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Clinical Trials on Pompe Disease Infantile-Onset
Total 905 results
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University of ArizonaBristol-Myers SquibbUnknownKidney Transplantation | New Onset Diabetes After TransplantUnited States
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Second Xiangya Hospital of Central South UniversityCompletedType 1 Diabetes Mellitus Maturity OnsetChina
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Swedish Orphan BiovitrumRecruitingStill's Disease, Adult-Onset | Macrophage Activation Syndrome | Stills Disease, Juvenile-OnsetUnited States, Canada, France, Germany, Italy, Netherlands, Spain
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REGENXBIO Inc.WithdrawnLate-infantile Neuronal Ceroid Lipofuscinosis Type 2 (CLN2)
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Zhujiang HospitalUnknownInfantile Hemangioma | Capillary Hemangioma | Capillary Hemangiomas | Hemangioma, Capillary Infantile | Strawberry HemangiomaChina
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BioMarin PharmaceuticalCompletedBatten Disease | CLN2 Disease | Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 | Jansky-Bielschowsky Disease | CLN2 DisorderUnited States, Germany, Italy, United Kingdom
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BioMarin PharmaceuticalCompletedBatten Disease | CLN2 Disease | Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 | Jansky-Bielschowsky Disease | CLN2 DisorderUnited States, Germany, Italy, United Kingdom
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Atlantic UniversityA.T. Still University of Health SciencesCompletedPartial Epilepsy | Focal Onset EpilepsyUnited States
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Centro Hospitalar Lisboa NorteCompletedPregnancy | Labour Onset and Length AbnormalitiesPortugal
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Centre Hospitalier Universitaire de NīmesRecruitingCerebral Palsy InfantileFrance
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National Institute of Arthritis and Musculoskeletal...RecruitingArthritis | Still's Disease, Adult-Onset | Systemic Inflammation | Autoinflammatory SyndromeUnited States
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University Hospital, CaenCompletedType 1 Diabetes Mellitus Maturity OnsetFrance
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Columbia UniversityNew York State Department of Health; Illumina, Inc.; GeneDxRecruitingEarly Onset Genetic Conditions With Near Complete PenetranceUnited States
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Karolinska InstitutetThe Swedish Research CouncilCompletedPANDAS | Obsessive-compulsive Disorder | Obsessive-compulsive Disorder With Acute Onset | Pediatric Autoimmune Neuropsychiatric Disorders Associated With Streptococcal Infections | Pediatric Acute-onset Neuropsychiatric Syndrome (PANS) | Childhood Acute Neuropsychiatric Symptoms (CANS)Sweden
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Columbia UniversityMedicem International CR s.r.o.CompletedLabor Onset and Length Abnormalities | Induced; BirthUnited States
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Novartis PharmaceuticalsTerminatedAge-related Macular Degeneration | Choroidal Neo-Vascular Age-onset Macular DegenerationUnited Kingdom, United States
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Universidad Nacional Autonoma de HondurasRecruitingLabor Onset and Length Abnormalities | First BirthHonduras
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Jaeb Center for Health ResearchNational Eye Institute (NEI)CompletedInfantile Esotropia | Acquired Non-accommodative Esotropia | Acquired Partially Accommodative EsotropiaUnited States
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Ann & Robert H Lurie Children's Hospital of ChicagoThrasher Research FundUnknownWest SyndromeUnited States
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All India Institute of Medical Sciences, New DelhiRecruiting
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University of PennsylvaniaCompletedLogopenic Progressive Aphasia | Posterior Cortical Atrophy (PCA) | Alzheimer's Disease, Early OnsetUnited States
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Capital Medical UniversityPeking University First Hospital; The First Affiliated Hospital of Anhui Medical... and other collaboratorsRecruitingAlzheimer Disease, Late Onset | Mild Cognitive Impairment(MCI) | Familial Alzheimer Disease (FAD) | Vascular Dementia (VaD) | Normal Control | Non-Alzheimer Degenerative DementiaChina
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Whanin Pharmaceutical CompanyCompletedPartial-onset Seizures With or Without Secondary GeneralisationKorea, Republic of
