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- US Clinical Trials Registry
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Clinical Trials on Neuromuscular Diseases in Children in Italy
Total 739 results
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Jazz PharmaceuticalsCompletedFibromyalgiaSpain, United States, Netherlands, United Kingdom, France, Germany, Italy
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Santhera PharmaceuticalsCompletedMuscular Dystrophy, Duchenne | Ambulatory CareUnited States, Spain, Austria, Belgium, France, Germany, Italy, Netherlands, Sweden, Switzerland
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PfizerTerminatedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Japan, Italy
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | DystrophinopathyUnited Kingdom, Canada, Germany, Spain, Sweden, Italy, Australia, Belgium, France, Israel
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Priovant Therapeutics, Inc.RecruitingDermatomyositisUnited States, Belgium, Germany, Hungary, Israel, Italy, Netherlands, Portugal, Korea, Republic of, Bulgaria, Poland, Romania, Czechia, Taiwan, Chile, Mexico, Turkey, Serbia, Spain, United Kingdom, Canada, Argentina
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CSL BehringCompletedPolyradiculoneuropathy, Chronic Inflammatory Demyelinating | Chronic Inflammatory Demyelinating Polyneuropathy (CIDP)United States, Japan, Australia, Canada, Czechia, France, Germany, Italy, Netherlands, Spain, United Kingdom
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Jazz PharmaceuticalsCompletedFibromyalgiaSpain, United States, Netherlands, United Kingdom, France, Germany, Italy, Poland
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Baxalta now part of ShireTakeda Development Center Americas, Inc.CompletedChronic Inflammatory Demyelinating PolyradiculoneuropathySpain, Canada, Poland, Italy, Serbia, Germany, Mexico, Turkey, United Kingdom, Czechia, France, United States, Argentina, Brazil, Colombia, Denmark, Greece, Slovakia
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Novartis PharmaceuticalsCompletedCML in Chronic PhaseGermany, Italy, Spain, Belgium, Croatia, Hungary, Netherlands, Austria, France, Greece, Sweden, Switzerland, Bulgaria, Romania, Slovenia, United Kingdom, Lithuania, Slovakia, Denmark, Finland, Norway, Poland, Czech Republic, Portugal, E... and more
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Instituto Grifols, S.A.TerminatedPost-polio SyndromeUnited States, Denmark, Spain, Germany, Poland, Canada, Czechia, Italy, Netherlands
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Active, not recruitingDuchenne Muscular DystrophyKorea, Republic of, Chile, Japan, China, United Kingdom, Netherlands, Spain, Norway, Russian Federation, Australia, Greece, Italy, New Zealand, Turkey, Mexico, Czechia, Canada
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Cooperative International Neuromuscular Research...United States Department of Defense; National Institutes of Health (NIH); U.S... and other collaboratorsUnknownDuchenne Muscular DystrophyUnited States, Canada, Australia, India, Israel, Argentina, Italy, Sweden
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Novartis PharmaceuticalsTerminatedGlioblastoma | Anaplastic Large Cell Lymphoma | Inflammatory Myofibroblastic Tumor | Tumors With Aberrations in ALKFrance, Czechia, Italy, Spain, Korea, Republic of, Thailand, Israel, Denmark
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GlaxoSmithKlineCompletedAmyotrophic Lateral SclerosisUnited States, France, Australia, Canada, Belgium, Germany, Korea, Republic of, Japan, Netherlands, Italy, United Kingdom
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AB ScienceRecruitingAmyotrophic Lateral SclerosisFrance, Spain, United States, Sweden, Denmark, Portugal, Italy, Israel, Germany, Norway, Poland, Russian Federation, Slovenia, Ukraine, Greece, Belgium, Serbia
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argenxRecruitingMyositis | Dermatomyositis | Polymyositis | Antisynthetase Syndrome | Immune-Mediated Necrotizing Myopathy | Active Idiopathic Inflammatory MyopathyKorea, Republic of, Thailand, United States, Bulgaria, Taiwan, Argentina, Belgium, Cyprus, Denmark, France, Georgia, Germany, Greece, Italy, Lithuania, Czechia, Sweden
