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Clinical Trials on Neurodegenerative Disease, Hereditary
Total 377723 results
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Price Vision GroupTerminatedFuchs' Endothelial DystrophyUnited States
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Singapore National Eye CentreUnknownFuchs' Endothelial DystrophySingapore
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Columbia UniversityUniversity of North Carolina, Chapel HillTerminated
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Wolfson Medical CenterUnknown
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Glostrup University Hospital, CopenhagenUnknownOptic Atrophy, Autosomal DominantDenmark
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Rutgers, The State University of New JerseyNational Cancer Institute (NCI); Georgetown UniversityNot yet recruitingHereditary Cancer | Genetic Testing
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Instituto Nacional de Ciencias Medicas y Nutricion...CompletedHereditary Cancer | Genetic CounselingMexico
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Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | Amyloidosis, Hereditary | Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC) | Amyloidosis, Hereditary, Transthyretin-Related | Familial Transthyretin Cardiac AmyloidosisUnited States, France, Italy, Spain, Canada, Germany, Belgium, Sweden, United Kingdom
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Centre Hospitalier Régional Metz-ThionvilleCompleted
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Brigham and Women's HospitalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedGenetic Predisposition to Disease | Hereditary DiseaseUnited States
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Susan J. HayflickOregon Health and Science UniversityRecruitingNeurodegeneration With Brain Iron Accumulation (NBIA)United States
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University Hospital, BordeauxInstitut National de la Santé Et de la Recherche Médicale, FranceCompletedNeurodegeneration With Brain Iron Accumulation (NBIA)France
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University Hospital, Strasbourg, FranceRecruitingBardet-Biedl Syndrome | Alström SyndromeFrance
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King's College LondonUniversity of Oxford; Neuroscience Technologies S.L.PUnknownChronic Pain | Hereditary Sensory and Autonomic Neuropathies | Erythromelalgia | Pain Insensitivity, CongenitalUnited Kingdom
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Liminal BioSciences Ltd.CompletedDiabetes | Inflammation and FibrosisUnited Kingdom
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Medical University of ViennaRecruiting
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PfizerCompletedHereditary Transthyretin Amyloidosis (ATTRv) Cardiomyopathy (CM), Mixed PhenotypeUnited States
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Massachusetts Eye and Ear InfirmaryCompletedFuchs' Endothelial DystrophyUnited States
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University of AarhusActive, not recruitingFuchs' Endothelial DystrophyDenmark
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Maastricht University Medical CenterZonMw: The Netherlands Organisation for Health Research and DevelopmentCompleted
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Oregon Health and Science UniversityTerminated
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University of California, San DiegoNew York University; Heinrich-Heine University, Duesseldorf; Universität TübingenRecruitingGenetic Disease | Mitochondrial Encephalomyopathies | Neonatal Encephalopathy | Mutation | Hereditary Spastic Paraplegia | White Matter Disease | Spastic ParaplegiaUnited States
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Pro-Change Behavior SystemsRecruitingMental Health Issue | Hereditary CancerUnited States
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Massachusetts General HospitalBroad Institute; Laboratory for Molecular MedicineCompletedGenetic Predisposition to Disease | Hereditary DiseaseUnited States
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Institut National de la Santé Et de la Recherche...UnknownAutoinflammatory Diseases, Hereditary
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TakedaRecruitingAngioedema | Hereditary Angioedema (HAE)Canada
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TakedaRecruitingHereditary Angioedema (HAE)United Kingdom
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ShireTakeda Development Center Americas, Inc.No longer availableAngioedema | Hereditary Angioedema (HAE)United States, Canada, Germany, Hungary, Spain
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ShireCompletedHereditary Angioedema (HAE)Japan
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ShireCompletedHereditary Angioedema (HAE)United States, Canada, Australia, Austria, Colombia, Germany, Hungary, Israel, Italy, Spain
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ShireCompletedHereditary Angioedema (HAE)United States, Canada, Jordan
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ShireCompletedHereditary Angioedema (HAE)United States
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ShireCompletedHereditary Angioedema (HAE)United States
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ShireCompleted
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ShireCompletedHereditary Angioedema (HAE)
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ShireDyax Corp.CompletedHereditary Angioedema (HAE)United States
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Universitaire Ziekenhuizen KU LeuvenFund for Scientific Research, Flanders, Belgium; Funds for Research in Ophthalmology... and other collaboratorsCompletedFuchs' Endothelial DystrophyBelgium
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EuroBloodNet AssociationNot yet recruitingHereditary Red Blood Cell Disorder (Disorder)Denmark, Netherlands
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Applied Therapeutics, Inc.Active, not recruitingHereditary Neuropathy Caused by SORD DeficiencyUnited States, United Kingdom, Czechia, Italy
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University of ZurichRecruitingNeurodegenerative DiseasesSwitzerland
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Johns Hopkins UniversityRecruitingGranular Dystrophy, CornealUnited States
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University Eye Hospital, FreiburgCompletedFuchs' Endothelial DystrophyGermany
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National Cancer Institute (NCI)CompletedColorectal Neoplasm | Hereditary NonpolyposisUnited States
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Pharnext SACompletedCharcot-Marie-Tooth Disease | Hereditary Neuropathy With Liability to Pressure Palsies | Genetic DisordersFrance
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Vaderis Therapeutics AGRecruitingHereditary Hemorrhagic Telangiectasia (HHT)United States, Spain, France, Belgium, Netherlands, Italy
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Taysha Gene Therapies, Inc.National Institute of Neurological Disorders and Stroke (NINDS)Active, not recruitingGene Transfer | Giant Axonal NeuropathyUnited States
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Centre Hospitalier Universitaire de BesanconCompleted
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University of RochesterLivionex IncCompletedCorneal Dystrophy, Band-ShapedUnited States
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University Hospital, RouenCompleted
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University of South FloridaUniversity of Miami; National Institutes of Health (NIH); University of KansasCompletedAmyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Progressive Muscular Atrophy | Hereditary Spastic Paraplegia