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Clinical Trials on Muscular Dystrophy, Duchenne in United States
Total 17803 results
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Summit TherapeuticsCompletedDuchenne Muscular DystrophyUnited Kingdom
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Vanderbilt University Medical CenterRecruitingDuchenne Muscular DystrophyUnited States
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Avidity Biosciences, Inc.RecruitingDuchenne Muscular Dystrophy | Exon 44United States
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Sarepta Therapeutics, Inc.Hoffmann-La RocheRecruitingDuchenne Muscular DystrophyBelgium, United States, Japan, Spain, Italy, United Kingdom
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ReveraGen BioPharma, Inc.University of Pittsburgh; Newcastle University; European Union; Cooperative International...CompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, United Kingdom, Spain, Netherlands, Sweden, Czechia, Australia, Greece, Israel
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Newcastle... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Germany, Italy
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Santhera PharmaceuticalsTerminatedDuchenne Muscular DystrophyUnited States, Belgium, United Kingdom, Austria, France, Germany, Italy, Spain, Switzerland
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyUnited Kingdom, Italy, Belgium, Netherlands, France
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PfizerTerminatedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Japan, Italy
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Vanderbilt University Medical CenterRecruitingDuchenne Muscular DystrophyUnited States
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Percheron TherapeuticsActive, not recruitingDuchenne Muscular DystrophyUnited Kingdom, Australia, Serbia, Turkey, Bulgaria
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophyKorea, Republic of, Chile, Taiwan, China, United States, United Kingdom, Netherlands, Spain, Australia, Norway, Russian Federation, Greece, Italy, Turkey, Mexico, Canada, Hong Kong, New Zealand, Ukraine
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ItalfarmacoSyneos HealthCompletedDuchenne Muscular DystrophyUnited States, Italy, Spain, Canada, Belgium, France, Germany, Israel, Netherlands, Serbia, United Kingdom
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PfizerTerminatedDuchenne Muscular DystrophyUnited States, Australia, Canada, United Kingdom, Japan, Bulgaria, Italy, Poland
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BioMarin PharmaceuticalNo longer availableDuchenne Muscular DystrophyUnited States, Germany, United Kingdom, Japan, Netherlands, France, Spain, Korea, Republic of, Italy, Belgium, Taiwan, Argentina, Australia, Bulgaria, Czechia, Israel, Norway, Poland, Russian Federation, Turkey
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States, Belgium, Israel, Spain, Canada, Australia, Switzerland, United Kingdom, France, China, Netherlands, Italy, Austria, Czechia
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Sarepta Therapeutics, Inc.TerminatedDuchenne Muscular DystrophyBelgium, France, Italy, United Kingdom
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Sarepta Therapeutics, Inc.TerminatedAn Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular DystrophyDuchenne Muscular DystrophyUnited States, Belgium, Canada, Spain, United Kingdom, Czechia, Germany, Israel, Bulgaria, France, Italy, Poland, Sweden
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PTC TherapeuticsParexel; Dohmen Life Science ServicesApproved for marketingDuchenne Muscular DystrophyUnited States
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GenethonRecruiting
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyBelgium, Netherlands, France, United Kingdom, Italy
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ItalfarmacoCromsourceEnrolling by invitationDuchenne Muscular DystrophySpain, United States, Canada, Belgium, France, Israel, Italy, Netherlands, Serbia, Germany, United Kingdom
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PfizerActive, not recruitingDuchenne Muscular DystrophyUnited States, Spain, Belgium, Korea, Republic of, Taiwan, Canada, Australia, Germany, Japan, France, Italy, United Kingdom, Russian Federation, Israel, Switzerland
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, Germany, Spain, Sweden, Canada, Italy, Australia, Belgium, France, Israel, United Kingdom
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Jett Foundation, Inc.Pfizer; Hoffmann-La Roche; Italfarmaco; Nationwide Children's Hospital; Capricor... and other collaboratorsCompletedDuchenne Muscular Dystrophy | Rare Diseases | Disability Physical | Burden, Dependency | Impairment | Disease ManagementUnited States
