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Clinical Trials on Muscular Dystrophy, Duchenne in United Kingdom
Total 17759 results
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Avidity Biosciences, Inc.CompletedMyotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy Type 1 (DM1) | Myotonic Dystrophy 1 | Myotonic Muscular Dystrophy | DM1 | Dystrophy Myotonic | Steinert DiseaseUnited States
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Radboud University Medical CenterAssistance Publique - Hôpitaux de Paris; Ludwig-Maximilians - University of... and other collaboratorsCompletedMyotonic Dystrophy Type 1Netherlands, France, Germany, United Kingdom
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular Dystrophy (FSHD)United States, France, Italy
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular Dystrophy | Limb Girdle Muscular DystrophyUnited States, Denmark, Italy
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Virginia Commonwealth UniversityWashington University School of Medicine; University of Iowa; University of Minnesota and other collaboratorsRecruitingMuscular Dystrophies | Limb Girdle Muscular DystrophyUnited States, United Kingdom
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Nationwide Children's HospitalMyonexus TherapeuticsRecruitingLimb-Girdle Muscular Dystrophy, Type 2EUnited States
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Fulcrum TherapeuticsActive, not recruitingFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Canada, France, Spain
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Fulcrum TherapeuticsCompletedFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Canada, France, Spain
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ProQR TherapeuticsWithdrawnCorneal Diseases | Fuchs Endothelial Corneal Dystrophy | FECD3 | LRS | Descemet's Membrane DisorderUnited Kingdom
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aTyr Pharma, Inc.CompletedLimb-Girdle Muscular Dystrophies | Facioscapulohumeral Muscular DystrophyUnited States, Denmark, France
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University of RochesterCompletedFacioscapulohumeral Muscular DystrophyUnited States
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Hugo W. Moser Research Institute at Kennedy Krieger...Concord Hospital; FSHD Global Research FoundationCompletedFacioscapulohumeral Muscular DystrophyUnited States, Australia
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Hugo W. Moser Research Institute at Kennedy Krieger...Active, not recruitingFacioscapulohumeral Muscular DystrophyUnited States
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Prothelia, Inc.Cure CMD; The Bönnemann Laboratory, NINDS, National Institutes of Health; Oscar... and other collaboratorsCompletedMerosin Deficient Congenital Muscular DystrophyUnited States
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University of Kansas Medical CenterNational Institutes of Health (NIH)CompletedFacioscapulohumeral Muscular DystrophyUnited States
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular DystrophyUnited States, Italy, Netherlands
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Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedLimb-Girdle Muscular DystrophyUnited States
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Bioblast Pharma Ltd.CompletedOculopharyngeal Muscular DystrophyUnited States, Israel, Canada
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Virginia Commonwealth UniversityRadboud University Medical Center; University of California, Los Angeles; University... and other collaboratorsRecruitingMyotonic Dystrophy 1United States, Netherlands, United Kingdom, New Zealand, Germany, Italy, Canada, France
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National Institute of Neurological Disorders and...TerminatedMyotonic Dystrophy Type-1 | Myotonic Dystrophy Type-2United States
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University of Kansas Medical CenterNational Institute of Neurological Disorders and Stroke (NINDS)Active, not recruitingFacioscapulohumeral Muscular DystrophyUnited States
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Hope Biosciences Stem Cell Research FoundationHope BiosciencesNo longer availableCongenital Muscular Dystrophy Due to Lamin A/C MutationUnited States
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Sarepta Therapeutics, Inc.Active, not recruiting
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The Emmes Company, LLCJain Foundation; Coalition to Cure Calpain 3 (C3)Terminated
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Benitec Biopharma, Inc.RecruitingOculopharyngeal Muscular DystrophyUnited States
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University of FloridaCompleted
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Sarepta Therapeutics, Inc.RecruitingLimb-girdle Muscular DystrophyUnited States
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Wake Forest University Health SciencesMuscular Dystrophy AssociationCompletedMuscular Dystrophies, Limb-Girdle (GENETICALLY CONFIRMED)United States
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Newcastle UniversityRecruiting
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedFacioscapulohumeral Muscular DystrophyUnited States, Spain, Canada
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Mayo ClinicNational Eye Institute (NEI)CompletedRetinal Disease | Best Vitelliform Macular Dystrophy | Bestrophinopathy | Adult Onset Vitelliform Macular Dystrophy | Autosomal Dominant VitreoretinalchoroidopathyUnited States
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Avidity Biosciences, Inc.Active, not recruitingNervous System Diseases | Genetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Neurodegenerative Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Heredodegenerative Disorders, Nervous System | Myotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy... and other conditionsUnited States
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PTC TherapeuticsTerminatedLimb-Girdle Muscular DystrophyUnited States, Norway, Canada, Sweden, Russian Federation, Denmark, France, Germany
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University of SouthamptonUnknownKeratoconus | Fuchs Dystrophy | Corneal DiseaseUnited Kingdom
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Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedMuscular DystrophiesUnited States
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National Eye Institute (NEI)National Cancer Institute (NCI)RecruitingStargardt-Like Macular DystrophyUnited States
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Santhera PharmaceuticalsCompleted
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AMO Pharma LimitedCompletedCongenital Myotonic DystrophyUnited States, Canada, New Zealand, Australia, United Kingdom
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Sarepta Therapeutics, Inc.RecruitingLimb-girdle Muscular DystrophyUnited States, Brazil, Belgium, Canada, Germany, Italy, Spain, Sweden, Turkey, United Kingdom
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Asklepios Biopharmaceutical, Inc.RecruitingMuscular Dystrophy | Limb Girdle Muscular Dystrophy | LGMD2I | LGMD | Limb-Girdle Muscular Dystrophy Type 2 | LGMD2 | FKRP | FKRP Mutation | Fukutin Related ProteinUnited States
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Sarepta Therapeutics, Inc.Active, not recruiting
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University of UtahCompletedMacular Dystrophy, CornealUnited States
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Nationwide Children's HospitalRecruiting
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Columbia UniversityNational Eye Institute (NEI); Centre Hospitalier National d'Ophtalmologie des... and other collaboratorsRecruitingRetinitis Pigmentosa | Best Vitelliform Macular DystrophyUnited States, Germany, France
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Sarepta Therapeutics, Inc.Active, not recruitingLimb-Girdle Muscular Dystrophy, Type 2EUnited States
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PepGen IncRecruitingMyotonic Dystrophy 1United States, Canada
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI); Cure CMDCompletedCongenital Muscular DystrophyUnited States
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Hoffmann-La RocheTerminatedMuscular Dystrophy (DMD)United States, Canada
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Expansion Therapeutics, Inc.CompletedMyotonic Dystrophy | Myotonic Dystrophy, Type 1 (DM1)United States
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Virginia Commonwealth UniversityRecruitingCongenital Myotonic Dystrophy | Childhood Myotonic Dystrophy | CDM | CHDMUnited States, Italy