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PfizerActive, not recruitingSickle Cell Disease | Vaso-occlusive Pain Episode in Sickle Cell Disease | Vaso-occlusive CrisisUnited States, Oman, Colombia, Brazil, Lebanon, Nigeria, Germany, Italy, Kenya, Saudi Arabia, Tanzania, Turkey
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PfizerTerminatedSickle Cell Disease | Vaso-occlusive Pain Episode in Sickle Cell Disease | Vaso-occlusive CrisisUnited States, Oman, France, Brazil, Colombia, Lebanon, Nigeria, Germany, Italy, Kenya, Saudi Arabia, Turkey, United Kingdom, Zambia
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AllerganCompletedCerebral Palsy | Muscle Spasticity | PediatricsUnited States, Korea, Republic of, Thailand, Hungary, Italy, Philippines, Poland, Russian Federation, Turkey
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Ionis Pharmaceuticals, Inc.CompletedHereditary Transthyretin-Mediated Amyloid PolyneuropathyUnited States, Spain, Taiwan, Italy, Germany, Argentina, Australia, Brazil, Canada, Cyprus, France, Greece, New Zealand, Portugal, Sweden, Turkey
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Stealth BioTherapeutics Inc.Active, not recruitingMitochondrial Diseases | Mitochondrial Myopathies | Mitochondrial Complex I Deficiency | Mitochondrial Pathology | Mitochondrial DNA Depletion | Mitochondrial DNA Mutation | Mitochondrial DNA Deletion | Mitochondrial Metabolism DefectSpain, United States, Italy, Netherlands, Australia, Germany, Hungary, New Zealand, Norway, United Kingdom
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Ionis Pharmaceuticals, Inc.RecruitingAmyotrophic Lateral SclerosisUnited States, Germany, Netherlands, Spain, Korea, Republic of, Canada, Switzerland, Belgium, Italy, United Kingdom, Ireland, Sweden, Taiwan, Brazil
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IpsenRecruitingSpasticity as Sequela of StrokeUnited States, Spain, France, United Kingdom, Germany, Italy, Sweden
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CytokineticsTerminatedAmyotrophic Lateral SclerosisCanada, United States, Australia, Spain, Belgium, Ireland, Italy, Netherlands, Sweden
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Sarepta Therapeutics, Inc.Hoffmann-La RocheRecruitingDuchenne Muscular DystrophyBelgium, United States, Japan, Spain, Italy, United Kingdom
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Newcastle... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Germany, Italy
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Santhera PharmaceuticalsTerminatedDuchenne Muscular DystrophyUnited States, Belgium, United Kingdom, Austria, France, Germany, Italy, Spain, Switzerland
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Novartis PharmaceuticalsCompletedTransfusional Iron Overload in β-thalassemiaUnited States, Greece, Argentina, Germany, Belgium, Italy, United Kingdom, France, Tunisia, Canada, Turkey, Brazil
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Apellis Pharmaceuticals, Inc.TerminatedMotor Neuron Disease | Amyotrophic Lateral SclerosisUnited States, Netherlands, Spain, Germany, Japan, Australia, France, Poland, Ukraine, Belgium, Czechia, Ireland, Italy, United Kingdom
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University of IowaJohns Hopkins University; University of Colorado, Denver; King's College Hospital... and other collaboratorsRecruitingCharcot-Marie-Tooth Disease, Type Ia (Disorder) | HMSNUnited States, Italy, United Kingdom, Australia
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Dyne TherapeuticsRecruitingDuchenne Muscular Dystrophy (DMD)United States, Belgium, Canada, United Kingdom, Australia, Spain, Italy
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PfizerRecruitingMyositisChina, United States, Japan, Korea, Republic of, Taiwan, Spain, Germany, Hungary, Poland, Argentina, Italy, India, Belgium, Mexico, France, Slovakia, Bulgaria
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AllerganCompletedCerebral Palsy | Muscle Spasticity | PediatricsUnited States, Korea, Republic of, Thailand, Philippines, Poland, Hungary, Russian Federation, Turkey, Italy
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ItalfarmacoCromsourceEnrolling by invitationDuchenne Muscular DystrophySpain, United States, Canada, Belgium, France, Israel, Italy, Netherlands, Serbia, Germany, United Kingdom
