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Clinical Trials on Muscular Dystrophy in United States
Total 17803 results
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Jerry R. MendellDuchenne Alliance; Milo TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Cure Rare Disease, IncUniversity of Massachusetts, WorcesterActive, not recruiting
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Craig McDonald, MDCardero Therapeutics, Inc.Completed
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University of FloridaEngage Health Inc.CompletedDuchenne Muscular DystrophyUnited States
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University of FloridaCureDuchenneCompletedMuscular Dystrophy, DuchenneUnited States
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University of FloridaUnited States Department of DefenseCompletedDuchenne Muscular DystrophyUnited States
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Jerry R. MendellEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedDuchenne Muscular DystrophyUnited States
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Boston Children's HospitalBeth Israel Deaconess Medical CenterCompletedDuchenne Muscular DystrophyUnited States
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular Dystrophy (FSHD)United States, France, Italy
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National Institute of Neurological Disorders and...CompletedMuscular Dystrophy | Muscular DiseaseUnited States
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Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedLimb-Girdle Muscular DystrophyUnited States
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Avidity Biosciences, Inc.CompletedMyotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy Type 1 (DM1) | Myotonic Dystrophy 1 | Myotonic Muscular Dystrophy | DM1 | Dystrophy Myotonic | Steinert DiseaseUnited States
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Astellas Pharma IncTerminatedDuchenne Muscular Dystrophy (DMD)United States
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aTyr Pharma, Inc.CompletedLimb-Girdle Muscular Dystrophies | Facioscapulohumeral Muscular DystrophyUnited States, Denmark, France
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Cedars-Sinai Medical CenterCompleted
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PTC TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Cedars-Sinai Medical CenterCompletedBecker Muscular DystrophyUnited States
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Cedars-Sinai Medical CenterTerminatedMuscular DystrophyUnited States
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Cedars-Sinai Medical CenterParent Project Muscular DystrophyCompleted
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Cedars-Sinai Medical CenterCompleted
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Cedars-Sinai Medical CenterMuscular Dystrophy AssociationCompleted
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National Center for Research Resources (NCRR)Children's National Research InstituteCompletedMuscular Dystrophy, DuchenneUnited States
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REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Edgewise Therapeutics, Inc.Medpace, Inc.CompletedBecker Muscular DystrophyUnited States
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Kevin FlaniganSarepta Therapeutics, Inc.Completed
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Kevin FlaniganActive, not recruitingDuchenne Muscular DystrophyUnited States
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Solid Biosciences Inc.CompletedDuchenne Muscular DystrophyUnited States
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Megan WaldropAudentes TherapeuticsActive, not recruitingDuchenne Muscular DystrophyUnited States
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Roxanna Marie BendixenTerminatedDuchenne Muscular DystrophyUnited States
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Craig McDonald, MDCardero Therapeutics, Inc.CompletedBecker Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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University of FloridaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)Completed
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National Human Genome Research Institute (NHGRI)CompletedDuchenne Muscular DystrophyUnited States
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Nationwide Children's HospitalCompletedDuchenne Muscular DystrophyUnited States
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Nationwide Children's HospitalAsklepios Biopharmaceutical, Inc.CompletedDuchenne Muscular DystrophyUnited States
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National Institute of Neurological Disorders and...TerminatedMyotonic Dystrophy Type-1 | Myotonic Dystrophy Type-2United States
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular DystrophyUnited States, Italy, Netherlands
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University of Kansas Medical CenterNational Institutes of Health (NIH)CompletedFacioscapulohumeral Muscular DystrophyUnited States
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Children's National Research InstituteFoundation to Eradicate DuchenneActive, not recruitingDuchenne Muscular DystrophyUnited States
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University of North Carolina, Chapel HillNational Institute of Neurological Disorders and Stroke (NINDS)CompletedMuscular Dystrophy, DuchenneUnited States
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Cooperative International Neuromuscular Research...Completed
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Rare Disease Research, LLCSarepta Therapeutics, Inc.TerminatedDuchenne Muscular DystrophyUnited States
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Cedars-Sinai Medical CenterCompleted
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Washington University School of MedicineBoston Children's Hospital; University of California, Davis; University of Minnesota and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States
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CureDuchenneRecruitingDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States
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Hope Biosciences Stem Cell Research FoundationHope BiosciencesNo longer availableCongenital Muscular Dystrophy Due to Lamin A/C MutationUnited States
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Sarepta Therapeutics, Inc.CompletedMuscular Dystrophy, DuchenneUnited States
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The Emmes Company, LLCJain Foundation; Coalition to Cure Calpain 3 (C3)Terminated
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Benitec Biopharma, Inc.RecruitingOculopharyngeal Muscular DystrophyUnited States
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University of FloridaCompleted