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Clinical Trials on Platelet Storage Pool Deficiency
Total 245 results
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Chiesi Farmaceutici S.p.A.Completed
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Zymenex A/SCompleted
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Eunice Kennedy Shriver National Institute of Child...Completed
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Zymenex A/SEuropean CommissionCompletedAlpha-MannosidosisBelgium, Denmark, Spain, United Kingdom
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University Hospital, AngersLigue contre le cancer, FranceRecruitingEssential Thrombocythemia | Myeloproliferative Neoplasm | Primary Myelofibrosis, Prefibrotic Stage | Primary Myelofibrosis, Fibrotic StageFrance
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Chiesi Farmaceutici S.p.A.CompletedAlpha-MannosidosisFrance
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Zymenex A/SEuropean CommissionCompletedA Placebo-Controlled Phase 3 Trial of Repeated Lamazym Treatment of Subjects With Alpha-MannosidosisAlpha-MannosidosisDenmark, United Kingdom, France, Germany, Poland
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Chiesi Farmaceutici S.p.A.Not yet recruiting
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Chiesi Farmaceutici S.p.A.CromsourceCompletedAlpha-MannosidosisFrance, Denmark, Austria, Germany, Italy
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Chiesi Farmaceutici S.p.A.Withdrawn
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Instituto Nacional de Ciencias Medicas y Nutricion...UnknownRenal Insufficiency | Vitamin D Deficiency | End Stage Renal Failure on Dialysis | Vascular CalcificationMexico
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Institut National de la Santé Et de la Recherche...RecruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Mucopolysaccharidosis III | Mucopolysaccharidosis IV | Mucopolysaccharidosis VII | Multiple Sulfatase Deficiency Disease | Mucopolysaccharidosis IXFrance
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NYU Langone HealthNational Cancer Institute (NCI)TerminatedStage I Multiple Myeloma | Stage II Multiple Myeloma | Stage III Multiple Myeloma | Thrombocytopenia | Refractory Multiple MyelomaUnited States
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Chung-Hsing WangSanofiNot yet recruiting
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SanofiRecruitingAcid Sphingomyelinase Deficiency (ASMD)France
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Noguchi Memorial Institute for Medical ResearchInternational Food Policy Research InstituteRecruitingHIV Infections | Child Development | Nutrition PoorGhana
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Baylor College of MedicineShireActive, not recruiting
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Genzyme, a Sanofi CompanyCompletedHuman Acid Sphingomyelinase DeficiencyUnited Kingdom, United States
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Nanfang Hospital of Southern Medical UniversityCompletedThrombelastography,Acute on Chronic Liver Failure, PlateletChina
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Zymenex A/SEuropean CommissionUnknown
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Zymenex A/SEuropean CommissionCompleted
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University of California, San FranciscoNational Cancer Institute (NCI)CompletedMyelodysplastic Syndromes | Leukemia | Congenital Amegakaryocytic Thrombocytopenia | Severe Congenital NeutropeniaUnited States
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SandozCompleted
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University Of PerugiaRecruitingObesity | Ketosis | Lysosomal Acid Lipase Deficiency | Ketogenic DietingItaly
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University of ArkansasCompletedCirrhosis | Sarcopenia | Portal Hypertension | Liver Transplant | End-stage Liver Disease (ESLD) | Poor Physical FitnessUnited States
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Hamad Medical CorporationTerminatedPolycythemia Vera | Essential Thrombocythemia | Primary Myelofibrosis, Prefibrotic Stage | Primary Myelofibrosis, Fibrotic StageQatar
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Creighton UniversityDialysis Clinic, Inc.CompletedVitamin D Deficiency | End Stage Renal Disease | Chronic Kidney DiseaseUnited States
