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Clinical Trials on Philadelphia Chromosome in United States
Total 599 results
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Montefiore Medical CenterJazz Pharmaceuticals; Foundation for Prader-Willi ResearchActive, not recruitingPrader-Willi SyndromeUnited States
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Duke UniversityNovartis; National Institutes of Health (NIH); National Center for Research Resources...TerminatedPrader-Willi SyndromeUnited States
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Wen-Hann TanBaylor College of Medicine; University of California, San Francisco; Vanderbilt... and other collaboratorsCompleted
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Eunice Kennedy Shriver National Institute of Child...CompletedSelf-Injurious Behavior | Prader-Willi SyndromeUnited States
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University of California, San DiegoBaylor College of Medicine; Boston Children's Hospital; Rare Diseases Clinical... and other collaboratorsCompletedNervous System Diseases | Angelman SyndromeUnited States
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Children's Hospital Los AngelesCompletedPrader-Willi SyndromeUnited States
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IpsenCompletedRenal Insufficiency, Chronic | Pituitary Diseases | Dwarfism | Turner SyndromeFrance, Germany, Finland, Spain, Belgium, Czechia, Denmark, Greece, Italy, Romania, Russian Federation, Slovakia, Ukraine, United Kingdom
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Zafgen, Inc.CompletedObesity | Prader-Willi Syndrome | Over-weightUnited States
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Bionano GenomicsColumbia University; University of Iowa; Medical College of Wisconsin; Augusta... and other collaboratorsRecruitingIntellectual Disability | Autism Spectrum Disorder | Fragile X Syndrome | Developmental Disability | Congenital Anomaly | Facioscapulohumeral Muscular Dystrophy 1United States
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Merck KGaA, Darmstadt, GermanyCompletedGrowth Hormone Deficiency | Turner SyndromeArgentina, Australia, Austria, Canada, France, Germany, Italy, Norway, Russian Federation, Singapore, Spain, Sweden, United Kingdom
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Institute for Neurodegenerative DisordersCompletedParkinson Disease | Alzheimer Disease | Mild Cognitive Impairment | Fragile X Syndrome | Huntington Disease | Autistic Spectrum DisordersUnited States
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Hoffmann-La RocheTerminatedDown SyndromeUnited States
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Boston Children's HospitalBaylor College of Medicine; Vanderbilt University Medical Center; Children's... and other collaboratorsCompleted
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Aardvark Therapeutics, Inc.Children's Hospital Colorado; Stanford UniversityRecruiting
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Ionis Pharmaceuticals, Inc.BiogenActive, not recruitingAngelman SyndromeUnited States, Israel, Italy, France, Australia, United Kingdom
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University of Kansas Medical CenterEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedBody Weight | Weight Loss | Body Weight Changes | Intellectual Disability | Developmental Disabilities | Down SyndromeUnited States
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Duke UniversityCanadian Institutes of Health Research (CIHR); National Institutes of Health... and other collaboratorsCompleted
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ProgenaBiomeRecruitingAutism Spectrum Disorder | Autistic Disorder | Autism | Autism, Akinetic | Autism; Atypical | Autism; Psychopathy | Autism Fragile Syndrome X | Autism With High Cognitive Abilities | Autism-Related Speech Delay | Autism, Susceptibility to, 6 | Autism Spectrum Disorder High-Functioning | Autistic Thinking | Autism... and other conditionsUnited States
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Vanda PharmaceuticalsRecruitingSleep Disturbances in Smith-Magenis SyndromeUnited States
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Montefiore Medical CenterRecruitingHyperphagia | Prader-Willi SyndromeUnited States
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Montefiore Medical CenterFoundation for Prader-Willi ResearchCompletedHyperphagia | Prader-Willi SyndromeUnited States
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University of HartfordUniversita di VeronaTerminatedCerebral Palsy | Down Syndrome | Autism | Balance | PostureUnited States
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University of Wisconsin, MadisonUltragenyx Pharmaceutical IncCompletedPrader-Willi Syndrome | Angelman SyndromeUnited States
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University of Wisconsin, MilwaukeeCompletedWilliams SyndromeUnited States
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OPKO Health, Inc.Elan PharmaceuticalsCompletedDown SyndromeUnited States
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Rutgers, The State University of New JerseyCompletedObesity | Prader-Willi SyndromeUnited States
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National Institute of Mental Health (NIMH)RecruitingWilliams Syndrome | DuplicationUnited States
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Weill Medical College of Cornell UniversityNational Institutes of Health (NIH); PWSAUSATerminatedPrader-willi SyndromeUnited States
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NYU Langone HealthWinthrop University HospitalWithdrawn
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Massachusetts General HospitalCompleted
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University of FloridaFoundation for Prader-Willi ResearchCompleted
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University of UtahThe Hospital for Sick Children; Boston Children's HospitalCompletedAtherosclerosis | Down Syndrome | Cardiovascular Risk FactorUnited States
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Hoffmann-La RocheCompleted
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University of MichiganNational Institutes of Health (NIH)Completed
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Ovid Therapeutics Inc.TerminatedAngelman SyndromeUnited States, Israel
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ART Fertility Clinics LLCUniversity Women's Hospital TübingenActive, not recruitingInfertility | Aneuploidy | Infertility, FemaleUnited Arab Emirates
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Life Molecular Imaging SACompletedDown Syndrome | Amyloid Beta-proteinUnited States
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RTI InternationalUniversity of North Carolina, Chapel HillEnrolling by invitationTuberous Sclerosis | Down Syndrome | Duchenne Muscular Dystrophy | Prader-Willi Syndrome | Fragile X Syndrome | Rett Syndrome | Turner Syndrome | Williams Syndrome | Angelman Syndrome | Chromosome 22q11.2 Deletion Syndrome | Klinefelter Syndrome | Phelan-McDermid Syndrome | Dup15Q Syndrome | Smith Magenis SyndromeUnited States
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Boston Children's HospitalUniversity of California, San Diego; Food and Drug Administration (FDA); Angelman... and other collaboratorsRecruiting
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Hoffmann-La RocheCompletedDown SyndromeUnited States, France, Italy, Canada, United Kingdom, Argentina, Spain
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Ovid Therapeutics Inc.CompletedAngelman SyndromeUnited States, Israel
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Vanda PharmaceuticalsCompletedSmith-Magenis Syndrome | CircadianUnited States
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Children's Hospital of PhiladelphiaEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedDown Syndrome | Subclinical HypothyroidismUnited States
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedAccelerated Phase Chronic Myelogenous Leukemia | Adult Acute Lymphoblastic Leukemia in Remission | Childhood Acute Lymphoblastic Leukemia in Remission | Childhood Chronic Myelogenous Leukemia | Chronic Phase Chronic Myelogenous Leukemia | Recurrent Adult Acute Lymphoblastic Leukemia | Recurrent... and other conditionsUnited States
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University of Kansas Medical CenterNational Institute on Aging (NIA)CompletedAlzheimer Disease | Down SyndromeUnited States
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National Center for Research Resources (NCRR)Completed
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University of FloridaNational Institutes of Health (NIH)Completed
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University of Colorado, DenverRecruitingAlzheimer Disease | Down Syndrome | Mild Cognitive ImpairmentUnited States
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National Institute of Dental and Craniofacial Research...TerminatedDiGeorge Syndrome | HypoparathyroidismUnited States
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University of OxfordHoffmann-La Roche; Foundation for Angelman Syndrome Therapeutics UKRecruiting