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Clinical Trials on Osteosclerosis in United Kingdom
Total 20 results
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InterMuneCompletedOsteopetrosisUnited States
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Lundquist Institute for Biomedical Innovation at...University of Minnesota; Horizon Pharma Ireland, Ltd., Dublin IrelandCompleted
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Masonic Cancer Center, University of MinnesotaTerminated
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St. Jude Children's Research HospitalTerminated
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University of ChicagoTerminated
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Masonic Cancer Center, University of MinnesotaCompleted
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Indiana UniversityHorizon Pharma Ireland, Ltd., Dublin IrelandCompleted
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National Institute of Arthritis and Musculoskeletal...RecruitingRheumatic DiseaseUnited States
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Rocket Pharmaceuticals Inc.California Institute for Regenerative Medicine (CIRM)TerminatedInfantile Malignant OsteopetrosisUnited States
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Eunice Kennedy Shriver National Institute of Child...CompletedBone Diseases, Metabolic | Osteogenesis Imperfecta | Melorheostosis | Connective Tissue DisordersUnited States
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Bellicum PharmaceuticalsTerminatedLymphoma, Non-Hodgkin | Acute Lymphoblastic Leukemia | Primary Immunodeficiency | Anemia, Sickle Cell | Hemoglobinopathies | Fanconi Anemia | Anemia, Aplastic | Myelodysplastic Syndrome | Thalassemia | Cytopenia | Diamond Blackfan Anemia | Osteopetrosis | Leukemia, Acute Myeloid (AML), ChildUnited Kingdom, Italy
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Carestream Health, Inc.CompletedOtosclerosis | Cholesteatoma | Chronic Otitis Media | Pulsatile Tinnitus | CerebroSpinal Fluid (CSF) Leak | OtospongiosisUnited States, Belgium, France
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VA Office of Research and DevelopmentFather Flanagan's Boys' HomeCompletedHearing Loss, Sensorineural | Otitis Media With Effusion | Hearing Loss, Conductive | Otosclerosis | Cholesteatoma | Tympanic Membrane Perforation | Hearing Loss, Mixed Conductive-SensorineuralUnited States
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Columbia UniversityUnknownSevere Combined Immunodeficiency | Fanconi Anemia | Bone Marrow Failure | OsteopetrosisUnited States
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Wake Forest University Health SciencesTerminatedAcute Myeloid Leukemia | Acute Lymphoblastic Leukemia | Chronic Myeloid Leukemia | Myelodysplastic Syndrome | Immune Deficiency | Lymphomas | Bone Marrow Failure | Osteopetrosis | HemoglobinopathyUnited States
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Christopher DvorakNo longer availableAcute Myeloid Leukemia | Leukocyte Disorders | Acute Lymphoblastic Leukemia | Chronic Myeloid Leukemia | Myelodysplastic Syndrome | Cytopenias | Immune Deficiency | Lymphomas | Bone Marrow Failure | Osteopetrosis | Hemoglobinopathy | Anemia Due to Intrinsic Red Cell AbnormalityUnited States
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Bellicum PharmaceuticalsActive, not recruitingStudy of Gene Modified Donor T-cells Following TCR Alpha Beta Positive Depleted Stem Cell TransplantLymphoma, Non-Hodgkin | Myelodysplastic Syndromes | Acute Lymphoblastic Leukemia | Anemia, Aplastic | Primary Immune Deficiency Disorder | Cytopenia | Osteopetrosis | Leukemia, Acute Myeloid (AML), Child | Hemoglobinopathy in ChildrenUnited States
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University of PittsburghRecruitingLysosomal Storage Diseases | Leukodystrophy | Niemann-Pick Diseases | Batten Disease | Gaucher Disease | Krabbe Disease | Alpha-Mannosidosis | Osteopetrosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | GM1 Gangliosidoses | MPS I | MPS II | Vanishing White Matter Disease | Multiple Sulfatase Deficiency... and other conditionsUnited States
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Children's Hospital Los AngelesCompletedGranuloma | Anemia | Thrombocytopenia | Neutropenia | Sickle Cell Disease | Thalassemia | Niemann-Pick Disease | Wiskott-Aldrich Syndrome | Osteopetrosis | Fucosidosis | Chediak Higashi Syndrome | Hurler DiseaseUnited States
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Masonic Cancer Center, University of MinnesotaRecruitingHurler Syndrome | Sphingolipidoses | Peroxisomal Disorders | Metachromatic Leukodystrophy | Alpha-Mannosidosis | Hunter Syndrome | Mucopolysaccharidosis Disorders | Maroteaux Lamy Syndrome | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Glycoprotein Metabolic Disorders | Recessive Leukodystrophies | Globoid... and other conditionsUnited States