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- US Clinical Trials Registry
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Clinical Trials on NPC Multiplex Families
Total 9781 results
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BiogenCompletedRelapsing-Remitting Multiple SclerosisIreland
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Mitsubishi Tanabe Pharma CorporationCompletedRelapsing-remitting Multiple SclerosisUnited Kingdom
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Mitsubishi Tanabe Pharma CorporationCompleted
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Mitsubishi Tanabe Pharma CorporationCompletedRelapsing-remitting Multiple SclerosisUnited Kingdom
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First Affiliated Hospital Xi'an Jiaotong UniversityRecruitingHomozygous Familial HypercholesterolemiaChina
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Beijing Suncadia Pharmaceuticals Co., LtdNot yet recruitingHomozygous Familial Hypercholesterolemia
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Organon and CoCompletedHypercholesterolemia | Heterozygous Familial Hypercholesterolemia
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Novartis PharmaceuticalsActive, not recruitingFamilial Hypercholesterolemia - HeterozygousUnited States, Germany, South Africa, Greece, Italy, Czechia, Taiwan, Slovakia, Turkey, France, Russian Federation, Canada, Spain, Jordan, Switzerland, Hungary, Poland, Netherlands, Norway, United Kingdom, Lebanon, Argentina, Brazil, ... and more
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Arrowhead PharmaceuticalsActive, not recruitingHomozygous Familial HypercholesterolemiaAustralia, Canada, United States, South Africa
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Novartis PharmaceuticalsCompletedHypercholesterolemia | Heterozygous Familial HypercholesterolemiaJapan
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AkesoAD Pharmaceuticals Co., Ltd.CompletedHomozygous Familial HypercholesterolemiaChina
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AmgenCompletedHeterozygous Familial HypercholesterolemiaUnited States, Canada, Italy, Norway, Belgium, Turkey, Australia, New Zealand, Austria, Czechia, South Africa, Poland, Spain, Switzerland, Netherlands, Taiwan, Finland, Brazil, Portugal, Slovenia, Russian Federation, Hungary, United... and more
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.TerminatedFamilial Partial LipodystrophyUnited States, Netherlands, Belgium, Brazil, Canada, Germany, Russian Federation
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Regeneron PharmaceuticalsSanofiCompletedHomozygous Familial HypercholesterolemiaUnited States, South Africa, Canada, Greece, Japan, Ukraine, Austria, Czechia, France, Germany, Italy, Taiwan, Turkey
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, Australia, Austria, Canada, France, Greece, Italy, Japan, South Africa, Ukraine
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Austrian Academic Institute for Clinical NutritionMedical University of ViennaCompletedHeterozygous Familial HypercholesterolemiaAustria
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Aegerion Pharmaceuticals, Inc.WithdrawnHomozygous Familial Hypercholesterolemia
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Merck Sharp & Dohme LLCCompletedHeterozygous Familial Hypercholesterolemia (HeFH)
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Cerenis Therapeutics, SACompleted
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Brno University HospitalRecruiting
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W.L.Gore & AssociatesActive, not recruitingMultiple PathologiesAustralia, Italy, United States, Brazil
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Cairo UniversityRiyadh Fertility and Reproductive Health centerCompleted
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University of California, Los AngelesRecruitingPrimary Progressive Multiple Sclerosis | Secondary Progressive Multiple SclerosisUnited States
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University College DublinCompletedPrimary Progressive Multiple Sclerosis | Secondary Progressive Multiple SclerosisIreland
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Innate ImmunotherapeuticsNational Multiple Sclerosis Society; Primorus Clinical TrialsCompletedPrimary Progressive Multiple Sclerosis | Secondary Progressive Multiple SclerosisNew Zealand
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Novartis PharmaceuticalsRecruitingHypercholesterolaemia | Familial HypercholesterolaemiaJapan
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AmgenCompletedFamilial HypercholesterolemiaCanada, Italy, Norway, Belgium, United States, Turkey, Australia, Austria, South Africa, Poland, Switzerland, Spain, Portugal, Slovenia, Brazil, Russian Federation, Hungary, United Kingdom, Colombia, Czechia, Netherlands, Greece, Ma...
