Clinical Trials on Neuronal Ceroid-Lipofuscinoses in France

Total 406 results

ZevraDenmark

Completed

Arimoclomol in Amyotropic Lateral Sclerosis

Amyotrophic Lateral Sclerosis

Canada, United States, Belgium, Netherlands, Poland, United Kingdom, France, Germany, Italy, Spain, Sweden, Switzerland
Laboratoire français de Fractionnement et de Biotechnologies
TFS Trial Form Support

Completed

LIME Study (LFB IVIg MMN Efficacy Study) (LIME)

Motor Neuron Disease

Spain, United Kingdom, Italy, France
Humanitas Mirasole SpA
KU Leuven; UMC Utrecht; University of Sheffield; Istituto Superiore di Sanità; University... and other collaborators

Recruiting

Open Label Extension of TUDCA-ALS Study (TUDCA-ALS OLE)

Amyotrophic Lateral Sclerosis

Germany, France, Netherlands, Italy, United Kingdom, Belgium, Ireland
Juniper Pharmaceuticals, Inc.
Eunice Kennedy Shriver National Institute of Child Health and Human Development...

Completed

PREGNANT Short Cervix Trial

Preterm Delivery | Short Cervix | Short Uterine Cervical Length

United States, Israel, Belarus, Chile, Czech Republic, India, Italy, Russian Federation, South Africa, Ukraine
Cirbia Silva Campos Teixeira

Completed

Strategies for Endocervical Canal Investigation in Women With Abnormal Screening Cytology and Negative Colposcopy

Cervical Cancer | Diagnoses Disease | Screening | HSIL of Cervix

Brazil
Assistance Publique Hopitaux De Marseille

Recruiting

Outcome Measures and Biomarkers in a Cohort of Spinal Muscular Atrophy Type III/ IV Patients (SMOB)

Spinal Muscular Atrophy

France
NightstaRx Ltd, a Biogen Company

Enrolling by invitation

Long-term Safety and Efficacy Follow-up of BIIB111 for the Treatment of Choroideremia and BIIB112 for the Treatment of X-Linked Retinitis Pigmentosa (SOLSTICE)

Choroideremia | X-Linked Retinitis Pigmentosa

United States, United Kingdom, Netherlands, Germany, France, Brazil, Canada, Denmark, Finland
Millendo Therapeutics US, Inc.

Terminated

Nevanimibe HCl for the Treatment of Classic CAH

Congenital Adrenal Hyperplasia

Spain, Israel, France, Brazil, Czechia
Sangamo Therapeutics

Completed

Clinical Trial of SB-509 in Subjects With Amyotrophic Lateral Sclerosis (ALS) (ALS)

Amyotrophic Lateral Sclerosis

United States
Biogen

Recruiting

A Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of BIIB115

Healthy Volunteer | Muscular Atrophy, Spinal

Korea, Republic of, Germany, Belgium, Netherlands, France, Italy, Poland, Canada, United Kingdom, Israel
ZIWIG
Monitoring Force Group

Recruiting

ALS Diagnosis From a Saliva Sample: a Non-coding RNA Analysis Approach (RNALS)

Amyotrophic Lateral Sclerosis | Amyotrophic Lateral Sclerosis, Sporadic

France
Hoffmann-La Roche

Recruiting

A Study to Evaluate the Efficacy and Safety of Faricimab in Patients With Choroidal Neovascularization Secondary to Pathologic Myopia (POYANG)

Choroidal Neovascularization Secondary to Pathologic Myopia

Korea, Republic of, China, Australia, Singapore, Poland, France, Germany, Italy, Taiwan, Hong Kong, Spain
GlaxoSmithKline

Completed

Pazopanib Plus Lapatinib Compared to Lapatinib Alone and Pazopanib Alone In Subjects With Metastatic Cervical Cancer

