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Clinical Trials on Oculopharyngeal Muscular Dystrophy in United Kingdom
Total 17754 results
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophyKorea, Republic of, Chile, Taiwan, China, United States, United Kingdom, Netherlands, Spain, Australia, Norway, Russian Federation, Greece, Italy, Turkey, Mexico, Canada, Hong Kong, New Zealand, Ukraine
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ItalfarmacoSyneos HealthCompletedDuchenne Muscular DystrophyUnited States, Italy, Spain, Canada, Belgium, France, Germany, Israel, Netherlands, Serbia, United Kingdom
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PfizerTerminatedDuchenne Muscular DystrophyUnited States, Australia, Canada, United Kingdom, Japan, Bulgaria, Italy, Poland
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BioMarin PharmaceuticalNo longer availableDuchenne Muscular DystrophyUnited States, Germany, United Kingdom, Japan, Netherlands, France, Spain, Korea, Republic of, Italy, Belgium, Taiwan, Argentina, Australia, Bulgaria, Czechia, Israel, Norway, Poland, Russian Federation, Turkey
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Fulcrum TherapeuticsActive, not recruitingFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Canada, France, Spain
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Fulcrum TherapeuticsCompletedFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Canada, France, Spain
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Astellas Pharma IncTerminatedDuchenne Muscular Dystrophy (DMD)United States
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ItalfarmacoCromsourceEnrolling by invitationDuchenne Muscular DystrophySpain, United States, Canada, Belgium, France, Israel, Italy, Netherlands, Serbia, Germany, United Kingdom
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CureDuchenneRecruitingDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States
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ProQR TherapeuticsWithdrawnCorneal Diseases | Fuchs Endothelial Corneal Dystrophy | FECD3 | LRS | Descemet's Membrane DisorderUnited Kingdom
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aTyr Pharma, Inc.CompletedLimb-Girdle Muscular Dystrophies | Facioscapulohumeral Muscular DystrophyUnited States, Denmark, France
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Catabasis PharmaceuticalsCompletedMuscular Dystrophy, DuchenneUnited States, Canada, Australia, United Kingdom, Germany, Ireland, Israel, Sweden
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Hugo W. Moser Research Institute at Kennedy Krieger...Concord Hospital; FSHD Global Research FoundationCompletedFacioscapulohumeral Muscular DystrophyUnited States, Australia
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Hugo W. Moser Research Institute at Kennedy Krieger...Active, not recruitingFacioscapulohumeral Muscular DystrophyUnited States
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University of RochesterCompletedFacioscapulohumeral Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular Dystrophy (DMD)United States
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Sarepta Therapeutics, Inc.Hoffmann-La RocheActive, not recruitingDuchenne Muscular DystrophyUnited States, Japan, Taiwan, Belgium, Spain, Germany, Hong Kong, Italy, United Kingdom
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Sarepta Therapeutics, Inc.Active, not recruitingMuscular Dystrophy, DuchenneUnited States, Korea, Republic of, India, Slovenia, Turkey, United Kingdom, Germany, Switzerland, Spain, Czechia, France, Serbia, Taiwan, Netherlands, Mexico, Colombia, Denmark, New Zealand, Norway, Greece, Hungary, Ireland, Italy, Jo... and more
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States, Belgium, Israel, Spain, Canada, Australia, Switzerland, United Kingdom, France, China, Netherlands, Italy, Austria, Czechia
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular Dystrophy (DMD)United States
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Hoffmann-La RocheCompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, Australia, Japan, France, Netherlands, Spain, Argentina, Germany, Italy, United Kingdom, Sweden
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Prothelia, Inc.Cure CMD; The Bönnemann Laboratory, NINDS, National Institutes of Health; Oscar... and other collaboratorsCompletedMerosin Deficient Congenital Muscular DystrophyUnited States
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular DystrophyUnited States, Italy, Netherlands
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University of Kansas Medical CenterNational Institutes of Health (NIH)CompletedFacioscapulohumeral Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.TerminatedAn Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular DystrophyDuchenne Muscular DystrophyUnited States, Belgium, Canada, Spain, United Kingdom, Czechia, Germany, Israel, Bulgaria, France, Italy, Poland, Sweden
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PfizerActive, not recruitingDuchenne Muscular DystrophyUnited States, Spain, Belgium, Korea, Republic of, Taiwan, Canada, Australia, Germany, Japan, France, Italy, United Kingdom, Russian Federation, Israel, Switzerland
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Not yet recruiting
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The Emmes Company, LLCUltragenyx Pharmaceutical Inc; Parent Project Muscular Dystrophy; Department...RecruitingDuchenne Muscular DystrophyUnited States
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Massachusetts General HospitalBoston Children's HospitalRecruitingDuchenne Muscular DystrophyUnited States
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University of PittsburghRecruitingDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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Jerry R. MendellDuchenne Alliance; Milo TherapeuticsCompletedDuchenne Muscular DystrophyUnited States
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Cure Rare Disease, IncUniversity of Massachusetts, WorcesterActive, not recruiting
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Craig McDonald, MDCardero Therapeutics, Inc.Completed
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University of FloridaEngage Health Inc.CompletedDuchenne Muscular DystrophyUnited States
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University of FloridaCureDuchenneCompletedMuscular Dystrophy, DuchenneUnited States
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University of FloridaUnited States Department of DefenseCompletedDuchenne Muscular DystrophyUnited States
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Jerry R. MendellEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedDuchenne Muscular DystrophyUnited States
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Boston Children's HospitalBeth Israel Deaconess Medical CenterCompletedDuchenne Muscular DystrophyUnited States
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National Institute of Neurological Disorders and...CompletedMuscular Dystrophy | Muscular DiseaseUnited States
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Nationwide Children's HospitalNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedLimb-Girdle Muscular DystrophyUnited States
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Virginia Commonwealth UniversityRadboud University Medical Center; University of California, Los Angeles; University... and other collaboratorsRecruitingMyotonic Dystrophy 1United States, Netherlands, United Kingdom, New Zealand, Germany, Italy, Canada, France
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Cedars-Sinai Medical CenterCompleted
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Red Nucleus Enterprise Solutions, LLCRecruiting
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Virginia Commonwealth UniversityNorthwestern University; University of RochesterRecruitingDuchenne Muscular DystrophyUnited States
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University of FloridaRecruiting
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Phrixus Pharmaceuticals, Inc.Charley's FundTerminated
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Children's Hospital Medical Center, CincinnatiIpsen; Charley's FundCompletedDuchenne Muscular DystrophyUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoCompletedDuchenne Muscular DystrophyUnited States
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National Human Genome Research Institute (NHGRI)Completed