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- US Clinical Trials Registry
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Clinical Trials on Neutral Lipid Storage Disease With Myopathy
Total 1894 results
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University of MinnesotaRecruitingGaucher DiseaseUnited States
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TakedaNot yet recruiting
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Duke UniversityRecruiting
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TakedaCompletedGaucher DiseaseUnited States
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ShireCompletedGaucher DiseaseIndia
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PfizerCompleted
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ShireQuintiles, Inc.Completed
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ISU Abxis Co., Ltd.CompletedGaucher DiseaseAustralia
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ProtalixCompleted
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ISU Abxis Co., Ltd.Withdrawn
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Genzyme, a Sanofi CompanyCompleted
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ProtalixCompleted
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University Hospital, Clermont-FerrandUnknown
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Brigham and Women's HospitalGenzyme, a Sanofi CompanyUnknown
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ProtalixCompleted
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ShireTerminated
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TakedaCompleted
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Genzyme, a Sanofi CompanyCompletedGaucher DiseaseCanada, Russian Federation, Tunisia
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ShireCompleted
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PfizerCompletedGaucher DiseaseUnited Kingdom, Canada, Israel, United States, Australia, Spain
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PfizerCompletedGaucher DiseaseChile, United Kingdom, Canada, Spain, Israel, United States, Australia, South Africa
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PfizerCompletedGaucher DiseaseIsrael, Paraguay, South Africa
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Yasmeen Abd Elbaset HamzaaUnknownGaucher Disease
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Genzyme, a Sanofi CompanyCompletedGaucher DiseaseUnited States
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Genzyme, a Sanofi CompanyCompletedGaucher DiseaseUnited States, Sweden, India, Netherlands, Austria, Japan, China, Serbia, France, Croatia, Australia, Portugal, Canada, Brazil, Greece, Romania, Russian Federation
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ISU Abxis Co., Ltd.Completed
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | Cholesterol Ester Storage Disease(CESD) | LAL-DeficiencyFrance, United States, United Kingdom, Czechia
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | LAL-Deficiency | Cholesterol Ester Storage Disease (CESD)France, United Kingdom, United States, Canada, Czechia
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National Institute of Neurological Disorders and...Completed
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University of MinnesotaRecruitingGaucher Disease, Type 3United States
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TakedaActive, not recruiting
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Shaare Zedek Medical CenterShireCompletedGaucher Disease, Type 1
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Shaare Zedek Medical CenterPfizerCompletedGaucher Disease, Type 1
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National Taiwan University HospitalSanofiCompleted
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ShireCompletedGaucher Disease, Type 1Israel, Paraguay, Argentina, Russian Federation, Tunisia
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ShireCompletedGaucher Disease, Type 1Spain, Israel, United States, India, Paraguay, United Kingdom, Russian Federation, Tunisia, Argentina
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PfizerWithdrawnType 1 Gaucher DiseaseUnited States
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National Taiwan University HospitalActelionUnknown
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ActelionCompletedGaucher Disease Type 1United States, Taiwan, Canada, Spain, Australia, France, Brazil, Hungary, Czechia, Germany, Italy, Netherlands, United Kingdom
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National Institute of Neurological Disorders and...CompletedType 2 Gaucher DiseaseUnited States
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Exsar CorporationSuspendedType I Gaucher DiseaseUnited States
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Hospital Universitario Reina Sofia de CordobaSpanish Society of Family and Community MedicineCompletedPatients With DyslipidemiaSpain
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AstraZenecaCompletedPatients With DyslipidemiaBrazil
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SanofiCompletedGaucher's DiseaseUnited States
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ShireCompletedGaucher DiseaseUnited States, Spain, United Kingdom, Israel
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ShireCompletedGaucher DiseaseIsrael, Romania, Serbia