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Clinical Trials on Pediatric: Genetic Syndrome
Total 47655 results
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Eisai Inc.AvailableAn Extended Access Program (EAP) for Participants Who Have Completed Rufinamide Study E2080-G000-303Lennox Gastaut SyndromePoland
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John Carroll UniversityUniversity Hospital Southampton NHS Foundation TrustActive, not recruitingPTEN Hamartoma Tumor SyndromeUnited States, United Kingdom
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Eisai Co., Ltd.CompletedLennox-Gastaut SyndromeJapan
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Institution de LavignyWithdrawnLennox-Gastaut SyndromeSwitzerland
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Lundbeck LLCCompletedLennox-Gastaut Syndrome
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INSYS Therapeutics IncWithdrawn
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Beijing Pins Medical Co., LtdQilu Hospital of Shandong University; Qingdao University; Yantai Yuhuangding... and other collaboratorsUnknownLennox-Gastaut SyndromeChina
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Myriad Genetic Laboratories, Inc.Myriad Genetics, Inc.CompletedHereditary CancerUnited States
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University Hospital, Strasbourg, FranceTerminatedPediatric Lung Ultrasound | Pediatric Chest Radiography | Pediatric Lung DiagnosisFrance
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University of BirminghamCompletedCancer | Pediatric ALL | Pediatric Solid Tumor | Pediatric AMLUnited Kingdom, Australia, Netherlands
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Xuanwu Hospital, BeijingNot yet recruitingLennox Gastaut SyndromeChina
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EpygenixNot yet recruiting
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Eisai LimitedCompletedLennox-Gastaut SyndromeJapan
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Khon Kaen UniversityCompleted
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Eisai LimitedCompletedLennox-Gastaut SyndromeFrance, United Kingdom, Germany, Spain, Denmark, Austria, Italy, Sweden
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NovartisCompletedFamilial Cold Autoinflammatory Syndrome | Cryopyrin-Associated Periodic Syndromes | Neonatal Onset Multisystem Inflammatory Disease | Muckle Wells SyndromeUnited States, Germany, Italy, Spain, United Kingdom, Turkey, France, Belgium, India
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TakedaNot yet recruitingDravet Syndrome (DS) | Lennox-Gastaut Syndrome (LGS)
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TakedaRecruitingDravet Syndrome (DS) | Lennox-Gastaut Syndrome (LGS)Spain
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Hospital de la RiberaUnknownDepression | Delirium | Malnutrition | Hip Fractures | GERIATRIC SYNDROMES | GERIATRIC ASSESSMENTSpain
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TakedaRecruitingDravet Syndrome (DS) | Lennox-Gastaut Syndrome (LGS)United Kingdom, Denmark
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TakedaActive, not recruitingEpilepsy | Dravet Syndrome (DS) | Lennox-Gastaut Syndrome (LGS)United States, Canada, Australia, China, Israel, Poland, Spain, Portugal
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Mansoura UniversityCompleted
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TakedaRecruitingLennox Gastaut Syndrome (LGS) | Dravet Syndrome (DS)United States, China, Spain, France, Belgium, Australia, Brazil, Canada, Germany, Greece, Hungary, Italy, Japan, Latvia, Netherlands, Poland, Serbia, Mexico, Russian Federation, Ukraine
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National Human Genome Research Institute (NHGRI)CompletedGenetics | Birth Defects | Genetic Disease | Genetic Linkage | Genetic VariationUnited States
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Boston Children's HospitalMassachusetts General Hospital; Mayo Clinic; Karolinska University Hospital; Baylor... and other collaboratorsActive, not recruitingAplastic Anemia | Dyskeratosis Congenita | Hoyeraal Hreidarsson Syndrome | Revesz SyndromeUnited States, Norway, Sweden
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Azienda Policlinico Umberto ICompletedPediatrics, Colon Capsule EndoscopyItaly
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Nationwide Children's HospitalActive, not recruitingPediatric Sepsis-induced MODSUnited States
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argenxNot yet recruiting
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argenxRecruitingCongenital Myasthenic SyndromeSpain, Italy, France, United Kingdom, United States, Canada
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Catalyst Pharmaceuticals, Inc.CompletedMyasthenic Syndromes, CongenitalUnited States
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Nicklaus Children's Hospital f/k/a Miami Children...Rady Pediatric Genomics & Systems Medicine InstituteRecruiting
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Mayo ClinicCompletedCongenital Myasthenic SyndromeUnited States
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Institut de Myologie, FranceAssistance Publique - Hôpitaux de ParisCompletedCongenital Myasthenic Syndrome
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Gillette Children's Specialty HealthcareTerminatedDravet Syndrome | Lennox-Gastaut SyndromeUnited States
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Jazz PharmaceuticalsCompletedEpilepsy | Dravet Syndrome | Lennox-Gastaut Syndrome
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Handok Inc.Terminated
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Federal Research Institute of Pediatric Hematology...UnknownAnesthesia | Pediatric Cancer | Beta-Thalassemia | Hepatic Metastases | Pediatric Tumor | Pediatric HepatoblastomaRussian Federation
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Zogenix International Limited, Inc., a subsidiary...CompletedDravet Syndrome | Lennox Gastaut SyndromeUnited States
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Yonsei UniversityUnknownDravet Syndrome | Lennox Gastaut SyndromeKorea, Republic of
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InheRET, IncUniversity of MichiganEnrolling by invitationHereditary Cancer-Predisposing SyndromeUnited States
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Jazz PharmaceuticalsEvidilya S.r.l.Not yet recruitingDravet Syndrome | Lennox Gastaut SyndromeItaly
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Eisai Inc.TerminatedLennox-Gastaut Syndrome (LGS)Korea, Republic of, United States, Australia, Belgium, Japan, Czechia, India
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Gillette Children's Specialty HealthcareUniversity of MinnesotaWithdrawnDravet Syndrome | Lennox Gastaut Syndrome
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NovartisCompletedMuckle Wells SyndromeUnited States, Spain, United Kingdom, France, Germany, India
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Novartis PharmaceuticalsCompletedFamilial Cold Autoinflammatory Syndrome | Muckle-Wells Syndrome | Neonatal Onset Multisystem Inflammatory Disease | Cryopyrin-associated Periodic SyndromesGermany, France, Belgium, Canada, Spain, Switzerland, United Kingdom
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University of Illinois College of Medicine at PeoriaRady Children's Institute of Genomic MedicineActive, not recruitingGenetic Disease | Genetic SyndromeUnited States
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Novartis PharmaceuticalsCompletedFamilial Cold Autoinflammatory Syndrome | Muckle-Wells Syndrome | Neonatal Onset Multisystem Inflammatory Disease | Cryopyrin-associated Periodic SyndromesJapan
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Novartis PharmaceuticalsCompletedFamilial Cold Autoinflammatory Syndrome | Muckle-Wells Syndrome | Neonatal Onset Multisystem Inflammatory Disease | Cryopyrin-associated Periodic SyndromesGermany, France, Belgium, Canada, Spain, Switzerland, United Kingdom
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SK Life Science, Inc.RecruitingSeizures | Lennox Gastaut SyndromeUnited States, Korea, Republic of, Taiwan, Colombia, Australia, Poland, Serbia, Mexico, Spain, Greece, Italy, Portugal, Germany, Argentina, Israel
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Gustave Roussy, Cancer Campus, Grand ParisCompleted