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Clinical Trials on Olivopontocerebellar Atrophies
Total 1090 results
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Nippon Shinyaku Co., Ltd.Active, not recruiting
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Craig McDonald, MDCardero Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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PfizerTerminatedA Low Interventional Study to Monitor Activity Using Wearable Sensors in Duchenne Muscular DystrophyDuchenne Muscular Dystrophy (DMD)United States
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Sarepta Therapeutics, Inc.Completed
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University Children's Hospital, ZurichUnknownDuchenne / Becker Muscular DystrophySwitzerland
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Benha UniversityCompletedDuchenne Muscular Dystrophy | Inflammatory MyopathyEgypt
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Centre d'Investigation Clinique et Technologique...UnknownHeart, Respiratory, Disease, FunctionalFrance
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University Hospital, Basel, SwitzerlandCompletedDuchenne's Muscular Dystrophy (DMD)Switzerland
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyUnited States, Netherlands, Belgium, Germany, Argentina, Brazil, France, Italy, Sweden, Turkey
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Kessler FoundationThe Craig H. Neilsen FoundationUnknownSkeletal Muscle Hypertrophy | Nervous System | Atrophy, Disuse | Disuse Osteoporosis | Structural; MarkerUnited States
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University Hospital, BonnForschungszentrum Juelich; The Marigold Foundation; Life and Brain Center BonnCompletedMyotonic Dystrophy 1 | Myotonic Dystrophy 2
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Shriners Hospitals for ChildrenCompletedDuchenne Muscular DystrophyUnited States
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Santhera PharmaceuticalsCompletedDuchenne Muscular Dystrophy (DMD)Belgium
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Prof. Dr. Volker ViereckActive, not recruitingVulvar Lichen Sclerosus | Chronic Skin DiseaseSwitzerland
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PYC TherapeuticsRecruitingOptic Atrophies, Hereditary | Autosomal Dominant Optic Atrophy | Optic Atrophy, Autosomal Dominant | Kjer Optic AtrophyAustralia
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Hoffmann-La RocheAssociation Française contre les Myopathies (AFM), ParisCompletedSpinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type III Non AmbulantGermany, Italy, France, Belgium, Poland, Netherlands, United Kingdom
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Wake Forest University Health SciencesNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMyotonic Dystrophy Type 2United States
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Virginia Commonwealth UniversityRecruitingCongenital Myotonic Dystrophy | Childhood Myotonic Dystrophy | CDM | CHDMUnited States, Italy
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Medical University of GdanskRecruitingMuscular Dystrophy, DuchennePoland
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University of OsloOslo University Hospital; Vikersund Rehabilitation CenterCompletedMyotonic Dystrophy Type 1 (DM1)Norway
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Stanford UniversityBiogenActive, not recruitingMyotonic Dystrophy 1United States
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University of OregonNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedSyndrome | Pain | Muscle Weakness | Tendinopathy | Shoulder Pain | Acute Pain | Impairment | Goals | Pathology | Injury | Infiltration | AtrophicUnited States
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McMaster UniversityCompletedMuscular Dystrophies | Myotonic Dystrophy 1Canada
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Expansion Therapeutics, Inc.CompletedMyotonic Dystrophy | Myotonic Dystrophy, Type 1 (DM1)United States
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Hugo W. Moser Research Institute at Kennedy Krieger...Johns Hopkins UniversityTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States
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Children's Hospital of Eastern OntarioJesse's Journey-The Foundation for Gene and Cell TherapyCompletedDuchenne Muscular DystrophyCanada
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Rigshospitalet, DenmarkUnknownFacioscapulohumeral Muscular Dystrophy 1aDenmark
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Cure CMDCongenital Muscle Disease International RegistrWithdrawnLAMA2-MD (Merosin Deficient Congenital Muscular Dystrophy, MDC1A)United States
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Monica Levy AndersenCompletedOther Diseases or ConditionsBrazil
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PTC TherapeuticsMuscular Dystrophy AssociationCompletedDuchenne Muscular DystrophyUnited States
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Novartis Gene TherapiesActive, not recruitingSMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type I | Spinal Muscular Atrophy Type IIIUnited States, Belgium, France, Japan, United Kingdom, Italy, Taiwan, Australia, Canada
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Argo SanteGenSight BiologicsCompleted
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Vertex Pharmaceuticals IncorporatedRecruitingMyotonic Dystrophy Type 1 (DM1)United Kingdom, Canada, Australia
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Centre Hospitalier Universitaire de NiceRecruitingFacioscapulohumeral Muscular Dystrophy Type 2France, Italy, Spain
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Assistance Publique - Hôpitaux de ParisNot yet recruitingMyotonic Dystrophy 1 | Steinert's Disease | MetforminFrance
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Dyne TherapeuticsRecruitingMyotonic Dystrophy Type 1 (DM1)United Kingdom, France, Netherlands, Italy, Germany, New Zealand
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The Emmes Company, LLCJain Foundation; Coalition to Cure Calpain 3 (C3)Terminated
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Swiss Federal Institute of TechnologyCompletedMuscle Weakness | Muscular Dystrophies | Muscular Dystrophy | Muscular Dystrophy, Facioscapulohumeral | Scapular Dyskinesis | Muscular WeaknessGermany, Switzerland
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PTC TherapeuticsTerminatedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Germany, Brazil, Bulgaria, Chile, Czechia, Poland, Sweden, Switzerland, Turkey
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Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | Upper Limb Function | Respiratory Function Test
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Radboud University Medical CenterAssistance Publique - Hôpitaux de Paris; Ludwig-Maximilians - University of... and other collaboratorsCompletedMyotonic Dystrophy Type 1Netherlands, France, Germany, United Kingdom
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Grete Andersen, MDCompletedFSHD - Facioscapulohumeral Muscular DystrophyDenmark
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Virginia Commonwealth UniversityEdgewise Therapeutics, Inc.RecruitingMuscular Dystrophies | Becker Muscular Dystrophy | Muscular Dystrophy in Children | Muscular Dystrophy, BeckerUnited States, New Zealand, United Kingdom
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Université du Québec à ChicoutimiRecruitingMyotonic Dystrophy Type 1 (DM1)Canada
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Memorial Sloan Kettering Cancer CenterCompletedBreast Cancer | Atrophic VaginitisUnited States
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Sahra ŞirvanEnrolling by invitationDuchenne Muscular DystrophyTurkey
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ItalfarmacoCompletedDuchenne and Becker Muscular Dystrophy | Polycytemia VeraCanada
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Universidad de AlmeriaCompletedNeurologic Disorder | Pediatric Disorder | Duchenne | Sensorimotor Disorder NosSpain
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular DystrophyUnited States
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Brazil, Chile, Czechia, Sweden, Switzerland, Turkey, Germany, Poland