- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Myasthenic+Syndromes%2C+Congenital
Total 2422 results
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Shriners Hospitals for ChildrenThe University of Texas Health Science Center, Houston; Oregon Health and Science... and other collaboratorsUnknownMarfan Syndrome | Marfan Related Disorders | Control SubjectsUnited States
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Quoin PharmaceuticalsRecruitingNetherton SyndromeUnited States
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Children's Healthcare of AtlantaTerminatedDiGeorge Syndrome | Congenital Heart DefectsUnited States
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Quoin PharmaceuticalsRecruitingNetherton SyndromeUnited States
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Sixera PharmaRecruitingNetherton SyndromeFrance
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University Hospital, ToulouseMedSharingRecruiting
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Children's Hospital of PhiladelphiaNovartis PharmaceuticalsCompletedNetherton SyndromeUnited States
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Assistance Publique - Hôpitaux de ParisCompleted
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Boston Scientific CorporationCompletedHeart Failure | Long QT Syndrome | Wide QRS Complexes | Cardiac ResynchronisationUnited Kingdom
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Masonic Cancer Center, University of MinnesotaNational Marrow Donor ProgramCompletedSickle Cell Disease | Thalassemia | Severe Congenital Neutropenia | Diamond-Blackfan Anemia | Shwachman-Diamond SyndromeUnited States
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October 6 UniversityCompletedCubital Tunnel Syndrome | Ulnar Nerve Entrapment at Elbow | Ulnar Nerve Compression | Ulnar Nerve Entrapment SyndromeEgypt
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Beijing Anzhen HospitalRecruitingHypoplastic Left Heart Syndrome | Aortic Coarctation | Atrial Septal AneurysmChina
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Centre Hospitalier Universitaire Saint PierreUniversité Libre de BruxellesWithdrawnNerve Entrapment Syndrome | Cluneal SyndromeBelgium
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Children's Hospital of PhiladelphiaNational Heart, Lung, and Blood Institute (NHLBI)Active, not recruiting
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University of AlbertaWomen and Children's Health Research Institute, CanadaCompletedHypoplastic Left Heart SyndromeCanada
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National Institute on Aging (NIA)CompletedMarfan Syndrome | Ehlers-Danlos Syndrome | Stickler SyndromeUnited States
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Azitra Inc.Not yet recruiting
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Daiichi SankyoRecruiting
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Boehringer IngelheimRecruitingNetherton SyndromeBelgium, United Kingdom, Australia, Germany, China, Malaysia, United States, Japan, France, Israel, Bulgaria, Italy, Switzerland, Austria, Netherlands, Portugal
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Great Ormond Street Hospital for Children NHS Foundation...Unknown
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Medisch Spectrum TwenteMedical School Medisch Spectrum Twente; Techmed University of Twente; Erasmus...RecruitingMesenteric Ischemia | Median Arcuate Ligament Syndrome | Dunbar Syndrome | Coeliac Artery Compression | Celiac Artery Compression SyndromeNetherlands
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Institut Jerome LejeuneFondation Jérôme LejeuneCompletedObstructive Sleep Apnea Syndrome | Down SyndromeFrance
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National Human Genome Research Institute (NHGRI)CompletedMarfan Syndrome | Connective Tissue Disease | Ehlers Danlos Syndrome | Dissecting Aneurysm | Nail Patella SyndromeUnited States
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Tang-Du HospitalRecruitingMyasthenia Gravis | ThymectomyChina
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Longeveron Inc.Active, not recruiting
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SanofiActive, not recruitingUsher's SyndromeUnited States, France
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National Cancer Institute (NCI)RecruitingFanconi Anemia | Inherited Bone Marrow Failure SyndromeUnited States
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University Hospital, ToursCompletedPort Wine Stain | Parkes Weber Syndrome | Klippel Trenaunay SyndromeFrance
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Children's Hospital of Eastern OntarioThe Physicians' Services Incorporated FoundationCompletedCerebral Palsy | Neuromuscular Diseases | Chronic Pain | Physical Disability | Concussion Post Syndrome | Congenital Heart DefectCanada
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Fondazione IRCCS Ca' Granda, Ospedale Maggiore...Federico II University; Istituto Auxologico Italiano; Università degli Studi...RecruitingBeckwith-Wiedemann SyndromeItaly
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King's College LondonCompletedMyelodysplastic Syndromes | Leukemia, Myeloid, AcuteUnited Kingdom
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Centre Hospitalier Universitaire de Saint EtienneEnrolling by invitationStroke | Apnea SyndromeFrance
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Centre Hospitalier Universitaire de NīmesCompleted22q11 Deletion Syndrome Di George SyndromeFrance
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Cystinosis Research FoundationUnknownCystinosis | Nephropathic Cystinosis | Renal Fanconi SyndromeUnited States
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Universitaire Ziekenhuizen KU LeuvenUnknownAnophthalmos; Acquired | Anophthalmic Socket SyndromeBelgium
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National Human Genome Research Institute (NHGRI)CompletedProteus SyndromeUnited States
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University Hospital, ToulouseRecruiting
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University Hospital, ToulouseCompleted
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SanofiCompleted
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Institut National de la Santé Et de la Recherche...UnknownHealthy | Netherton SyndromeFrance
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Boston Children's HospitalLitron LaboratoriesCompletedHeterotaxy SyndromeUnited States
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University of UtahWithdrawnThoracic Insufficiency Syndrome | TISUnited States
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Peter MacCallum Cancer Centre, AustraliaNational Health and Medical Research Council, Australia; University of MelbourneRecruitingHematologic Diseases | Inherited Platelet Disorder | Inherited BMF SyndromeAustralia
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CelgeneCompletedMyelodysplastic Syndromes | Beta-thalassemiaAustria
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National Human Genome Research Institute (NHGRI)Recruiting
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Stephan EliezRecruitingtACS | 22Q11 Deletion SyndromeSwitzerland
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Zynerba Pharmaceuticals, Inc.Completed22Q Deletion SyndromeUnited States, Australia
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National Institute of Mental Health (NIMH)CompletedDiGeorge Syndrome | Velocardiofacial Syndrome | 22q11.2 SyndromeUnited States
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Massachusetts General HospitalBoston University; Mayo Clinic; Beth Israel Deaconess Medical Center; The Cleveland... and other collaboratorsTerminatedLong qt Syndrome | Torsade de PointesUnited States