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Clinical Trials on N-Acetylneuraminic Acid Storage Disease
Total 8519 results
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SanofiRecruitingGlycogen Storage Disease Type IIBelgium, United States, Italy, Spain, Taiwan, United Kingdom, Netherlands, France, Germany
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Genzyme, a Sanofi CompanyActive, not recruitingGlycogen Storage Disease Type IIFrance
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type IIChina
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Duke UniversityNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedGlycogen Storage Disease Type IIUnited States
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Columbia UniversityWithdrawnGlycogen Storage Disease Type IIUnited States
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Genzyme, a Sanofi CompanyActive, not recruiting
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Centre Hospitalier de CayenneCompleted
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Southeast University, ChinaZhongda Hospital; Chinese Nutrition SocietyActive, not recruitingMetabolic Diseases | Dyslipidemias | Oxidative Stress | Immune System Disorder | Fatty Acid Metabolism DisorderChina
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Nationwide Children's HospitalActive, not recruiting
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University of AarhusActive, not recruitingHeart Failure | Ketosis | KetonemiaDenmark
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Centre Hospitalier de CayenneCompleted
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Serhat Gumrukcu, MD PhDFrida Therapeutics LLCRecruiting
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Amicus TherapeuticsAvailable
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Duke UniversityCompleted
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Duke UniversityGenzyme, a Sanofi CompanyCompleted
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Duke UniversityCompletedPompe DiseaseUnited States
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Duke UniversityCompleted
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Dwight Koeberl, M.D., Ph.D.Completed
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University of California, IrvineGenzyme, a Sanofi CompanyCompletedPompe DiseaseUnited States
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Amicus TherapeuticsTerminated
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University of FloridaTerminated
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O & O Alpan LLCCompleted
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Genzyme, a Sanofi CompanyCompleted
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type IIUnited States, France, Netherlands
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National Taiwan University HospitalUnknown
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Children's Healthcare of AtlantaTerminatedCongenital Disorders
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Medical University of GrazCompletedHealthy | Oxidative Stress | Vitamin B 12 Deficiency | Polyphenols | Thiamine and Niacin Deficiency States | Pyridoxine Deficiency | Folic Acid Deficiency Anemia, Dietary | Peroxidase; Defect | Homocystine; Metabolic DisorderAustria
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Thomas KanderCompletedBleeding | Trauma | Hypothermia | AcidosisSweden
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Ai PengUnknown
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Duke UniversityWithdrawnHypoxia | Lactic AcidosisUnited States
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Meir Medical CenterCompletedFolic Acid Deficiency | Vitamin B12 DeficiencyIsrael
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Makerere UniversityCompletedCompare Blood Age for TransfusionUganda
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University of FloridaWithdrawnKetosis | Gastrointestinal Infections
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University of CincinnatiWithdrawnCardiovascular Disease | Morbid Obesity | Fatty Acid LevelsUnited States
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University Hospital, ToulouseInstitut Claudius RegaudRecruitingCervical Cancer TNM Staging Regional Lymph Nodes (N)France
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Fresenius KabiNot yet recruitingMalnutrition | Pediatric ALL | Essential Fatty Acid Deficiency | Parenteral Nutrition Associated Liver Disease (PNALD)
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Amicus TherapeuticsRecruitingPompe DiseaseUnited States, Germany
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Duke UniversitySanofiRecruiting
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Duke UniversityGenzyme, a Sanofi CompanyRecruitingPompe DiseaseUnited States
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Genzyme, a Sanofi CompanyCompleted
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Valerion Therapeutics, LLCTerminatedPompe DiseaseUnited States, United Kingdom
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University of FloridaNational Heart, Lung, and Blood Institute (NHLBI)CompletedPompe DiseaseUnited States
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BioMarin PharmaceuticalCompletedPompe DiseaseUnited States, United Kingdom, France, Australia, Germany
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BioMarin PharmaceuticalTerminatedPompe DiseaseUnited States, United Kingdom, Australia, France, Germany, New Zealand
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University of FloridaCompletedPompe DiseaseUnited States
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National Taiwan University HospitalUnknown
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Genzyme, a Sanofi CompanyTerminatedPompe DiseaseUnited States
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Pompe DiseaseUnited States