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Clinical Trials on Nephritis, Hereditary
Total 3710 results
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Stanford UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Hugo W. Moser... and other collaboratorsCompletedX-linked AdrenoleukodystrophyUnited States
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, Germany, Argentina, Australia, France, United Kingdom
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University of Puerto RicoNational Institutes of Health (NIH)CompletedFamilial Adenomatous PolyposisPuerto Rico
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Vanderbilt-Ingram Cancer CenterNational Cancer Institute (NCI)TerminatedFamilial Adenomatous Polyposis | Deep Fibromatosis/Desmoid TumorUnited States
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Shenzhen Geno-Immune Medical InstituteUnknown
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NeuroVia, Inc.WithdrawnX-Linked AdrenoleukodystrophyAustralia, Argentina, United Kingdom, Colombia, Chile, France, Russian Federation, Ukraine
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Academisch Medisch Centrum - Universiteit van Amsterdam...Completed
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Xinhua Hospital, Shanghai Jiao Tong University...UnknownLymphoma | Acute Myeloid Leukemia | Neuroblastoma | Retinoblastoma | Hepatoblastoma | Acute Lymphoid LeukemiaChina
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Rabin Medical CenterUnknown
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NYU Langone HealthWithdrawnEpilepsy | Tuberous Sclerosis | Dravet Syndrome | Focal Seizures | Lennox-Gastaut SyndromeUnited States
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Nantes University HospitalUniversité de NantesUnknownChronic Inflammatory Demyelinating Polyneuropathy | Anti-MAG Neuropathy | Charcot-Marie-Tooth Disease, Type IAFrance
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Masonic Cancer Center, University of MinnesotaWithdrawnCerebral Adrenoleukodystrophy
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National Cancer Institute (NCI)CompletedFamilial Adenomatous PolyposisUnited States, Puerto Rico
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Washington University School of MedicineCompletedNeurofibromatosis Type 1 | Pediatric Brain TumorUnited States
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The Cleveland ClinicOhio State University Comprehensive Cancer CenterCompletedFamilial Adenomatous PolyposisUnited States
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University Hospital, ToulouseCompleted
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FDA Office of Orphan Products DevelopmentHugo W. Moser Research Institute at Kennedy Krieger, Inc.Completed
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The University of Texas Health Science Center,...Society for Pediatric DermatologyCompletedTuberous Sclerosis | Neurofibromatoses | Neurofibroma | AngiofibromaUnited States
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Roswell Park Cancer InstituteCompletedLymphoma | Brain and Central Nervous System Tumors | Neuroblastoma | RetinoblastomaUnited States
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Skane University HospitalCompletedDiabetes Complications | Carpal Tunnel Syndrome | Peripheral Neuropathy | Entrapment NeuropathiesSweden
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Far Eastern Memorial HospitalNational Taiwan University Hospital; Fu Jen Catholic UniversityUnknownAdrenoleukodystrophyTaiwan
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National Institute of Allergy and Infectious Diseases...CompletedChronic Granulomatous Disease | Leukocyte Disorder | Job's Syndrome | Chediak Higashi SyndromeUnited States
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Radboud University Medical CenterDutch Cancer SocietyUnknownAdenomatous Polyposis ColiNetherlands
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National Institute of Neurological Disorders and...CompletedMuscle Rigidity | Spasm | Stiff Man SyndromeUnited States
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National Center for Research Resources (NCRR)Icahn School of Medicine at Mount SinaiCompletedMetabolism, Inborn Errors | Leukodystrophy, Globoid Cell | Tay-Sachs Disease | Porphyria, ErythropoieticUnited States
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Fairview University Medical CenterUnknownHemophagocytic Lymphohistiocytosis | Graft Versus Host Disease | Chediak-Higashi Syndrome | Virus-Associated Hemophagocytic Syndrome | X-Linked Lymphoproliferative Syndrome | Familial Erythrophagocytic LymphohistiocytosisUnited States
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Abide TherapeuticsCompletedMultiple Sclerosis | Neuromyelitis Optica Spectrum Disorder | Transverse Myelitis | Longitudinally Extensive Transverse MyelitisUnited Kingdom
