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Clinical Trials on Paroxysmal Nocturnal Hemoglobinuria (PNH) in United Kingdom
Total 83 results
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Alexion PharmaceuticalsAchillion, a wholly owned subsidiary of AlexionCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United Kingdom, New Zealand, Korea, Republic of, Italy
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Alnylam PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)Spain, United Kingdom
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Apellis Pharmaceuticals, Inc.RecruitingParoxysmal Nocturnal Hemoglobinuria (PNH) | Paroxysmal HemoglobinuriaMalaysia, United States, Czechia, France, Netherlands, Serbia, Spain, Thailand, United Kingdom
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Alexion PharmaceuticalsTerminatedParoxysmal Nocturnal Hemoglobinuria (PNH)United States, Czech Republic, Italy, Poland, United Kingdom
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King's College Hospital NHS TrustCompletedParoxysmal Nocturnal HaemoglobinuriaUnited Kingdom
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AlexionActive, not recruitingParoxysmal Nocturnal Hemoglobinuria (PNH)United Kingdom, Italy, Canada, Korea, Republic of, New Zealand, Spain, Turkey
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Ra PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United Kingdom, Australia, Canada, Denmark, Finland, Germany, Hungary, New Zealand
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Ra PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United States
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AlexionCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United States, Korea, Republic of, Canada, France, Germany, Spain, United Kingdom, Japan, Australia, Italy, Netherlands
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BioCryst PharmaceuticalsTerminatedBCX9930 for Treatment of PNH in Subjects With Inadequate Response to C5 Inhibitor Therapy (REDEEM-1)Paroxysmal Nocturnal Hemoglobinuria (PNH)United Kingdom, Hungary, France, Italy, Spain
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AlexionCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)Belgium, France, Italy, Japan, Spain, Taiwan, United Kingdom, United States, Canada, Czechia, Germany, Sweden, Singapore, Korea, Republic of, Russian Federation, Austria, Poland, Argentina, Australia, Brazil, Estonia, Malaysia, Mexico, Thaila... and more
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Apellis Pharmaceuticals, Inc.CompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United States
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Alexion Pharmaceuticals, Inc.Achillion, a wholly owned subsidiary of AlexionCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)United Kingdom, United States, Italy
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Regeneron PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)Hong Kong, Hungary, Korea, Republic of, Malaysia, United Kingdom
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Ra Pharmaceuticals, Inc.TerminatedParoxysmal Nocturnal Hemoglobinuria (PNH)United States, Australia, Canada, Finland, Germany, Hungary, New Zealand, United Kingdom
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BioCryst PharmaceuticalsActive, not recruitingParoxysmal Nocturnal Hemoglobinuria | PNHUnited Kingdom, Austria, South Africa
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Novartis PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)China, Germany, Singapore, Korea, Republic of, Italy, United Kingdom, Malaysia, France
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Novartis PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH)Italy, Japan, Taiwan, Germany, France, United Kingdom, Spain, Korea, Republic of, Czechia, Brazil, Netherlands, United States
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Alexion PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria | PNHAustralia, France, United Kingdom, Belgium, Germany, Netherlands, Ireland, United States, Switzerland, Italy
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AKARI TherapeuticsEnrolling by invitationParoxysmal Nocturnal Hemoglobinuria (PNH)United States
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Alexion PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria | PNHKorea, Republic of, Canada, France, Germany, Spain, Taiwan, United Kingdom
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Memorial Sloan Kettering Cancer CenterNational Cancer Institute (NCI)CompletedLeukemia | Lymphoblastic Lymphoma | Myelodysplastic Syndrome | Paroxysmal Nocturnal Hemoglobinuria (PNH) | Allogeneic Stem Cell Transplant | Non-HodgkinsUnited States
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Alexion PharmaceuticalsCompletedParoxysmal Hemoglobinuria, NocturnalUnited States, Australia, Belgium, Canada, Germany, Italy, Spain, Sweden, United Kingdom, France, Ireland, Netherlands
