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Clinical Trials on Neoplastic Syndromes, Hereditary
Total 39466 results
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Washington University School of MedicineTaiho Oncology, Inc.RecruitingMyelodysplastic SyndromesUnited States
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Cardiff UniversityNovartisUnknownTuberous SclerosisUnited Kingdom
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Johns Hopkins UniversityNational Cancer Institute (NCI); Lustgarten FoundationCompletedPancreatic Neoplasm | Peutz-Jeghers SyndromeUnited States
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Rush University Medical CenterEmory UniversityEnrolling by invitationTuberous Sclerosis | Fragile X Syndrome | Rett Syndrome | Hamartoma Syndrome, Multiple | Angelman Syndrome | Creatine Deficiency, X-linked | Telomeric 22Q13 Monosomy Syndrome | Chromosome 15Q, Partial DeletionUnited States
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White Plains HospitalActive, not recruitingPancreatic Cancer | Pancreatic Adenocarcinoma | Lynch Syndrome | Pancreas Cancer | HNPCC | Familial Pancreatic Cancer | Hereditary Pancreatitis | BRCA 1/2 | FAMMM | Familial Atypical Multiple Mole Melanoma | Peutz Jeghers SyndromeUnited States
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University Health Network, TorontoSunnybrook Health Sciences Centre; University of Toronto; Hamilton Health Sciences... and other collaboratorsActive, not recruitingUniversal Screening for Lynch Syndrome in Women With Endometrial and Non-Serous Ovarian Cancer (LS2)Colorectal Neoplasms | Ovarian Neoplasms | Lynch Syndrome | Endometrial NeoplasmsCanada
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PellePharm, Inc.CompletedBasal Cell Nevus SyndromeUnited States, Spain, Germany, United Kingdom, Italy, France, Belgium, Canada, Denmark, Netherlands
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Novartis PharmaceuticalsCompletedCryopyrin Associated Periodic SyndromeCanada
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Ascend Biopharmaceuticals LtdSuspendedBasal Cell Carcinoma in Basal Cell Nevus SyndromeUnited States
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University Hospital, LilleCompleted
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Istituto Ortopedico RizzoliActive, not recruitingOsteogenesis Imperfecta | Multiple Osteochondroma | Ollier DiseaseItaly
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Istituto Ortopedico RizzoliCatholic University of the Sacred Heart; Regione Emilia-RomagnaCompletedOsteogenesis Imperfecta | Multiple Osteochondroma
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)UnknownWilms' Tumor | AniridiaUnited States
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National Cancer Institute (NCI)CompletedMyelodysplastic Syndromes | LeukemiaUnited States
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Aspira Women's HealthTerminatedHereditary Breast and Ovarian Cancer | Adnexal Mass | Germline BRCA1 Gene Mutation | Germline BRCA2 Gene MutationUnited States
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Universitätsklinikum Hamburg-EppendorfCompletedNephrotic Syndrome | Wilms Tumor | Frasier Syndrome | Denys-Drash SyndromeGermany
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Handok Inc.Terminated
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Lei LiUnknownColorectal Neoplasms, Hereditary Nonpolyposis | Endometrial NeoplasmsChina
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National Heart, Lung, and Blood Institute (NHLBI)CompletedMyelodysplastic Syndrome | Acute Myeloid Leukemia (AML) | Chronic Myeloid Leukemia (CML)United States
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Pharvaris Netherlands B.V.RecruitingHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | Hereditary Angioedema Types I and II | Hereditary Angioedema Attack | Hereditary Angioedema With C1 Esterase Inhibitor Deficiency | Hereditary Angioedema - Type 1 | Hereditary Angioedema - Type 2 | C1 Esterase Inhibitor... and other conditionsUnited States, Puerto Rico
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Regeneron PharmaceuticalsCompletedGenetic Diseases, Inborn | Familial Cold Autoinflammatory Syndrome (FCAS) | Familial Cold Urticaria | Muckle-Wells Syndrome (MWS)United States
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Pharvaris Netherlands B.V.RecruitingHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | Hereditary Angioedema Types I and II | Hereditary Angioedema Attack | Hereditary Angioedema With C1 Esterase Inhibitor Deficiency | Hereditary Angioedema - Type 1 | Hereditary Angioedema - Type 2 | C1 Esterase Inhibitor... and other conditionsUnited States, Bulgaria, Czechia, Hungary, Spain, France, Germany, Poland, Canada, Israel
