- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Pompe Disease
Total 380517 results
-
University Children's Hospital, ZurichSanofiCompleted
-
Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe DiseaseUnited States
-
Genzyme, a Sanofi CompanyCompletedPompe Disease Late-Onset | Glycogen Storage Disease Type II GSD IIUnited States
-
Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe DiseaseUnited States, Israel, France, United Kingdom
-
Royal Brompton & Harefield NHS Foundation TrustGenzyme, a Sanofi CompanyUnknownPompe's Disease
-
Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Pompe Disease | Glycogenesis 2 Acid Maltase DeficiencyUnited States, Canada, Australia
-
Genzyme, a Sanofi CompanyTerminatedGlycogen Storage Disease Type II (GSD-II) | Pompe Disease | Glycogenesis 2 Acid Maltase DeficiencyUnited States, Israel
-
Jordi Perez LopezHospital Vall d'HebronUnknown
-
LMU KlinikumCompletedHealthy | Myotonic Dystrophy Type 2 | Pompe Disease (Late-onset) | Spinal Muscular Atrophy Type 3 | Myotonic Dystrophy Type 1 (DM1) | Facioscapulohumeral Muscular Dystrophy 1 | Inclusion Body Myositis, SporadicGermany
-
Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe DiseaseUnited States
-
Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Pompe DiseaseUnited States
-
University Hospital Center of MartiniqueRecruiting
-
University of California, IrvineCompletedMuscle Weakness | Pompe DiseaseUnited States
-
SanofiCompletedPompe Disease | Mucopolysaccharidosis Type I (MPS I)Italy
-
Genzyme, a Sanofi CompanyApproved for marketingGlycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe Disease (Late-Onset)United States
-
Centre Hospitalier Universitaire de NiceCompletedPompe's DiseaseFrance
-
McMaster UniversityNot yet recruitingObesity | Lysosomal Storage Diseases | Muscle Loss | Glycogen Storage Disease Type II | Pompe Disease | Nutrition Poor | Glycogen Storage Disease Type II, Adult | Glycogen Storage Disease Type II Late Onset
-
Centre Hospitalier Universitaire de NiceCompleted
-
M.A.G.I.C. Clinic LTDHanalytics Solutions Inc.RecruitingMitochondrial Diseases | Fabry Disease | Metabolic Disease | Gaucher Disease | Pompe DiseaseCanada
-
CENTOGENE GmbH RostockWithdrawnLung Disease | Cerebral Aneurysm | Macroglossia | Cardiac Diseases | Obstructive Sleep Apnoea | Muscular Weakness | Hepato-splenomegalyGermany, India, Sri Lanka
-
O & O Alpan LLCUnknownFabry Disease | Niemann-Pick Disease | Gaucher Disease | Pompe Disease | Lysosomal Storage DisordersUnited States
-
Centre Hospitalier Universitaire de LiegeSanofi; Takeda; University of Liege; Orchard Therapeutics; Centre Hospitalier Régional... and other collaboratorsRecruitingCongenital Adrenal Hyperplasia | Hemophilia A | Hemophilia B | Mucopolysaccharidosis I | Mucopolysaccharidosis II | Cystic Fibrosis | Alpha 1-Antitrypsin Deficiency | Sickle Cell Disease | Fanconi Anemia | Chronic Granulomatous Disease | Wilson Disease | Severe Congenital Neutropenia | Ornithine Transcarbamylase... and other conditionsBelgium
-
Gangnam Severance HospitalRecruitingPancretic Dissease (Benign/Malignancy) | BIle Duct Diseae(Benign/Malignancy) | Ampulla of Vater Disease (Benign/Malignancy)Korea, Republic of
-
University of MichiganNational Institutes of Health (NIH); National Institute of Dental and Craniofacial...CompletedPeriodontal Disease | Non-diseased PatientsUnited States
-
Yonsei UniversityActive, not recruitingCoronary Artery DiseasseKorea, Republic of
-
First Affiliated Hospital of Wenzhou Medical UniversityCompletedLiver Diseases | Small Bowel Disease | Colorectal Disease | Gastric Diseases | Digestive Tract DiseasesChina
-
Facet BiotechCompletedCrohn's Disease | Colitis | Digestive System Disease | Gastrointestinal Disease | Intestinal DiseaseUnited States, Canada
-
Klinikum Westbrandenburg GmbHUnknown
-
Boston Children's HospitalRecruitingValve Disease, Heart | Valve Heart Disease | Valve Disease, AorticUnited States
-
McMaster Children's HospitalSt. Justine's HospitalCompletedInflammatory Bowel Diseases | Crohn Disease | Colitis | Pediatric Crohns DiseaseCanada
-
First Affiliated Hospital of Harbin Medical UniversityUnknownColon Disease; | Rectal Disease;China
-
Academisch Medisch Centrum - Universiteit van Amsterdam...CelltrionRecruitingBowel Disease | Inflammatory Disease | Disease CrohnNetherlands
-
Medtronic - MITGCompletedInflammatory Bowel Disease, Crohn DiseaseIsrael
-
Hospices Civils de LyonNot yet recruitingCrohn Disease | Pediatric Crohns DiseaseFrance
-
Morphic Therapeutic, IncRecruitingInflammatory Bowel Diseases | Crohn's DiseaseUnited States, Georgia
-
Qu Biologics Inc.CompletedCrohn's Disease | Inflammatory Bowel DiseaseCanada
-
National Heart, Lung, and Blood Institute (NHLBI)CompletedHeart Diseases | Cardiovascular Diseases | Vascular Diseases | Raynaud's Disease
-
University of LeicesterRecruitingHeart Failure | Chronic Obstructive Pulmonary Disease | Asthma | Type 2 Diabetes | Coronary Heart Disease | Interstitial Lung DiseaseUnited Kingdom
-
Fundación Pública Andaluza Progreso y SaludTelefónica S.A.; Agency of Social Services and Dependency of Andalusia; Salud...UnknownChronic Lung Disease | Chronic Heart DiseaseSpain
-
The Second Hospital of Nanjing Medical UniversityAir Force Military Medical University, ChinaRecruitingInflammatory Bowel Disease | Crohn's DiseasesChina
-
Abbott Medical DevicesCompletedCoronary Artery Disease | Coronary Heart Disease | Peripheral Vascular Disease | Peripheral Artery Disease | Arterial Occlusive DiseaseUnited States
-
Central Hospital, Nancy, FranceInstitut Régional de Médecine Physique et de RéadaptationUnknownInterest of Hydrophysiotherapy Care in Parkinson Disease's Motor and Non-motor Symptoms (THERMAPARK)Interest of Hydrophysiotherapy Care in Parkinson Disease's Non-motor Symptoms
-
National Institutes of Health Clinical Center (CC)National Institute of Allergy and Infectious Diseases (NIAID); NovartisTerminatedCrohn's Disease | Colitis | Inflammatory Bowel DiseaseUnited States
-
University of BernMerck Sharp & Dohme LLC; University Hospital, Basel, Switzerland; University... and other collaboratorsCompleted
-
Fondazione IRCCS Policlinico San Matteo di PaviaUniversity of PaviaRecruitingCalcific Aortic Valve DiaseaseItaly
-
First Affiliated Hospital of Harbin Medical UniversityUnknownColon Disease; | Rectal DiseaseChina
-
Children's Hospital Los AngelesCompleted
-
University of BariUnknownIBS in Celiac DeseaseItaly
-
Ryazan State Medical UniversityCompletedChronic Obstructive Pulmonary Disease | Peripheral Artery DiseaseRussian Federation