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Sarepta Therapeutics, Inc.Hoffmann-La RocheActive, not recruitingDuchenne Muscular DystrophyUnited States, Japan, Taiwan, Belgium, Spain, Germany, Hong Kong, Italy, United Kingdom
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Great Ormond Street Hospital for Children NHS Foundation...Catholic University of the Sacred Heart; Università degli Studi di Ferrara; Universidad... and other collaboratorsRecruitingDuchenne Muscular Dystrophy | Becker Muscular DystrophyDenmark, France, Italy, Spain, United Kingdom, Netherlands
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Hoffmann-La RocheCompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, Australia, Japan, France, Netherlands, Spain, Argentina, Germany, Italy, United Kingdom, Sweden
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Subha RamanBallou SkiesCompletedDuchenne Muscular DystrophyUnited States
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University Hospital, Basel, SwitzerlandCompletedDuchenne Muscular DystrophyFrance, Spain, Germany, Netherlands, Switzerland, United Kingdom
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ItalfarmacoRecruitingDuchenne Muscular DystrophyCanada, Italy, France, Belgium, Germany, Netherlands, United Kingdom
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GlaxoSmithKlineCompletedMuscular DystrophiesGermany, Belgium, Turkey, Netherlands, Spain, Israel, Australia, France, United Kingdom
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States, Spain, Canada, Australia, China, Italy, Belgium, France, Netherlands, Austria, United Kingdom
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Capricor Inc.CompletedDuchenne Muscular Dystrophy | CardiomyopathyUnited States
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, Duchenne | Musculoskeletal DiseaseUnited States, Taiwan, India, Korea, Republic of, Thailand, Australia, Brazil, Bulgaria, Canada, China, Hong Kong, Malaysia, Mexico, Poland, Puerto Rico, Russian Federation, Turkey, Japan
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyUnited States, Netherlands, Belgium, Germany, Argentina, Brazil, France, Italy, Sweden, Turkey
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Active, not recruitingDuchenne Muscular DystrophyKorea, Republic of, Chile, Japan, China, United Kingdom, Netherlands, Spain, Norway, Russian Federation, Australia, Greece, Italy, New Zealand, Turkey, Mexico, Czechia, Canada
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University of PittsburghRespirtech, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Korea, Republic of, Italy, United Kingdom, Canada, Poland, Spain, France, Germany, Belgium, Australia, Czechia, Serbia, Greece, Argentina, Bulgaria, Denmark, Hungary, India, Ireland, Israel, Mexico, Russian Federation, ...
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Cooperative International Neuromuscular Research...United States Department of Defense; National Institutes of Health (NIH); U.S... and other collaboratorsUnknownDuchenne Muscular DystrophyUnited States, Canada, Australia, India, Israel, Argentina, Italy, Sweden
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, Belgium, Australia, Canada, France, Germany, Israel, Italy, Spain, Sweden, United Kingdom
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | DystrophinopathyUnited Kingdom, Canada, Germany, Spain, Sweden, Italy, Australia, Belgium, France, Israel
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GlaxoSmithKlineTerminatedMuscular DystrophiesFrance, Bulgaria, Denmark, Germany, Belgium, Canada, Spain, Turkey, United Kingdom, Korea, Republic of, Brazil, Netherlands, Italy, Japan, Czech Republic, Chile, Israel, Hungary, Russian Federation, Australia, Poland, Norway, Argentina and more
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Northwestern UniversityCompletedBecker Muscular Dystrophy | Limb-girdle Muscular DystrophyUnited States
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Craig McDonald, MDCardero Therapeutics, Inc.Completed
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States, Canada, Argentina, Australia, Israel, Italy
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National Human Genome Research Institute (NHGRI)Completed
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Cedars-Sinai Medical CenterCompleted
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Cedars-Sinai Medical CenterCompletedBecker Muscular DystrophyUnited States
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Cedars-Sinai Medical CenterTerminatedMuscular DystrophyUnited States