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National Heart, Lung, and Blood Institute (NHLBI)CompletedParoxysmal Hemoglobinuria, NocturnalUnited States
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Alexion PharmaceuticalsCompletedParoxysmal Nocturnal HemoglobinuriaUnited Kingdom
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BioCryst PharmaceuticalsCompletedParoxysmal Nocturnal HemoglobinuriaUnited Kingdom, Austria, South Africa
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National Heart, Lung, and Blood Institute (NHLBI)RecruitingParoxysmal Nocturnal Hemoglobinuria (PNH) | Severe Aplastic Anemia (SAA) | Hypo-Plastic Myelodysplastic Syndrome (MDS)United States
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Sidney Kimmel Comprehensive Cancer Center at Johns...CompletedAplastic Anemia | Paroxysmal Hemoglobinuria, NocturnalUnited States
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David Rizzieri, MDCompletedSickle Cell Anemia | Pure Red Cell Aplasia | Paroxysmal Nocturnal Hemoglobinuria (PNH) | Severe Aplastic AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedParoxysmal HemoglobinuriaUnited States
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AlexionCompletedParoxysmal Nocturnal HemoglobinuriaFrance, United Kingdom, Norway, Russian Federation, Netherlands, United States
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Regeneron PharmaceuticalsCompletedParoxysmal Nocturnal HemoglobinuriaUnited Kingdom
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Aplastic Anemia and MDS International FoundationNational Organization for Rare DisordersRecruiting
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Omeros CorporationRecruitingParoxysmal Nocturnal HemoglobinuriaSwitzerland, Germany, Ukraine, United Kingdom
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Omeros CorporationRecruitingParoxysmal Nocturnal HemoglobinuriaGermany, Greece, Switzerland, United Kingdom
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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University of UtahNational Institutes of Health (NIH)CompletedHemoglobinuria, ParoxysmalUnited States
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Apellis Pharmaceuticals, Inc.CompletedParoxysmal Nocturnal HemoglobinuriaUnited States, France, Russian Federation, Korea, Republic of, Canada, Germany, Australia, Japan, Spain, Belgium, United Kingdom
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Alexion PharmaceuticalsCompletedHemoglobinuria, ParoxysmalUnited States
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BioCryst PharmaceuticalsActive, not recruitingParoxysmal Nocturnal HemoglobinuriaUnited Kingdom, Hungary, France, Spain, Malaysia, South Africa, Korea, Republic of
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Regeneron PharmaceuticalsTerminatedParoxysmal Nocturnal HemoglobinuriaHong Kong, Korea, Republic of, Malaysia, Hungary, Taiwan, United Kingdom
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Jonsson Comprehensive Cancer CenterCompleted
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Regeneron PharmaceuticalsCompletedParoxysmal Nocturnal HemoglobinuriaKorea, Republic of, Taiwan, Malaysia, Hong Kong, Hungary, United Kingdom
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Alexion Pharmaceuticals, Inc.Active, not recruitingParoxysmal Nocturnal HemoglobinuriaFrance, Italy, Spain, United States, Thailand, Korea, Republic of, United Kingdom, Israel, Czechia, Greece, Poland, Brazil, Japan, Canada, Malaysia
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Novartis PharmaceuticalsRecruitingParoxysmal Nocturnal HemoglobinuriaFrance, Spain, Italy, Turkey, Germany, United States, Korea, Republic of, United Kingdom
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Regeneron PharmaceuticalsTerminatedParoxysmal Nocturnal HemoglobinuriaUnited States
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Regeneron PharmaceuticalsRecruitingParoxysmal Nocturnal HemoglobinuriaMexico, Korea, Republic of, Turkey, Italy, United Kingdom, Thailand, Poland, Singapore, Spain, Taiwan, Canada, Japan, United States, Malaysia, Greece, Romania, Hungary
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Alexion Pharmaceuticals, Inc.RecruitingParoxysmal Nocturnal HemoglobinuriaUnited States
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Novartis PharmaceuticalsRecruitingParoxysmal Nocturnal HemoglobinuriaUnited States, Korea, Republic of, Singapore, Germany, Taiwan, Italy, Turkey, France, Malaysia, Lithuania, Netherlands, United Kingdom, Japan, Czechia, Spain, China, Brazil
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Hoffmann-La RocheChugai PharmaceuticalRecruitingParoxysmal Nocturnal HemoglobinuriaUnited States, Korea, Republic of, Spain, Germany, Italy, Sweden, Netherlands, Japan, Belgium, Greece, Colombia, Saudi Arabia, Turkey, Poland, Ireland, Brazil, Canada, Czechia, Estonia, France, Hong Kong, Singapore, Taiwan, United Kingdom and more