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Clinical Trials on Porphyria in United States
Total 39 results
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The University of Texas Medical Branch, GalvestonTerminatedHereditary Coproporphyria | Acute Intermittent Porphyria | Variegate PorphyriaUnited States
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The University of Texas Medical Branch, GalvestonCompletedAcute PorphyriasUnited States
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Alnylam PharmaceuticalsTerminatedAcute Hepatic Porphyria | Acute Intermittent Porphyria (AIP) | Hereditary Coproporphyria (HCP) | Variegate Porphyria (VP) | ALA Dehydratase Deficient Porphyria (ADP) | Hepatic Porphyrias | Porphyria AcuteUnited States
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Icahn School of Medicine at Mount SinaiRecruiting
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University of California, San FranciscoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University... and other collaboratorsCompletedAcute Intermittent Porphyria (AIP) | Hereditary Coproporphyria (HCP) | Variegate Porphyria (VP)United States
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University of Texas Southwestern Medical CenterNovartis PharmaceuticalsCompletedPorphyria Cutanea TardaUnited States
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The University of Texas Medical Branch, GalvestonActive, not recruitingHereditary Coproporphyria | Acute Intermittent Porphyria | Variegate PorphyriaUnited States
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Zymenex A/SCompleted
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Icahn School of Medicine at Mount SinaiRecruitingAcute Intermittent Porphyria (AIP)United States
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Alnylam PharmaceuticalsCompletedAcute Intermittent PorphyriaUnited States, United Kingdom, Sweden
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University of South FloridaUniversity of Miami; University of Alabama at Birmingham; Icahn School of Medicine... and other collaboratorsCompletedPorphyriasUnited States
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Alnylam PharmaceuticalsCompletedAcute Intermittent PorphyriaUnited States, United Kingdom, Sweden
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Alnylam PharmaceuticalsCompletedAcute Hepatic Porphyria | Acute Intermittent Porphyria | Porphyria, Acute Intermittent | Acute Porphyria | Hereditary Coproporphyria (HCP) | Variegate Porphyria (VP) | ALA Dehydratase Deficient Porphyria (ADP)United States, Spain, United Kingdom, Korea, Republic of, Australia, Bulgaria, Canada, Denmark, Finland, France, Germany, Italy, Japan, Mexico, Netherlands, Poland, Sweden, Taiwan
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The University of Texas Medical Branch, GalvestonCompletedPorphyria Cutanea TardaUnited States
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National Center for Research Resources (NCRR)University of TexasCompleted
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Alnylam PharmaceuticalsRecruitingAcute Hepatic PorphyriaBelgium, France, Germany, United Kingdom, United States, Italy, Sweden
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Brigham and Women's HospitalCompleted
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Alnylam PharmaceuticalsCompletedAcute Hepatic PorphyriaUnited States, Belgium, Bulgaria, France, Italy, Mexico, Spain, Taiwan, United Kingdom, Netherlands, Korea, Republic of, Switzerland, Czechia, Poland, Finland, Australia, Germany, Israel, Norway, South Africa
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Vanderbilt University Medical CenterRecruitingPostural Orthostatic Tachycardia Syndrome | Acute Hepatic PorphyriaUnited States
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University of Alabama at BirminghamPorphyria Rare Disease Clinical Research ConsortiumCompletedErythropoietic Protoporphyria (EPP)United States
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National Center for Research Resources (NCRR)University of TexasCompleted
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National Center for Research Resources (NCRR)University of TexasUnknown
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National Center for Research Resources (NCRR)University of TexasCompleted
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Wake Forest University Health SciencesNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Gilead... and other collaboratorsCompleted
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National Center for Research Resources (NCRR)Icahn School of Medicine at Mount SinaiCompletedMetabolism, Inborn Errors | Leukodystrophy, Globoid Cell | Tay-Sachs Disease | Porphyria, ErythropoieticUnited States
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Amy K. Dickey, M.D.Wake Forest University Health Sciences; University of TexasRecruitingErythropoietic Protoporphyria | X-linked ProtoporphyriaUnited States
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Disc Medicine, IncEnrolling by invitationErythropoietic ProtoporphyriaUnited States, Australia
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Clinuvel Pharmaceuticals LimitedCompletedErythropoietic ProtoporphyriaUnited States
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University of UtahNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University... and other collaboratorsTerminatedErythropoietic Protoporphyria (EPP) | X Linked Erythropoietic ProtoporphyriaUnited States
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Icahn School of Medicine at Mount SinaiNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedErythropoietic Protoporphyria | EPP | X-linked Protoporphyria | XLPUnited States
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Mitsubishi Tanabe Pharma America Inc.CompletedErythropoietic Protoporphyria (EPP)United States
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Disc Medicine, IncActive, not recruitingErythropoietic ProtoporphyriaUnited States
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Clinuvel Pharmaceuticals LimitedCompletedErythropoietic ProtoporphyriaUnited States
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Clinuvel Pharmaceuticals LimitedCompletedErythropoietic ProtoporphyriaNetherlands, Finland, France, Germany, Ireland, United Kingdom
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Mitsubishi Tanabe Pharma America Inc.Active, not recruitingEPP | XLPUnited States, Germany, Japan, Spain, Italy, Sweden, Australia, Canada, Norway, United Kingdom
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Mitsubishi Tanabe Pharma America Inc.CompletedEPP | XLPSpain, United States, Germany, Norway, Italy, Australia, Canada, Japan, Sweden, United Kingdom
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Icahn School of Medicine at Mount SinaiNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Rare... and other collaboratorsCompletedErythropoietic Protoporphyria | EPP | XLP | X-Linked Protoporphyria | XLPP | X-Linked Dominant Erythropoietic Protoporphyria | XLEPP | XLDPUnited States
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Mitsubishi Tanabe Pharma America Inc.RecruitingErythropoietic Protoporphyria (EPP) | X-Linked Protoporphyria (XLP)United States, Spain, France, United Kingdom, Japan, Italy, Australia, Bulgaria, Czechia, Netherlands, Poland
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4Life Research, LLCCompletedSin Health | Skin Hydration | Skin Wrinkles | Skin Porphyrins | Facial Skin Red Spots | Facial Skin Red VasculatureUnited States