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Clinical Trials on Nondystrophic Myotonia in United States
Total 234 results
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Richard Barohn, MDRare Diseases Clinical Research Network; Office of Rare Diseases (ORD)CompletedMyotonic Disorders | Myotonia Congenita | Nondystrophic MyotoniasCanada, United States, United Kingdom
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Myotonic Dystrophy FoundationRecruitingMyotonic Dystrophy | Myotonic Dystrophy 1 | Steinert's Disease | Congenital Myotonic Dystrophy | PROMM (Proximal Myotonic Myopathy) | Steinert Disease | Dystrophia Myotonica 1 | Myotonic Dystrophy 2 | Dystrophia Myotonica | Dystrophia Myotonica 2 | Myotonia Dystrophica | Myotonic Dystrophy, Congenital | Myotonic... and other conditionsUnited States
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Ohio State UniversityGilead SciencesCompletedMyotonic Dystrophy 1 | Myotonia Congenita | Paramyotonia CongenitaUnited States
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Stanford UniversityBiogenActive, not recruitingMyotonic Dystrophy 1United States
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University of Texas Southwestern Medical CenterMassachusetts General HospitalRecruitingDystonia | Dystonia; Idiopathic | Dystonia, Primary | Dystonia, Secondary | Dystonia, Familial | Dystonia Disorder | Dystonias, Sporadic | Dystonia; Orofacial | Dystonia Lenticularis | Dystonia, Paroxysmal | Dystonia 6 | Dystonia 5 | Dystonia 8 | Dystonia 9 | Dystonia 19 | Dystonia 10 | Dystonia 11 | Dystonia 20 | Dystonia 12 | Dystonia... and other conditionsUnited States
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMuscular Dystrophy | Myotonic Dystrophy Type 2 | Myotonic Dystrophy Type 1 | Myotonic Dystrophy | Facioscapulohumeral Muscular Dystrophy | Steinert's Disease | Congenital Myotonic Dystrophy | PROMM (Proximal Myotonic Myopathy) | Myotonic Muscular DystrophyUnited States
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Richard Barohn, MDCompletedNon-Dystrophic Myotonia | MyotoniaUnited States, Canada, Italy, United Kingdom
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National Institute of Neurological Disorders and...TerminatedMyotonic Dystrophy Type-1 | Myotonic Dystrophy Type-2United States
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University College, LondonRecruitingNon-Dystrophic MyotoniaUnited Kingdom
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Avidity Biosciences, Inc.CompletedMyotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy Type 1 (DM1) | Myotonic Dystrophy 1 | Myotonic Muscular Dystrophy | DM1 | Dystrophy Myotonic | Steinert DiseaseUnited States
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National Institute of Neurological Disorders and...Active, not recruitingDystonia | Focal Dystonia | Musician's DystoniaUnited States
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Stanford UniversityUnknownMyotonic Dystrophy Type 1United States
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University of FloridaBachmann Strauss Dystonia & Parkinson Foundation, Inc.Completed
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PepGen IncRecruitingMyotonic Dystrophy 1United States, Canada
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University of RochesterCompletedMyotonic DystrophyUnited States
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Imsmed IncorporatedCompleted
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Massachusetts General HospitalRecruiting
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Expansion Therapeutics, Inc.CompletedMyotonic Dystrophy | Myotonic Dystrophy, Type 1 (DM1)United States
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University of Colorado, DenverCompleted
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National Institute of Neurological Disorders and...Completed
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Duke UniversityAmerican Academy of NeurologyNot yet recruiting
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Virginia Commonwealth UniversityRadboud University Medical Center; University of California, Los Angeles; University... and other collaboratorsRecruitingMyotonic Dystrophy 1United States, Netherlands, United Kingdom, New Zealand, Germany, Italy, Canada, France
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National Institute of Neurological Disorders and...CompletedOromandibular Dystonia | Cranial DystoniaUnited States
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Avidity Biosciences, Inc.Active, not recruitingNervous System Diseases | Genetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Neurodegenerative Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Heredodegenerative Disorders, Nervous System | Myotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy... and other conditionsUnited States
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University of MinnesotaCompleted
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National Institute of Neurological Disorders and...Completed
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University of FloridaAmerican Brain Foundation; NeuroneticsCompletedDystonia | Primary Cervical DystoniaUnited States
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Virginia Commonwealth UniversityUniversity of Western Ontario, Canada, Children's Health Research Institute; Fondazione Serena Onlus - Centro Clinico NeMO MilanoRecruitingCongenital Myotonic DystrophyUnited States, Italy, Canada
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Virginia Commonwealth UniversityRecruitingCongenital Myotonic Dystrophy | Childhood Myotonic Dystrophy | CDM | CHDMUnited States, Italy
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University of FloridaDystonia Medical Research FoundationTerminated
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National Institute of Neurological Disorders and...CompletedCervical Dystonia | Dystonia | Focal Dystonia | Movement DisorderUnited States
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National Institute of Neurological Disorders and...Completed
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National Institute of Neurological Disorders and...Prachaya Srivanitchapoom, MDTerminated
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National Institute of Neurological Disorders and...CompletedCervical Dystonia | Essential Tremor | Focal DystoniaUnited States
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Duke UniversityAmerican Academy of NeurologyRecruiting
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Wake Forest University Health SciencesRecruitingMyotonic Dystrophy Type 2United States
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University of MinnesotaNational Institutes of Health (NIH); National Center for Research Resources... and other collaboratorsCompletedDystonia, Focal, Task-specificUnited States
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Emory UniversityIpsenCompleted
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); University... and other collaboratorsCompletedMyotonic Dystrophy Type 1United States
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Vanderbilt University Medical CenterVanderbilt Institute for Clinical and Translational ResearchCompletedNervous System Diseases | Neurologic Manifestations | Movement Disorders | Neuromuscular Manifestations | Cervical Dystonia | Focal Dystonia | Signs and Symptoms | Spasmodic TorticollisUnited States
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Edward BurtonTerminated
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Dyne TherapeuticsRecruitingMyotonic Dystrophy Type 1 (DM1)United Kingdom, France, Netherlands, Italy, Germany, New Zealand
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Ionis Pharmaceuticals, Inc.CompletedMyotonic Dystrophy Type 1United States
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National Institute of Neurological Disorders and...Completed
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University of PennsylvaniaTeva Branded Pharmaceutical Products R&D, Inc.Active, not recruiting
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Kristina SimonyanNational Institute of Neurological Disorders and Stroke (NINDS)CompletedSpasmodic Dysphonia | Writer's Cramp | Singer's Dystonia | Musician's Focal Hand DystoniaUnited States
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Emory UniversitySuspended
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National Institute of Neurological Disorders and...Completed
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National Institute of Neurological Disorders and...Completed
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Henry Ford Health SystemAllerganCompleted