Dystrophy 2 | Dystrophia Myotonica | Dystrophia Myotonica 2 | Myotonia Dystrophica | Myotonic Dystrophy, Congenital | Myotonic... and other conditionsUnited States
-
Johns Hopkins UniversityRecruitingCompartment Syndrome of Leg | Extracorporeal Membrane Oxygenation Complication | Limb Ischemia, Critical | Limb IschemiaUnited States
-
University of Illinois at ChicagoAmerican Heart AssociationRecruitingPeripheral Arterial Disease | Lower Limb Amputation Below Knee (Injury) | Lower Limb Amputation Above Knee (Injury) | Amputation | Peripheral Vascular Disease | Lower Limb Amputation KneeUnited States
-
Abbott Medical DevicesActive, not recruiting
-
Cure CMDRecruitingEmery-Dreifuss Muscular Dystrophy | Congenital Myasthenic Syndrome | Limb-Girdle Muscular Dystrophy | Congenital Muscular Dystrophy With ITGA7 (Integrin Alpha-7) Deficiency | Alpha-Dystroglycanopathy (Congenital Muscular Dystrophy and Abnormal Glycosylation of Dystroglycan With Severe Epilepsy) and other conditionsUnited States
-
Edgewise Therapeutics, Inc.CompletedMuscular DystrophiesUnited States
-
National Heart, Lung, and Blood Institute (NHLBI)Terminated
-
GlaxoSmithKlineCompleted
-
FDA Office of Orphan Products DevelopmentCompletedMuscular DystrophiesUnited States
-
Santhera PharmaceuticalsCompleted
-
Wake Forest University Health SciencesCompleted
-
Hugo W. Moser Research Institute at Kennedy Krieger...Active, not recruitingFacioscapulohumeral Muscular DystrophyUnited States
-
Duke UniversityNational Heart, Lung, and Blood Institute (NHLBI)Completed
-
Katherine MathewsNational Institute of Neurological Disorders and Stroke (NINDS)Recruiting
-
Edgewise Therapeutics, Inc.CompletedNervous System Diseases | Genetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Healthy VolunteerUnited States
-
Michael MurphyZimmer BiometCompletedPeripheral Artery Disease | Critical Limb Ischemia | Vascular DiseaseUnited States
-
Duke UniversityCompleted