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- US Clinical Trials Registry
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Clinical Trials on Nemaline Myopathy
Total 388 results
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Northwestern UniversityTerminated
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Rigshospitalet, DenmarkUniversity of CopenhagenCompletedIntensive Care (ICU) MyopathyDenmark
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DynacureWithdrawnCentronuclear MyopathyGermany, France
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University of ManchesterKing's College Hospital NHS Trust; Northern Care Alliance NHS Foundation Trust and other collaboratorsActive, not recruitingMyositis | Idiopathic Inflammatory MyopathyUnited Kingdom
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Valerion Therapeutics, LLCInstitut de Myologie, France; GenethonCompletedMyotubular MyopathyFrance, Belgium, United States, Canada, Germany, Italy, Spain
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Newcastle UniversityUnknownHereditary Inclusion Body Myopathy | GNE MyopathyUnited Kingdom
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Tohoku UniversityCompletedHereditary Inclusion Body Myopathy | Nonaka MyopathyJapan
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Peking University People's HospitalUnknownInflammatory Myopathy
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Eduardo N. ChiniRecruitingMitochondrial MyopathyUnited States
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University of HelsinkiHelsinki University Central Hospital; University of Iowa; Institute for Molecular...CompletedMitochondrial Myopathies
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Guy's and St Thomas' NHS Foundation TrustUniversity College, London; The Whittington Hospital NHS TrustCompleted
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University of Sao PauloRecruitingNeurologic Manifestations | Myopathy | ElectroPhys: MyopathyBrazil
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Peking University People's HospitalUnknown
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Reata, a wholly owned subsidiary of BiogenAbbVieCompletedMItochondrial MyopathiesUnited States, Denmark
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Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy (HIBM)United States
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Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy | GNE MyopathyUnited States, Israel
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National Institute of Nursing Research (NINR)Not yet recruitingRyanodine Receptor 1-Related Myopathy | Ryanodine Receptor 1 Related DisordersUnited States
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Centre Hospitalier Universitaire de NiceRecruitingMitochondrial MyopathiesFrance
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University of HelsinkiHelsinki University Central Hospital; Institute for Molecular MedicineCompletedMitochondrial MyopathiesFinland
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National Institute of Arthritis and Musculoskeletal...UnknownMitochondrial MyopathyUnited States
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Academisch Medisch Centrum - Universiteit van Amsterdam...Princess Beatrix Muscle FoundationRecruitingMyositis | Dermatomyositis | Polymyositis | Antisynthetase Syndrome | Immune-Mediated Necrotizing Myopathy | Inflammatory Myopathy, IdiopathicNetherlands
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Stealth BioTherapeutics Inc.CompletedMitochondrial MyopathyUnited States
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Guy's and St Thomas' NHS Foundation TrustCompleted
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Children's Hospital of PhiladelphiaNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMitochondrial Diseases | Mitochondrial MyopathiesUnited States
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Rigshospitalet, DenmarkCompletedMitochondrial Myopathies | Healthy ControlsDenmark
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argenxRecruitingMyositis | Dermatomyositis | Polymyositis | Antisynthetase Syndrome | Immune-Mediated Necrotizing Myopathy | Active Idiopathic Inflammatory MyopathyUnited States, Germany, Spain, Korea, Republic of, Austria, Turkey, Lithuania, Australia, Thailand, Serbia, Poland, Italy, France, Netherlands, Argentina, United Kingdom, Georgia, Belgium, Bulgaria, Canada, Cyprus, Denmark, Greece, Hu... and more
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Assistance Publique - Hôpitaux de ParisTerminatedSelenoprotein N-related MyopathyFrance
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Cristina Domínguez GonzálezRecruiting
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Rigshospitalet, DenmarkCompletedMitochondrial Myopathies | Fatty Acid Oxidation DefectsDenmark
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argenxRecruitingMyositis | Dermatomyositis | Polymyositis | Antisynthetase Syndrome | Immune-Mediated Necrotizing Myopathy | Active Idiopathic Inflammatory MyopathyKorea, Republic of, Thailand, United States, Bulgaria, Taiwan, Argentina, Belgium, Cyprus, Denmark, France, Georgia, Germany, Greece, Italy, Lithuania, Czechia, Sweden
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Children's Hospital of PhiladelphiaUniversity of Pennsylvania; United Mitochondrial Disease Foundation (UMDF)Recruiting
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Myotonic Dystrophy FoundationRecruitingMyotonic Dystrophy | Myotonic Dystrophy 1 | Steinert's Disease | Congenital Myotonic Dystrophy | PROMM (Proximal Myotonic Myopathy) | Steinert Disease | Dystrophia Myotonica 1 | Myotonic Dystrophy 2 | Dystrophia Myotonica | Dystrophia Myotonica 2 | Myotonia Dystrophica | Myotonic Dystrophy, Congenital | Myotonic... and other conditionsUnited States
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Technical University of MunichCharite University, Berlin, Germany; Helmholtz Zentrum MünchenRecruitingCritical Illness | Muscle Weakness | Critical Illness Myopathy | Critical Care | Critical Illness Polyneuropathy | Metabolomics | Intensive Care (ICU) MyopathyGermany
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Mads Peter Godtfeldt StemmerikRecruiting
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Technical University of MunichHelmholtz Zentrum MünchenCompletedCritical Illness | Muscle Weakness | Critical Illness Myopathy | Critical Care | Critical Illness Polyneuropathy | Metabolomics | Intensive Care (ICU) MyopathyGermany
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Università degli Studi di BresciaUnknownCritical Illness Myopathy | Critical Illness PolyneuropathyItaly
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The First Affiliated Hospital with Nanjing Medical...Not yet recruitingCardiac Disease | Inflammatory Myopathy
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Cabaletta BioRecruitingIdiopathic Inflammatory Myopathy | Dermatomyositis | Immune-Mediated Necrotizing Myopathy | Anti-Synthetase SyndromeUnited States
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Barts & The London NHS TrustQueen Mary University of LondonCompletedSurgery | Critical Illness Myopathy | Aortic Diseases | Intensive Care Unit Syndrome | Intensive Care (ICU) Myopathy | Intensive Care NeuropathyUnited Kingdom
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National Center for Research Resources (NCRR)University of RochesterCompletedMitochondrial Myopathy
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Eunice Kennedy Shriver National Institute of Child...Completed
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University Hospital, MontpellierCompleted
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Institut National de la Santé Et de la Recherche...CompletedDuchenne or Severe Becker MyopathyFrance
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National Human Genome Research Institute (NHGRI)National Center for Advancing Translational Sciences (NCATS)Completed
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National Taiwan University HospitalUnknownRhabdomyolysis | MyopathyTaiwan
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Rigshospitalet, DenmarkCompleted
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Rigshospitalet, DenmarkOdense University Hospital; University of Southern DenmarkCompletedMyositis | Dermatomyositis | Polymyositis | Immune-Mediated Necrotizing MyopathyDenmark
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Ludwig-Maximilians - University of MunichCompletedInclusion Body Myositis, Sporadic | Inclusion Body Myopathy, Autosomal-recessive | Inclusion Body Myopathy, Autosomal-dominant | Congenital Cataracts, Facial Dysmorphism, And NeuropathyGermany
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University of Sao PauloRecruiting
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Leadiant Biosciences, Inc.National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsActive, not recruiting