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Augusta UniversityUnknownCardiovascular Diseases | Hemodialysis | Chronic Kidney Disease Stage 5 | Chronic Kidney Disease Stage 3 | Chronic Kidney Disease Stage 4 | Vitamin K DeficiencyUnited States
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SanofiRecruitingAcid SphingoMyelinase Deficiency | Gaucher Disease, SplenomegalyFrance
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Ultragenyx Pharmaceutical IncTerminatedWilson Disease | Ornithine Transcarbamylase Deficiency | Glycogen Storage Disease Type IASpain, United Kingdom, Canada, United States, Brazil
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Fundación Española de Hematología y HemoterapíaRecruitingGaucher Disease | Acid SphingoMyelinase DeficiencySpain
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Postgraduate Institute of Medical Education and...RecruitingIron Deficiency Anemia | Chronic Liver FailureIndia
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Winthrop University HospitalNational Kidney FoundationCompletedVitamin D Deficiency | End Stage Renal DiseaseUnited States
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Zymenex A/SEuropean CommissionCompletedAlpha MannosidosisCzechia, Germany, Norway, United Kingdom
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Duke UniversityCompletedHemoglobinopathies | Thalassemia | Lysosomal Storage Disease | Immunodeficiencies | Inborn Errors of Metabolism | Sickle Cell | Non Malignant Disorders | Congenital Marrow FailuresUnited States
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SanofiPulse Infoframe Ltd.RecruitingNiemann-Pick Diseases | Acid Sphingomyelinase DeficiencyUnited States
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Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
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AryoGen Pharmed Co.CompletedFactor VII Deficiency | Hemophilia A With Inhibitor | Hemophilia B With Inhibitor | Glanzmann's ThrombastheniaIran, Islamic Republic of
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Federal Research Institute of Pediatric Hematology...CompletedWiskott-Aldrich SyndromeRussian Federation
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Federal Research Institute of Pediatric Hematology...RecruitingWiskott-Aldrich SyndromeRussian Federation
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Catalyst BiosciencesTerminatedFactor VII Deficiency | Hemophilia A With Inhibitor | Glanzmann ThrombastheniaUnited States, India, Italy, Russian Federation, Ukraine
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Weill Medical College of Cornell UniversityNovartis PharmaceuticalsTerminatedBleeding | Thrombocytopenia | Wiskott-Aldrich SyndromeUnited States
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Sun Yat-sen UniversityRecruitingColorectal Cancer Stage II | Colorectal Cancer Stage III | MSI-H | Mmr DeficiencyChina
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University of PittsburghRecruitingLysosomal Storage Diseases | Leukodystrophy | Niemann-Pick Diseases | Batten Disease | Gaucher Disease | Krabbe Disease | Alpha-Mannosidosis | Osteopetrosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | GM1 Gangliosidoses | MPS I | MPS II | Vanishing White Matter Disease | Multiple Sulfatase Deficiency... and other conditionsUnited States
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The University of Hong KongNovartisRecruitingPrimary Myelofibrosis | Polycythemia Vera | Essential Thrombocythemia | Myeloproliferative Neoplasm | Post-polycythemia Vera Myelofibrosis | Post-essential Thrombocythemia Myelofibrosis | Primary Myelofibrosis, Prefibrotic Stage | Primary Myelofibrosis, Fibrotic StageHong Kong
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University of California, San FranciscoRecruitingSphingolipidoses | Enzyme DeficiencyUnited States
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Passage Bio, Inc.Active, not recruitingGM1 Gangliosidosis | GM1 Gangliosidosis, Type I | GM1 Gangliosidosis, Type 2 | Beta-Galactosidase-1 (GLB1) DeficiencyUnited States, Canada, United Kingdom, Turkey, Brazil
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National Center for Research Resources (NCRR)University of California, Los AngelesCompletedThrombocytopenia | Inborn Errors of Metabolism | Metachromatic Leukodystrophy | Fanconi's Anemia | Thalassemia Major | Pure Red-Cell AplasiaUnited States
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Genzyme, a Sanofi CompanyTerminatedFabry Disease | Alpha Galactosidase A DeficiencyUnited States, Austria, United Kingdom