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Michael ShyJohns Hopkins University; University of Colorado, Denver; King's College Hospital... and other collaboratorsRecruitingCharcot Marie Tooth DiseaseUnited States, Australia, Italy, United Kingdom, Canada
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Fulcrum TherapeuticsActive, not recruitingFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Spain, Italy, Denmark, Canada, Germany, France, Netherlands, United Kingdom
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BiogenIonis Pharmaceuticals, Inc.CompletedAmyotrophic Lateral SclerosisUnited States, Canada, Belgium, France, Australia, Japan, Denmark, Korea, Republic of, United Kingdom, Germany, Italy, Poland
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Ionis Pharmaceuticals, Inc.CompletedAmyloidosis | Familial Amyloid Polyneuropathy | FAP | TTR | TransthyretinUnited States, Spain, Argentina, Brazil, France, Germany, Italy, Portugal, United Kingdom
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Novartis PharmaceuticalsMitsubishi Tanabe Pharma CorporationCompletedChronic Inflammatory Demyelinating PolyradiculoneuropathySpain, United States, Belgium, Germany, Italy, Israel, Australia, France, United Kingdom, Netherlands, Czechia, Japan, Canada, Greece, Poland
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Egetis TherapeuticsSolasia Pharma K.K.TerminatedColorectal Cancer | Chemotherapy-induced Peripheral NeuropathyFrance, Korea, Republic of, Italy, Japan, Spain, Belgium, Germany, United Kingdom, Czechia, Taiwan
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophyKorea, Republic of, Chile, Taiwan, China, United States, United Kingdom, Netherlands, Spain, Australia, Norway, Russian Federation, Greece, Italy, Turkey, Mexico, Canada, Hong Kong, New Zealand, Ukraine
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ItalfarmacoSyneos HealthCompletedDuchenne Muscular DystrophyUnited States, Italy, Spain, Canada, Belgium, France, Germany, Israel, Netherlands, Serbia, United Kingdom
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PfizerTerminatedDuchenne Muscular DystrophyUnited States, Australia, Canada, United Kingdom, Japan, Bulgaria, Italy, Poland
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BioMarin PharmaceuticalNo longer availableDuchenne Muscular DystrophyUnited States, Germany, United Kingdom, Japan, Netherlands, France, Spain, Korea, Republic of, Italy, Belgium, Taiwan, Argentina, Australia, Bulgaria, Czechia, Israel, Norway, Poland, Russian Federation, Turkey
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Translational Research Center for Medical Innovation...RecruitingNeutral Lipid Storage DiseaseChina, United States, France, Austria, Germany, Italy, Japan, Netherlands, United Kingdom
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Ionis Pharmaceuticals, Inc.CompletedAmyloidosis | Familial Amyloid Polyneuropathy | FAP | TTR | TransthyretinNew Zealand, United States, Spain, Argentina, Brazil, France, Germany, Italy, Portugal, United Kingdom
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GlaxoSmithKlineCompletedTetanus | Diphtheria | Acellular Pertussis | Poliomyelitis | Diphtheria-Tetanus-aPertussis-Hepatitis B-Poliomyelitis-Haemophilus Influenzae Type b VaccinesFinland, Australia, Spain, Italy, Canada, Czechia
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CSL BehringICON Clinical ResearchCompletedPolyradiculoneuropathy | Chronic Inflammatory Demyelinating PolyneuropathyUnited States, Australia, Belgium, Canada, Czechia, Estonia, Finland, France, Germany, Israel, Italy, Japan, Netherlands, Poland, Spain, United Kingdom
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PTC TherapeuticsActive, not recruitingAmyotrophic Lateral SclerosisUnited States, Belgium, Spain, Australia, Germany, Italy, Czechia, France, Netherlands, Japan, Poland, Argentina, Sweden
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...CompletedClear Cell Renal Cell Carcinoma | Chronic Myelomonocytic Leukemia | Previously Treated Myelodysplastic Syndrome | Recurrent Adult Acute Myeloid Leukemia | Recurrent Adult Lymphoblastic Lymphoma | Untreated Adult Acute Myeloid Leukemia | Adult Acute Myeloid Leukemia in Remission | Childhood Acute... and other conditionsUnited States, Germany, Italy