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Clinical Trials on Myasthenic Syndromes, Congenital in United Kingdom
Total 16766 results
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UK Kidney AssociationRecruitingVasculitis | AL Amyloidosis | Tuberous Sclerosis | Fabry Disease | Cystinuria | Focal Segmental Glomerulosclerosis | IgA Nephropathy | Bartter Syndrome | Pure Red Cell Aplasia | Membranous Nephropathy | Atypical Hemolytic Uremic Syndrome | Autosomal Dominant Polycystic Kidney Disease | Cystinosis | Nephronophthisis | BK Nephropathy and other conditionsUnited Kingdom
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University Hospitals of North Midlands NHS TrustCompletedAtrial Septal Defect | Heart Septal Defects, Atrial | Foramen Ovale, PatentUnited Kingdom
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ResMedImperial College London; Royal Brompton & Harefield NHS Foundation TrustCompletedHeart Failure | Sleep Apnea SyndromesUnited Kingdom
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Palvella Therapeutics, Inc.RecruitingBCCs in Gorlin Syndrome PatientsUnited States, United Kingdom
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Western Sussex Hospitals NHS TrustUnknown
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Hoffmann-La RocheCompleted
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GenethonActive, not recruitingWiskott-Aldrich SyndromeUnited Kingdom, France
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Rare Diseases... and other collaboratorsTerminatedAndersen-Tawil SyndromeUnited States
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AlbireoActive, not recruitingAlagille SyndromeUnited Kingdom, United States, France, Germany, Netherlands, Italy, Belgium, Malaysia, Poland, Turkey
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The Leeds Teaching Hospitals NHS TrustCompleted
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Joanne Kurtzberg, MDAldagenCompletedAnemia, Aplastic | MDS | Inborn Errors of Metabolism | Congenital Marrow Failure | Congenital Immunodeficiency SyndromeUnited States
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Embody Orthopaedic LimitedImperial College LondonActive, not recruitingHip Dysplasia | Hip Osteoarthritis | Hip NecrosisUnited Kingdom
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St. George's Hospital, LondonCompletedThoracic Aortic Aneurysm | Bicuspid Cardiac ValveUnited Kingdom
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K2M, Inc.WithdrawnAdolescent Idiopathic ScoliosisUnited Kingdom
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University of RochesterWithdrawnObstructive Sleep Apnea Syndrome | Hypoplastic Left Heart Syndrome | Single Ventricle PhysiologyUnited States
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Mayo ClinicRecruitingHypoplastic Left Heart Syndrome (HLHS)United States
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St George's, University of LondonUniversity College London HospitalsUnknownPeripheral Neuropathy | CMT - Charcot-Marie-Tooth Disease | Hereditary Peripheral Neuropathy | CMT1AUnited Kingdom
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University of NebraskaRecruitingUpper Extremity Deformities, Congenital | Amniotic Band SyndromeUnited States
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University of NottinghamMedical Research Council; National Institute for Health Research, United KingdomRecruitingFrail Elderly Syndrome | Frailty | Frailty SyndromeUnited Kingdom
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University College, LondonMoorfields Eye Hospital NHS Foundation Trust; Targeted Genetics CorporationCompletedRetinal DegenerationUnited Kingdom
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National Institute of Allergy and Infectious Diseases...Completed
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GlaxoSmithKlineWithdrawnAutoimmune DiseasesUnited Kingdom
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Cardiff UniversityUniversity of CanterburyRecruitingCleft Lip and Palate | Parenting | Neurofibromatoses | Skin Condition | Alopecia | Craniofacial | Limb DifferenceUnited Kingdom
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Hussain KaziCompletedOsteoarthritis | Rheumatoid Arthritis | Avascular Necrosis | Developmental Dysplasia of the HipUnited Kingdom
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Gilead SciencesCompletedHIV InfectionsUnited Kingdom
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Prof. Janet DunnKing's College Hospital NHS Trust; University of Manchester; University of Birmingham and other collaboratorsRecruitingMyelodysplastic Syndromes (MDS)United Kingdom
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University of NebraskaWithdrawnUpper Extremity Deformities, Congenital | Amniotic Band SyndromeUnited States
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Kyowa Kirin, Inc.TerminatedAcute Myeloid Leukemia | Myelodysplastic SyndromeUnited Kingdom
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DNage B.V.TerminatedCockayne SyndromeUnited States, France, United Kingdom
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UCSF Benioff Children's Hospital OaklandNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Medical... and other collaboratorsCompletedSickle Cell Disease | Thalassemia | Diamond-Blackfan AnemiaUnited States, United Kingdom, Germany
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Blackpool Teaching Hospitals NHS Foundation TrustNot yet recruitingShoulder Subacromial Pain SyndromeUnited Kingdom
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Cardiff and Vale University Health BoardSouth East Wales Trials Unit (SEWTU); TenovusCompletedAnterior Resection SyndromeUnited Kingdom
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Cell Medica LtdUniversity College, London; Cell Therapy CatapultCompletedMyelodysplastic Syndromes (MDS) | Acute Myeloid Leukaemia (AML)United Kingdom, Germany, Belgium
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Mirati Therapeutics Inc.TerminatedAcute Myeloid Leukemia (AML) | Myelodysplastic Syndrome (MDS)United States, Canada, United Kingdom
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The Whiteley ClinicBauerfeindRecruitingPelvic Congestive SyndromeUnited Kingdom
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Gilead SciencesCompleted
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Duke UniversityPatient-Centered Outcomes Research Institute; Beth Israel Deaconess Medical...CompletedAutoimmune Diseases | Neurological DisorderUnited States, Canada
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PENTA FoundationCompleted
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Chelsea and Westminster NHS Foundation TrustMerck Sharp & Dohme LLC; Imperial College London; University of LiverpoolCompletedHuman Immunodeficiency VirusUnited Kingdom
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Guy's and St Thomas' NHS Foundation TrustVeryan Medical Ltd.RecruitingPost Thrombotic SyndromeUnited Kingdom
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Indiana UniversityRecruitingCongenital Heart Defects | Heterotaxy SyndromeUnited States
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NHS LothianUniversity of EdinburghRecruitingHip Dysplasia | Hip Osteoarthritis | Hip Arthropathy | Arthritis of HipUnited Kingdom
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University College, LondonSociety for Cardiothoracic Surgery in Great Britain & Ireland; British Congenital...Unknown
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Everett MeyerCompletedLeukemia, Myeloid | Myeloproliferative Disorders | Anemia | Neural Tube Defects | Myelodysplastic Syndromes (MDS) | Bone Marrow Transplant FailureUnited States
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St. Bartholomew's HospitalUnknownMyelodysplastic Syndromes | Leukemia | Infection | Graft Versus Host Disease | Myelodysplastic/Myeloproliferative NeoplasmsUnited Kingdom
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Baxalta now part of ShireCompletedCongenital Thrombotic Thrombocytopenic PurpuraUnited States, United Kingdom
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Mauro H. SchenoneNot yet recruitingHypoplastic Left Heart SyndromeUnited States
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Medical College of WisconsinChildren's Hospital and Health System Foundation, WisconsinCompletedHypoplastic Left Heart SyndromeUnited States
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Radboud University Medical CenterRecruitingMyelodysplastic Syndromes (MDS)Denmark, Switzerland, Serbia, Austria, Croatia, Czechia, France, Germany, Greece, Israel, Italy, Netherlands, Poland, Portugal, Romania, Spain, Sweden, United Kingdom
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Resolve TherapeuticsNewcastle-upon-Tyne Hospitals NHS Trust; University Hospital BirminghamCompletedSjogren's SyndromeUnited Kingdom