Metastatic Cervical Cancer | Neoplasms, Uterine Cervix

United States, Germany, Spain, Thailand, Belgium, Italy, Argentina, Canada, Ireland, India, France, Estonia, Mexico
Humanitas Mirasole SpA
KU Leuven; UMC Utrecht; University of Sheffield; Istituto Superiore di Sanità; University... and other collaborators

Active, not recruiting

Safety and Efficacy of TUDCA as add-on Treatment in Patients Affected by ALS (TUDCA-ALS)

Amyotrophic Lateral Sclerosis (ALS)

United Kingdom, Germany, France, Netherlands, Belgium, Ireland, Italy
Pfizer

Terminated

An Open Label Trial to Investigate Macugen for the Preservation of Visual Function in Subjects With Neovascular AMD (PERSPECTIVES)

Macular Degeneration | Age Related Macular Degeneration (AMD) | Choroidal Neovascularization (CNV)

Canada, Belgium, United Kingdom, France, Poland, Spain, Turkey, Czech Republic, Italy, Greece, Germany, Austria, Portugal, Denmark, Finland
Assistance Publique - Hôpitaux de Paris

Terminated

Amyotrophic Lateral Sclerosis and Frontotemporal Dementia

Amyotrophic Lateral Sclerosis | Frontotemporal Dementia

France
Hoffmann-La Roche

Completed

A Study to Evaluate Long Term Safety, Tolerability, and Effectiveness of Olesoxime in Patients With Spinal Muscular Atrophy (SMA)

Muscular Atrophy, Spinal

Belgium, United Kingdom, Germany, France, Italy, Netherlands, Poland
Biogen

Approved for marketing

Expanded Access Program for Tofersen in Participants With Superoxide Dismutase 1-Amyotropic Lateral Sclerosis

Superoxide Dismutase 1-Amyotropic Lateral Sclerosis

United States
Novartis Pharmaceuticals

Completed

Randomized Study for Efficacy and Safety of Ranibizumab 0.5mg in Treat-extend and Monthly Regimens in Patients With nAMD (TREND)

Age-related Macular Degeneration | Choroidal Neovascularization

Korea, Republic of, Croatia, Germany, India, Russian Federation, Turkey, United Kingdom, Egypt, Israel, Belgium, Denmark, Hungary, Slovenia, Spain, Switzerland, Italy, Portugal, Slovakia, Chile
Alcyone Therapeutics, Inc
Biogen

Recruiting

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy (PIERRE)

Scoliosis | Spinal Muscular Atrophy | Spine Deformity

United States
Anelixis Therapeutics, LLC

Completed

Multiple Doses of AT-1501-A201 in Adults With ALS

Amyotrophic Lateral Sclerosis

United States, Canada
Hoffmann-La Roche

Active, not recruiting

A Study of Risdiplam (RO7034067) in Adult and Pediatric Participants With Spinal Muscular Atrophy (Jewelfish)

Spinal Muscular Atrophy

Belgium, United States, United Kingdom, France, Poland, Italy, Switzerland, Netherlands, Germany
Hospices Civils de Lyon

Completed

Diagnostic Performance of 18F-FDG-PET and Diffusion-weighted MRI in the Assessment of Stage IB to IIB2 Cervical Squamous-cell Carcinoma Response to Concomitant Radiochemotherapy and Brachytherapy (ERRICC)

Cancer of the Uterine Cervix

France
Hoffmann-La Roche

Terminated

A Study of RO6885247 in Adult and Pediatric Patients With Spinal Muscular Atrophy (MOONFISH)

Muscular Atrophy, Spinal

France, Turkey, Canada, United States, Italy, Netherlands, Sweden, Switzerland, United Kingdom
Transposon Therapeutics, Inc.

