- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Myopathy Congenital
Total 9155 results
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Universidade Estadual do Oeste do ParanáCompletedIntensive Care (ICU) Myopathy | Functional Independence
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Ultragenyx Pharmaceutical IncCompletedGNE Myopathy | Hereditary Inclusion Body Myopathy (HIBM)United States, Israel
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Sándor BeniczkyUniversity of Aarhus; Danish Council for Independent Research; Søster og Verner...CompletedCritical Illness Myopathy | Myopathy Critical IllnessDenmark
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Jose Alberola-RubioCompletedPelvic Pain | Pelvic Floor Disorders | Pelvic Pain Syndrome | Electromyography | EMG Syndrome | EMG: Myopathy | ElectroPhys: MyopathySpain
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Astellas Pharma IncActive, not recruitingPrimary Mitochondrial MyopathyUnited States
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Hartford HospitalUniversity of ConnecticutUnknown
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Translational Research Center for Medical Innovation...TerminatedPrimary Triglyceride Deposit Cardiomyovasculopathy (TGCV) | Neutral Lipid Storage Disease With Myopathy (NLSD-M)Italy, Japan
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University of WashingtonGrifols Biologicals, LLCWithdrawnImmune-Mediated Necrotizing MyopathyUnited States
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Northwell HealthHoffmann-La Roche; New York Presbyterian Hospital; University of Medicine and...CompletedCongenital Urological AbnormalitiesUnited States
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National Human Genome Research Institute (NHGRI)National Center for Advancing Translational Sciences (NCATS); Therapeutics...CompletedGNE Myopathy | Hereditary Inclusion Body Myopathy (HIBM)United States
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Central Hospital, Nancy, FranceUnknown
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Izmir Katip Celebi UniversityUnknownFunctional Disturbance | Intensive Care (ICU) MyopathyTurkey
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Northwestern UniversityTerminated
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Rigshospitalet, DenmarkUniversity of CopenhagenCompletedIntensive Care (ICU) MyopathyDenmark
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University of ManchesterKing's College Hospital NHS Trust; Northern Care Alliance NHS Foundation Trust and other collaboratorsActive, not recruitingMyositis | Idiopathic Inflammatory MyopathyUnited Kingdom
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Newcastle UniversityUnknownHereditary Inclusion Body Myopathy | GNE MyopathyUnited Kingdom
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Tohoku UniversityCompletedHereditary Inclusion Body Myopathy | Nonaka MyopathyJapan
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Peking University People's HospitalUnknownInflammatory Myopathy
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Eduardo N. ChiniRecruitingMitochondrial MyopathyUnited States
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University of HelsinkiHelsinki University Central Hospital; University of Iowa; Institute for Molecular...CompletedMitochondrial Myopathies
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Guy's and St Thomas' NHS Foundation TrustUniversity College, London; The Whittington Hospital NHS TrustCompleted
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University of Sao PauloRecruitingNeurologic Manifestations | Myopathy | ElectroPhys: MyopathyBrazil
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Peking University People's HospitalUnknown
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Radboud University Medical CenterUnknownMyotonic Dystrophy Type 2 | McArdle Disease | Nemaline Myopathy Type 6
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Reata, a wholly owned subsidiary of BiogenAbbVieCompletedMItochondrial MyopathiesUnited States, Denmark
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Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy | GNE MyopathyUnited States, Israel
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Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy (HIBM)United States
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National Institute of Nursing Research (NINR)Not yet recruitingRyanodine Receptor 1-Related Myopathy | Ryanodine Receptor 1 Related DisordersUnited States
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Centre Hospitalier Universitaire de NiceRecruitingMitochondrial MyopathiesFrance
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University of HelsinkiHelsinki University Central Hospital; Institute for Molecular MedicineCompletedMitochondrial MyopathiesFinland
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National Institute of Arthritis and Musculoskeletal...UnknownMitochondrial MyopathyUnited States
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Academisch Medisch Centrum - Universiteit van Amsterdam...Princess Beatrix Muscle FoundationRecruitingMyositis | Dermatomyositis | Polymyositis | Antisynthetase Syndrome | Immune-Mediated Necrotizing Myopathy | Inflammatory Myopathy, IdiopathicNetherlands
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Guy's and St Thomas' NHS Foundation TrustCompleted
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Stealth BioTherapeutics Inc.CompletedMitochondrial MyopathyUnited States
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Children's Hospital of PhiladelphiaNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMitochondrial Diseases | Mitochondrial MyopathiesUnited States
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Rigshospitalet, DenmarkCompletedMitochondrial Myopathies | Healthy ControlsDenmark
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argenxRecruitingMyositis | Dermatomyositis | Polymyositis | Antisynthetase Syndrome | Immune-Mediated Necrotizing Myopathy | Active Idiopathic Inflammatory MyopathyUnited States, Germany, Spain, Korea, Republic of, Austria, Turkey, Lithuania, Australia, Thailand, Serbia, Poland, Italy, France, Netherlands, Argentina, United Kingdom, Georgia, Belgium, Bulgaria, Canada, Cyprus, Denmark, Greece, Hu... and more
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Cristina Domínguez GonzálezRecruiting
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Assistance Publique - Hôpitaux de ParisTerminatedSelenoprotein N-related MyopathyFrance
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Rigshospitalet, DenmarkCompletedMitochondrial Myopathies | Fatty Acid Oxidation DefectsDenmark
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argenxRecruitingMyositis | Dermatomyositis | Polymyositis | Antisynthetase Syndrome | Immune-Mediated Necrotizing Myopathy | Active Idiopathic Inflammatory MyopathyKorea, Republic of, United States, Bulgaria, Belgium, Denmark, Georgia, Greece, Lithuania, Argentina
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Children's Hospital of PhiladelphiaUniversity of Pennsylvania; United Mitochondrial Disease Foundation (UMDF)Recruiting
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Technical University of MunichCharite University, Berlin, Germany; Helmholtz Zentrum MünchenRecruitingCritical Illness | Muscle Weakness | Critical Illness Myopathy | Critical Care | Critical Illness Polyneuropathy | Metabolomics | Intensive Care (ICU) MyopathyGermany
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Mads Peter Godtfeldt StemmerikRecruiting
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Technical University of MunichHelmholtz Zentrum MünchenCompletedCritical Illness | Muscle Weakness | Critical Illness Myopathy | Critical Care | Critical Illness Polyneuropathy | Metabolomics | Intensive Care (ICU) MyopathyGermany
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Università degli Studi di BresciaUnknownCritical Illness Myopathy | Critical Illness PolyneuropathyItaly
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The First Affiliated Hospital with Nanjing Medical...Not yet recruitingCardiac Disease | Inflammatory Myopathy
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Cabaletta BioRecruitingIdiopathic Inflammatory Myopathy | Dermatomyositis | Immune-Mediated Necrotizing Myopathy | Anti-Synthetase SyndromeUnited States
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Barts & The London NHS TrustQueen Mary University of LondonCompletedSurgery | Critical Illness Myopathy | Aortic Diseases | Intensive Care Unit Syndrome | Intensive Care (ICU) Myopathy | Intensive Care NeuropathyUnited Kingdom