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Therapeutic Advances in Childhood Leukemia ConsortiumRecruitingNeurofibromatosis 1 | JMML | Leukemia, Juvenile Myelomonocytic | JCML | CBL SyndromeUnited States
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Massachusetts General HospitalJohns Hopkins UniversityRecruitingNeurofibromatosis 1United States
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Masonic Cancer Center, University of MinnesotaRecruiting
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Imagine InstituteRWTH Aachen University; Ruhr University of Bochum; Medical University of WarsawRecruitingEpilepsy | Tuberous SclerosisFrance
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Spectrum Health HospitalsCompleted
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University of ManchesterCompletedNeurofibromatosis 1United Kingdom
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University of California, Los AngelesEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsUnknown
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University Hospital, MontpellierUnknownTuberous Sclerosis ComplexFrance
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University of California, Los AngelesCompletedNeurofibromatosis 1United States
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Katarzyna KotulskaRecruitingTuberous Sclerosis ComplexPoland
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Stanford UniversityJohns Hopkins University; University of California, San FranciscoRecruitingNeurofibromatosis 1United States
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National Cancer Institute (NCI)RecruitingNeurofibromatosis 1United States
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Children's Hospital Medical Center, CincinnatiUnited States Department of DefenseRecruitingNeurofibromatosis 1United States
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University Hospitals Bristol and Weston NHS Foundation...University College, London; The Tuberous Sclerosis AssociationActive, not recruitingTuberous Sclerosis ComplexUnited Kingdom
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NobelpharmaTerminated
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Harry T Whelan, MDCompletedNeurofibromatosesUnited States
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University of ManchesterCompletedNeurofibromatosis 1United Kingdom
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Massachusetts General HospitalThe Children's Tumor FoundationCompletedNeurofibromatosesUnited States
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University of California, Los AngelesBoston Children's HospitalCompletedTuberous Sclerosis ComplexUnited States
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University of PennsylvaniaH. Lundbeck A/STerminatedComplex Partial SeizuresUnited States
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Children's Hospital Medical Center, CincinnatiMassachusetts General Hospital; The University of Texas Health Science Center... and other collaboratorsCompletedTuberous Sclerosis ComplexUnited States
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Assistance Publique - Hôpitaux de ParisFrench National Referral Center for NeurofibromatosesUnknown
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M.D. Anderson Cancer CenterCompleted
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University of FloridaCelgene CorporationTerminatedMyelodysplastic Syndromes | Leukemia, MyeloidUnited States
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CENTOGENE GmbH RostockCompletedHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | C1 Esterase Inhibitor Deficiency | HAE | Angio Edema | C4 Deficiency | Hereditary Angioedema Type IIITurkey, Armenia, Georgia, India, Peru, Poland, Romania
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St. Jude Children's Research HospitalGlaxoSmithKline; National Institutes of Health (NIH)CompletedWilms TumorUnited States, Canada
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Assistance Publique - Hôpitaux de ParisInstitut ImagineNot yet recruitingAutoinflammatory Disease | FMF | TRAPS | MKD | Cryopyrin Associated Periodic Syndrome | HaploinsufficiencyFrance
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Federico II UniversityUniversity of Genova; University Hospital, Udine, Italy; University of Perugia...CompletedGastrointestinal Neoplasms | Respiratory Tract Neoplasms | Pancreatic Neoplasms | Multiple Endocrine Neoplasia | Thymic NeoplasmsItaly