Active, not recruiting

A Phase 2a Study of TPN-101 in Patients With C9ORF72 ALS/FTD

Amyotrophic Lateral Sclerosis | Frontotemporal Dementia

Spain, United States, Belgium, France, Germany
Hospices Civils de Lyon

Completed

Toxin Treatment for Amyotrophic Lateral Sclerosis (ALS) Related Sialorrhea (ALS-TOX)

Amyotrophic Lateral Sclerosis | Sialorrhea

France
Assistance Publique - Hôpitaux de Paris

Not yet recruiting

Development of Non-Invasive Prenatal Diagnosis for Single Gene Disorders (DANNIgene)

Hemophilia A | Hemophilia B | Cystic Fibrosis | Sickle Cell Disease | Muscular Dystrophy, Duchenne | Fragile X Syndrome | Huntington Disease | Myotonic Dystrophy | Autosomal Recessive Polycystic Kidney Disease | Neurofibromatosis-Noonan Syndrome | Muscular Dystrophy, Becker | Invasive PreNatal Diagnosis in a... and other conditions

France
Annexon, Inc.

Recruiting

Study of ANX005 in Adults With Amyotrophic Lateral Sclerosis (ALS)

Amyotrophic Lateral Sclerosis

United States, Canada
Novartis Pharmaceuticals

Recruiting

Study of Safety and of the Mechanism of BLZ945 in ALS Patients

Amyotrophic Lateral Sclerosis

Australia, United States, Finland, Sweden
Diurnal Limited

Completed

Comparison of Chronocort Versus Standard Hydrocortisone Replacement Therapy in Participants Aged 16 Years and Over With Congenital Adrenal Hyperplasia (CONnECT)

Congenital Adrenal Hyperplasia

France, United States, Japan
Brian Wainger
Massachusetts General Hospital; GlaxoSmithKline; ALS Association; Harvard University

Completed

Clinical Trial of Ezogabine (Retigabine) in ALS Subjects

Amyotrophic Lateral Sclerosis

United States
Ono Pharmaceutical Co. Ltd

Completed

A Phase II Multi-centre, Extension Study to Investigate the Long Term Safety of ONO-2506PO in Patients Diagnosed With Amyotrophic Lateral Sclerosis (ALS)

Amyotrophic Lateral Sclerosis (ALS)

Belgium, France, Germany, Italy, Netherlands, Switzerland, United Kingdom
Ferrer Internacional S.A.
Julius Clinical; Stichting TRICALS Foundation

Active, not recruiting

Study to Investigate the Efficacy and Safety of FAB122 (Daily Oral Edaravone) in Patients With Amyotrophic Lateral Sclerosis (ADORE)

Amyotrophic Lateral Sclerosis

Belgium, Netherlands, United Kingdom, Spain, Germany, France, Ireland, Italy, Poland, Portugal, Sweden
Teva Branded Pharmaceutical Products R&D, Inc.

Completed

Talampanel for Amyotrophic Lateral Sclerosis (ALS) (ALS)

ALS

United States, Netherlands, Canada, Italy, Spain, Belgium, France, Germany, Hungary, Israel
Bjorn Oskarsson, MD
University of California, Davis; ALS Association

Completed

Mexiletine for the Treatment of Muscle Cramps in ALS

Muscle Cramps in Amyotrophic Lateral Sclerosis

United States
Diurnal Limited

Enrolling by invitation

Long-term Safety Study of Chronocort in the Treatment of Participants With Congenital Adrenal Hyperplasia

Congenital Adrenal Hyperplasia

United States, France, Japan
Forbes Norris MDA/ALS Research Center
Muscular Dystrophy Association

Completed

A Multi-Center Controlled Screening Trial of Safety and Efficacy of Lithium Carbonate in Subjects With Amyotrophic Lateral Sclerosis (ALS) (Lithium)

Amyotrophic Lateral Sclerosis

United States
Corcept Therapeutics

Active, not recruiting

Dazucorilant in Patients With Amyotrophic Lateral Sclerosis (DAZALS)

Amyotrophic Lateral Sclerosis

United States, Belgium, Canada, France, Germany, Ireland, Netherlands, Poland, Spain, United Kingdom
Ono Pharmaceutical Co. Ltd