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, South Africa, Australia, Austria, Canada, Czechia, France, Greece, Italy, Japan, Ukraine
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Shanghai Junshi Bioscience Co., Ltd.CompletedHeterozygous Familial HypercholesterolemiaChina
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Mirum Pharmaceuticals, Inc.CompletedProgressive Familial Intrahepatic Cholestasis (PFIC)United States, United Kingdom, Poland, France
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Daniel GaudetUltragenyx Pharmaceutical IncActive, not recruitingSafety and Effectiveness of Evinacumab for the Treatment of Homozygous Familial HypercholesterolemiaHomozygous Familial HypercholesterolemiaCanada
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Innovent Biologics (Suzhou) Co. Ltd.Completed
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Amryt PharmaActive, not recruitingHomozygous Familial Hypercholesterolaemia (HoFH)Germany, Israel, Italy, Saudi Arabia, Spain, Tunisia
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AkesoAD Pharmaceuticals Co., Ltd.CompletedHeterozygous Familial HypercholesterolemiaChina
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Nantes University HospitalCompletedFamilial HypobetalipoproteinemiaFrance
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Nantes University HospitalCompletedStudy of cardiovAscular Contrasted Phenotypes in Patients With FamIliaI hypercholesteRolemia (SAFIR)Homozygous Familial HypercholesterolemiaFrance
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The Medicines CompanyCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, South Africa
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, Canada
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Madrigal Pharmaceuticals, Inc.CompletedHeterozygous Familial HypercholesterolemiaDenmark
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Central South UniversityCompletedHomozygous Familial HypercholesterolemiaChina
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CymaBay Therapeutics, Inc.CompletedHomozygous Familial HypercholesterolemiaCanada, France, Netherlands, Norway
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Merck Sharp & Dohme LLCTerminatedHyperlipoproteinemia Type II | Homozygous Familial Hypercholesterolemia
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Oslo University HospitalUniversity of Oslo; Sunnaas Rehabilitation Hospital; South-Eastern Norway Regional...RecruitingTrauma Injury | Trauma, Multiple | PolytraumaNorway
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Centre Hospitalier de CornouailleCompletedOrgan Failure, MultipleFrance
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NovartisCompletedClinically Isolated Syndrome | Relapsing Multiple Sclerosis | Relapsing Remitting Multiple Sclerosis | Secondary Progressive Multiple SclerosisUnited States
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Association de Recherche Bibliographique pour les...Centre Hospitalier Universitaire de Nice; Centre Hospitalier Princesse GraceCompletedHealthy | Clinically Isolated Syndrome | Multiple Sclerosis (MS) | Radiologically Isolated Syndrome | Multiple Sclerosis (MS) Relapsing Remitting | Multiple Sclerosis (MS) Primary Progressive | Multiple Sclerosis (MS) Secondary ProgressiveMonaco
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Karolinska University HospitalUnknownDefect of Skull Ossification | Other Specified Skull or Face Bone Anomaly | Cranial Dysostosis Nec | HemicraniectomySweden
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IMS HEALTH GmbH & Co. OHGEMD SeronoCompletedRelapsing-remitting Multiple SclerosisUnited States, Canada
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BayerCompletedRelapsing Remitting Multiple Sclerosis (RRMS)China, Slovakia, France, Germany, Korea, Republic of, Saudi Arabia, Singapore, Sweden, Taiwan, Colombia, Czech Republic, Estonia, Italy, Jordan, Lebanon, Mexico, Slovenia, United Kingdom, Argentina, Bahrain, Egypt, United Arab Emirates and more
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Texas Tech UniversityNational Center for Complementary and Integrative Health (NCCIH)CompletedMultiple Drug UseUnited States