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Promius Pharma, LLCCompleted
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University of Puerto RicoNational Institute on Minority Health and Health Disparities (NIMHD)CompletedEffectiveness of a Multi-level Clinic and Family Asthma Intervention With a Randomized Control TrialInfantile AsthmaPuerto Rico
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Celia BañulsInstituto de Salud Carlos IIIActive, not recruiting
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Universidad Católica San Antonio de MurciaCompletedInfant Conditions | Gastro-Intestinal Disorder | Colic, Infantile
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Jip GroenInBiomeRecruitingMicrobial Colonization | Neonatal Infection | Neonatal Sepsis, Early-Onset | Microbial Disease | Clinical Sepsis | Culture Negative Neonatal Sepsis | Neonatal Sepsis, Late-Onset | Culture Positive Neonatal SepsisNetherlands
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Imperial College London Diabetes CentreUnknownGestational Diabetes | Maturity-onset Diabetes of the Young | GDM | MODYUnited Arab Emirates
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Assistance Publique - Hôpitaux de ParisCompletedCongenital Cerebellar Ataxias | Early-onset Cerebellar AtaxiasFrance
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University Hospital, BrestRecruiting
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Helsinki University Central HospitalUniversity of Helsinki; Noona HealthcareCompletedBreast Cancer, Early-Onset
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UCB Pharma SAUCB Japan Co. Ltd.CompletedEpilepsy | Partial Onset SeizuresChina, Japan
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UCB Japan Co. Ltd.ParexelCompletedEpilepsy | Partial-onset SeizuresJapan
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Massachusetts General HospitalNational Institute of Nursing Research (NINR); Dana-Farber Cancer Institute; University... and other collaboratorsRecruitingPain | Disabilities Multiple | Cerebral Palsy InfantileUnited States, Australia
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KU LeuvenOdisee University college for applied sciencesNot yet recruitingStress | Insomnia | Sleep | Anxiety | Distress, Emotional | Sleep Problem | Early Onset Dementia | Young Onset DementiaBelgium
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China Academy of Chinese Medical SciencesUnknownBronchitis | Infantile Diarrhea | Viral Pneumonia | Bacillary Dysentery | Virus Hepatitis
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Duke UniversityUniversity College, London; Stanford University; Sambodhi Research and Communication... and other collaboratorsCompletedDiarrhea, Infantile | Childhood PneumoniaIndia
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SK Life Science, Inc.Not yet recruiting
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University of CincinnatiAmerican College of GastroenterologyCompletedAcute Cellular Graft Rejection | New Onset Diabetes After TransplantUnited States
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UCB Japan Co. Ltd.CompletedEpilepsy | Partial Onset SeizuresJapan
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UCB Japan Co. Ltd.CompletedEpilepsy | Partial Onset SeizuresJapan
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Aziende Chimiche Riunite Angelini Francesco S.p.AHippocrates ResearchCompletedEpilepsy | Focal Onset SeizureUnited Kingdom, France, Germany
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Jiangxi Qingfeng Pharmaceutical Co. Ltd.UnknownEpilepsy | Focal-Onset SeizureChina
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Eisai Co., Ltd.CompletedEpilepsy | Partial-onset Seizures
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Boston Children's HospitalRecruitingEpilepsy | Dravet Syndrome | Infantile Spasms | Epileptic Encephalopathy | Ohtahara Syndrome | Early Myoclonic Epileptic Encephalopathy | PCDH19-related Epilepsy and Related Conditions | KCNQ2-Related Epileptic Encephalopathy | Epilepsy of Infancy With Migrating Focal Seizures (Disorder)United States
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Tehran University of Medical SciencesUnknownInfantile Spinal Muscular Atrophy, Type I [Werdnig- Hoffman]Iran, Islamic Republic of
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ASCEND TherapeuticsCompletedHypogonadism | Low Testosterone | Late Onset HypogonadismUnited States
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University of Novi SadRecruitingAtrial Fibrillation New OnsetSerbia
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Population Health Research InstituteCanadian Cardiovascular Society; Canadian Stroke Prevention Intervention NetworkCompletedAtrial Fibrillation New OnsetCanada