Completed

Placebo Controlled Study of ONO2506PO in the Presence of Riluzole in Patients With Amyotrophic Lateral Sclerosis (ALS)

Amyotrophic Lateral Sclerosis (ALS)

Belgium, France, Austria, Germany, Italy, Netherlands, Switzerland, United Kingdom
Cytokinetics

Completed

Dose Titration Study to Test Safety and Effects of CK-2017357 in Patients With Amyotrophic Lateral Sclerosis (ALS)

Amyotrophic Lateral Sclerosis

United States
Biogen

Completed

Methodology Study of Novel Outcome Measures to Assess Progression of ALS

Amyotrophic Lateral Sclerosis

Canada, United States, Belgium, Germany, Switzerland, Ireland, Netherlands, France, United Kingdom
PTC Therapeutics

Active, not recruiting

Study to Assess the Effects of PTC857 Treatment in Participants With Amyotrophic Lateral Sclerosis ALS (CARDINALS)

Amyotrophic Lateral Sclerosis

United States, Belgium, Spain, Australia, Germany, Italy, Czechia, France, Netherlands, Japan, Poland, Argentina, Sweden
Novartis Pharmaceuticals

Completed

Safety and Efficacy of Intravenous OAV101 (AVXS-101) in Pediatric Patients With Spinal Muscular Atrophy (SMA) (SMART)

Spinal Muscular Atrophy

Taiwan, Belgium, Canada, United States, Australia, France, Italy, Portugal, United Kingdom
University of Washington
Massachusetts General Hospital

Completed

Mexiletine in Sporadic Amyotrophic Lateral Sclerosis (Mexiletine-2)

Sporadic Amyotrophic Lateral Sclerosis

United States
Clene Nanomedicine

Available

Intermediate Expanded Access Protocol (EAP) CNMAu8.EAP02

Amyotrophic Lateral Sclerosis

United States
Novartis Pharmaceuticals

Active, not recruiting

Phase IIIb, Open-label, Multi-center Study to Evaluate Safety, Tolerability and Efficacy of OAV101 Administered Intrathecally to Participants With SMA Who Discontinued Treatment With Nusinersen or Risdiplam (STRENGTH)

Spinal Muscular Atrophy

Japan, Belgium, Spain, Canada, United States, Australia, Italy, France, Netherlands
Amylyx Pharmaceuticals Inc.

Active, not recruiting

Phase III Trial of AMX0035 for Amyotrophic Lateral Sclerosis Treatment (Phoenix)

Amyotrophic Lateral Sclerosis

United States, Belgium, Spain, Netherlands, United Kingdom, Germany, Sweden, France, Ireland, Italy, Poland, Portugal
Amylyx Pharmaceuticals Inc.

Enrolling by invitation

Extension Study Evaluating The Safety And Tolerability of AMX0035

Amyotrophic Lateral Sclerosis

Belgium, Spain, Netherlands, United Kingdom, Sweden, France, Germany, Ireland, Italy, Poland, Portugal
Biogen

Completed

A Study to Assess the Efficacy and Safety of Nusinersen (ISIS 396443) in Participants With Later-onset Spinal Muscular Atrophy (SMA) (CHERISH)

Spinal Muscular Atrophy

United States, Germany, Spain, Canada, France, Hong Kong, Italy, Japan, Korea, Republic of, Sweden
Sanofi

Terminated

Phase 2 Study for SAR443820 in Participants With Amyotrophic Lateral Sclerosis (ALS) (HIMALAYA)

Amyotrophic Lateral Sclerosis

Netherlands, China, Poland, Italy, Belgium, United States, Canada, France, Germany, Japan, Spain, Sweden, United Kingdom

Clinical Trials on Neuronal Ceroid-Lipofuscinoses in France

Sponsors and Collaborators

Medical Conditions

Drug Interventions

CROs by country

CROs in Myanmar

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