- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Oculopharyngeal Muscular Dystrophy in United Kingdom
Total 17748 results
-
Lupin Ltd.Active, not recruitingMyotonic DystrophyFrance, Germany, United Kingdom
-
Bionano GenomicsColumbia University; University of Iowa; Medical College of Wisconsin; Augusta... and other collaboratorsRecruitingIntellectual Disability | Autism Spectrum Disorder | Fragile X Syndrome | Developmental Disability | Congenital Anomaly | Facioscapulohumeral Muscular Dystrophy 1United States
-
Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States, Canada, Argentina, Australia, Israel, Italy
-
PTC TherapeuticsTerminatedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Germany, Brazil, Bulgaria, Chile, Czechia, Poland, Sweden, Switzerland, Turkey
-
Indiana University School of MedicineMuscular Dystrophy AssociationCompletedMuscular Dystrophy | Arrhythmia | Sudden Cardiac DeathUnited States
-
PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Brazil, Chile, Czechia, Sweden, Switzerland, Turkey, Germany, Poland
-
National Eye Institute (NEI)CompletedMacular DegenerationUnited States
-
University of Texas Southwestern Medical CenterRecruitingDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | Dilated Cardiomyopathy | Cardiomyopathy, Hypertrophic | Heart Failure With Reduced Ejection Fraction | Cardiac Sarcoidosis | Heart Failure With Preserved Ejection FractionUnited States
-
Oxford University Hospitals NHS TrustRecruitingRetinal Degeneration | Retinal Dystrophies | Retinal DiseaseUnited Kingdom
-
Astellas Institute for Regenerative MedicineCompletedStargardt's Macular DystrophyUnited States
-
Astellas Institute for Regenerative MedicineCompletedStargardt's Macular DystrophyUnited States
-
Stanford UniversityUnknownMyotonic Dystrophy Type 1United States
-
Great Ormond Street Hospital for Children NHS Foundation...CompletedIdiopathic Scoliosis | Spine Deformities | Neuromuscular DystrophyUnited Kingdom
-
University of RochesterCompletedMyotonic DystrophyUnited States
-
University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Imsmed IncorporatedCompleted
-
Massachusetts General HospitalRecruiting
-
Virginia Commonwealth UniversityUniversity of Western Ontario, Canada, Children's Health Research Institute; Fondazione Serena Onlus - Centro Clinico NeMO MilanoRecruitingCongenital Myotonic DystrophyUnited States, Italy, Canada
-
University of Kansas Medical CenterHoffmann-La Roche; Seattle Children's Hospital; University of Rochester; University... and other collaboratorsRecruitingFSHDUnited States, Canada, United Kingdom
-
National Institute of Nursing Research (NINR)CompletedCerebral Palsy | Neuromuscular DiseaseUnited States
-
Manhattan Eye, Ear & Throat HospitalNorthwell HealthWithdrawnPattern Dystrophy of MaculaUnited States
-
University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); University... and other collaboratorsCompletedMyotonic Dystrophy Type 1United States
-
Moorfields Eye Hospital NHS Foundation TrustCompletedRetinal Degeneration | Diabetic Retinopathy | Retinal Dystrophies | AMDUnited Kingdom
-
Stanford UniversityBiogenActive, not recruitingMyotonic Dystrophy 1United States
-
University of OxfordCompletedAge-related Macular Degeneration | Retinitis Pigmentosa | Inherited Retinal Dystrophies | Optic Nerve PathologyUnited Kingdom
-
Cure CMDRecruitingEmery-Dreifuss Muscular Dystrophy | Congenital Myasthenic Syndrome | Limb-Girdle Muscular Dystrophy | Congenital Muscular Dystrophy With ITGA7 (Integrin Alpha-7) Deficiency | Alpha-Dystroglycanopathy (Congenital Muscular Dystrophy and Abnormal Glycosylation of Dystroglycan With Severe Epilepsy) and other conditionsUnited States
-
Wake Forest University Health SciencesNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMyotonic Dystrophy Type 2United States
-
Legacy Health SystemDevers Eye Institute; Lions Eye Bank of Oregon Vision Research Laboratory; Fischer...UnknownFuchs' Corneal Endothelial DystrophyUnited States
-
Ionis Pharmaceuticals, Inc.CompletedMyotonic Dystrophy Type 1United States
-
Gillette Children's Specialty HealthcareUniversity of MinnesotaCompletedSpinal Muscular Dystrophy | Neuromuscular DisabilityUnited States
-
AMO Pharma LimitedRecruitingCongenital Myotonic DystrophyUnited States, Canada, Australia, New Zealand
-
Pixium Vision SACompletedRetinitis Pigmentosa | Choroideremia | Cone Rod DystrophyAustria, Spain, United Kingdom, France, Germany
-
Insmed IncorporatedMuscular Dystrophy AssociationCompleted
-
Boston Children's HospitalMuscular Dystrophy AssociationRecruitingCentronuclear Myopathy | Myotubular Myopathy | Nemaline Myopathy | Central Core Disease | Congenital Fiber Type Disproportion | Multiminicore Disease | Rigid Spine Muscular Dystrophy | Undefined Congenital MyopathyUnited States
-
State University of New York at BuffaloActive, not recruitingFuchs DystrophyUnited States
-
Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedCharcot-Marie-Tooth Disease | Facioscapulohumeral Muscular DystrophyUnited States, Spain, Canada
-
Harmony Biosciences, LLCActive, not recruitingMyotonic Dystrophy 1 | Excessive Daytime SleepinessUnited States, Canada
-
Wake Forest University Health SciencesTerminatedFuchs Dystrophy | Cystoid Macular EdemaUnited States
-
Medical College of WisconsinCompletedCataract | Fuchs' Corneal DystrophyUnited States
-
GlaxoSmithKlineCompleted
-
FDA Office of Orphan Products DevelopmentCompletedMuscular DystrophiesUnited States
-
Cornea Research Foundation of AmericaCompletedBullous Keratopathy | Fuchs' Endothelial Corneal Dystrophy | Iridocorneal Endothelial Syndrome | Posterior Polymorphous DystrophyUnited States
-
University College, LondonRecruitingNon-Dystrophic MyotoniaUnited Kingdom
-
Edgewise Therapeutics, Inc.CompletedMuscular DystrophiesUnited States
-
National Heart, Lung, and Blood Institute (NHLBI)Terminated
-
University of Texas Southwestern Medical CenterWithdrawnCorneal Epithelial DystrophyUnited States
-
Wake Forest University Health SciencesCompleted
-
Massachusetts Eye and Ear InfirmaryRecruitingFuchs' Endothelial Corneal DystrophyUnited States
-
Katherine MathewsNational Institute of Neurological Disorders and Stroke (NINDS)Recruiting
-
King's College LondonUniversity College, LondonCompletedRecessive Dystrophic Epidermolysis BullosaUnited Kingdom