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Mayo ClinicTerumo BCTCompletedNeuromyelitis Optica | Neuromyelitis Optica Spectrum Disorder | Recurrent Idiopathic Longitudinally Extensive Transverse MyelitisUnited States
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Stanford UniversityWithdrawnNeuromyelitis OpticaUnited States
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Barbara Ann Karmanos Cancer InstituteNational Cancer Institute (NCI); Children's Hospital of MichiganTerminatedUnspecified Childhood Solid Tumor, Protocol Specific | Osteosarcoma | Neuroblastoma | Retinoblastoma | Recurrent/Refractory Childhood Hodgkin Lymphoma | Wilms Tumor and Other Childhood Kidney Tumors | Childhood Choroid Plexus Tumor | Childhood Soft Tissue Sarcoma | Childhood Medulloblastoma | Childhood... and other conditionsUnited States
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Universitätsklinikum Hamburg-EppendorfRecruitingFamilial Adenomatous Polyposis | Adenomatous Polyposis Coli | Duodenal AdenomaGermany
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IRCCS Ospedale San RaffaeleNot yet recruitingRare Diseases | Corneal Neovascularization | Limbal Stem Cell Deficiency | Aniridia | Neurotrophic Keratopathy | Ocular Cicatricial Pemphigoid | Ocular Graft-versus-host Disease | EEC Syndrome
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Minoryx Therapeutics, S.L.RecruitingX-linked AdrenoleukodystrophyFrance
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Laurent ServaisSYSNAVRecruitingDuchenne Muscular Dystrophy | Myotonic Dystrophy 1 | Congenital Muscular Dystrophy | Centronuclear Myopathy | Charcot-Marie-Tooth | Fascioscapulohumeral Muscular DystrophyBelgium
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Leiden University Medical CenterRecruiting
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University of SienaRecruitingBehcet Syndrome | Uveitis | Hereditary Autoinflammatory Diseases | Schnitzler Syndrome | Scleritis | PFAPA Syndrome | Still Disease | Autoinflammatory Syndrome, Unspecified | Vexas SyndromeEgypt, Spain, Turkey, Italy, Saudi Arabia, Greece, Belgium, United States, Algeria, Brazil, Germany, Ghana, Iran, Islamic Republic of, Lebanon, Morocco, Poland, Portugal, Romania, Taiwan
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Massachusetts General HospitalEuropean Leukodystrophy AssociationRecruitingRestless Legs Syndrome | AdrenoleukodystrophyUnited States, Netherlands
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Viking Therapeutics, Inc.RecruitingAdrenomyeloneuropathy Form (AMN) of X-linked Adrenoleukodystrophy (X-ALD)United States, France, Germany, Italy, United Kingdom
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University of AarhusRecruitingConstipation | Childhood Acute Lymphoblastic Leukemia | Neurofibromatosis 1 | Chronic Constipation With OverflowDenmark
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Western Sydney Local Health DistrictRecruitingFamilial Adenomatous PolyposisAustralia
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Massachusetts Eye and Ear InfirmaryMassachusetts General Hospital; United States Department of DefenseRecruitingNeurofibromatosis 2 | Vestibular Schwannoma | Acoustic NeuromaUnited States
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Memorial Sloan Kettering Cancer CenterActive, not recruitingMesothelioma | Wilms Tumor | Pleural MesotheliomaUnited States
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National Cancer Institute (NCI)Children's Oncology GroupActive, not recruitingJuvenile Myelomonocytic Leukemia | Neurofibromatosis Type 1United States
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Minoryx Therapeutics, S.L.Active, not recruitingCerebral AdrenoleukodystrophySpain, Germany, France, Argentina
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National Cancer Institute (NCI)WithdrawnNeoplasms | Myelodysplastic Syndromes | Adenomatous Polyposis Coli | Neurofibroma, PlexiformUnited States
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Guy's and St Thomas' NHS Foundation TrustCompletedNeurofibromatosis 2United Kingdom
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University Hospital, BrestCompletedPost Traumatic Stress Disorder | Neurofibromatosis 1 | Diagnoses DiseaseFrance
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FDA Office of Orphan Products DevelopmentCompletedNeurofibromatosis 2United States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedMyelodysplastic Syndrome | Acute Myeloid Leukemia (AML) | Chronic Myeloid Leukemia (CML)United States
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Thomas S. ScanlanWithdrawnAdrenomyeloneuropathy | X-Linked AdrenoleukodystrophyUnited States