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Clinical Trials on Pyruvate Kinase Deficiency in New Zealand
Total 1548 results
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Agios Pharmaceuticals, Inc.Active, not recruitingPediatric Pyruvate Kinase Deficiency | Pediatric Hemolytic AnemiaUnited States, Spain, Denmark, Turkey, Netherlands, Czechia, United Kingdom, Germany, Canada, Switzerland
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Agios Pharmaceuticals, Inc.Active, not recruitingPyruvate Kinase DeficiencyUnited States, Canada, Netherlands, United Kingdom, France, Italy
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Boston Children's HospitalAgios Pharmaceuticals, Inc.CompletedPyruvate Kinase Deficiency | Congenital Non-Spherocytic Hemolytic AnemiaUnited States, Germany, Canada, Czechia, Italy, Netherlands
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Loulou FoundationActive, not recruitingCyclin-Dependent Kinase-Like 5 Deficiency DisorderUnited States, Spain, Italy, France, Canada, Germany, United Arab Emirates
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UCB BIOSCIENCES, Inc.Zogenix, Inc.Active, not recruitingThymidine Kinase 2 DeficiencyUnited States, Israel, Spain
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Columbia UniversityUniversitat Autonoma de Barcelona; Instituto de Salud Carlos III; University... and other collaboratorsActive, not recruitingThymidine Kinase 2 Deficiency | Mitochondrial DNA Depletion Syndrome 2 Myopathic TypeUnited States
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Swiss Federal Institute of TechnologyCompletedPregnancy Related | Iodine DeficiencyNew Zealand
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Arcturus Therapeutics, Inc.CompletedOrnithine Transcarbamylase DeficiencyNew Zealand
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Arrowhead PharmaceuticalsCompleted
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Dicerna Pharmaceuticals, Inc.WithdrawnAlpha 1-Antitrypsin DeficiencyNew Zealand
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyCompleted
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CSL LimitedCompletedPrimary Immune DeficiencyAustralia, New Zealand
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AlexionRecruitingWolman Disease | Cholesterol Ester Storage Disease | Lysosomal Acid Lipase Deficiency | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2 | Acid Lipase Deficiency | LIPA Deficiency | LAL-DeficiencyFrance, Belgium, United States, Spain, Germany, Greece, Israel, Italy, Slovenia, United Kingdom, Brazil, Canada, Denmark, Australia, Croatia, Czechia, Ireland, Mexico, Netherlands, Poland, Portugal, Saudi Arabia
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Intellia TherapeuticsNot yet recruitingHereditary AngioedemaFrance, New Zealand, United Kingdom
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AlexionCompletedWolman Disease | Lysosomal Acid Lipase DeficiencyUnited States, Canada, United Kingdom, Italy, France
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Baxalta now part of ShireCompletedAlpha 1-Antitrypsin DeficiencyNew Zealand, Australia
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Baxalta now part of ShireBaxter Healthcare, Ltd. (New Zealand), Baxter Healthcare Pty. Ltd. (Australia)CompletedAlpha 1-Antitrypsin DeficiencyAustralia, New Zealand
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Zogenix MDS, Inc.CompletedThymidine Kinase 2 (TK2)United States, Spain, Israel
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Intellia TherapeuticsActive, not recruitingHereditary AngioedemaFrance, New Zealand, Germany, United Kingdom, Netherlands, Australia
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ViiV HealthcareCompletedHIV InfectionsUnited States, New Zealand
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | Cholesterol Ester Storage Disease(CESD) | LAL-DeficiencyFrance, United States, United Kingdom, Czechia
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ProofPilotJoovvUnknownTestosterone Deficiency | Estrogen DeficiencyUnited States
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Fu Jen Catholic UniversityCompletedVitamin B 12 DeficiencyTaiwan
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | LAL-Deficiency | Cholesterol Ester Storage Disease (CESD)France, United Kingdom, United States, Canada, Czechia
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Murdoch Childrens Research InstituteRoyal Children's HospitalCompletedPrimary Immunodeficiency | Invasive Pneumococcal Disease, Protection Against | Invasive Pneumococcal Disease, Recurrent Isolated, 1 | Invasive Pneumococcal Disease, Recurrent Isolated, 2Australia, New Zealand
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Inhibrx, Inc.CompletedAlpha-1 Antitrypsin Deficiency | AATDUnited States, New Zealand, United Kingdom
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Hospital for Special Surgery, New YorkCompletedVitamin D DeficiencyUnited States
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Sitaram Bhartia Institute of Science and ResearchUniversity College, London; Public Health Foundation of India; Paropakar Matenity...CompletedVitamin B 12 DeficiencyIndia, Nepal
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CSL LimitedCompleted
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Alexion PharmaceuticalsTerminatedLysosomal Acid Lipase DeficiencyUnited States
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Icahn School of Medicine at Mount SinaiCompletedIron Deficiency AnemiaUnited States
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Ascendis Pharma Endocrinology Division A/SCompletedA Safety, Tolerability and Efficacy Study of TransCon hGH in Children With Growth Hormone DeficiencyEndocrine System Diseases | Pituitary Diseases | Hormone Deficiency | Growth Hormone Deficiency, PediatricUnited States, Canada, Australia, New Zealand
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James J. Peters Veterans Affairs Medical CenterCompletedMacrocytic Anemia With Vitamin B12 DeficiencyUnited States
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Northwell HealthStaten Island University HospitalCompletedVitamin B12 DeficiencyUnited States
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University College, LondonSitaram Bhartia Institute of Science and Research; Paropakar Maternity and...UnknownVitamin B 12 Deficiency | Child Developmental Delay | Child Malnutrition | Maternal ExposureIndia, Nepal
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Lady Hardinge Medical CollegeCompletedVitamin D DeficiencyIndia
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Weill Medical College of Cornell UniversityRecruitingTestosterone DeficiencyUnited States
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Rockefeller UniversityCompletedVitamin D DeficiencyUnited States
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Rochester General HospitalCompletedSecondary Immune DeficiencyUnited States
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Astellas Pharma Global Development, Inc.CompletedAcute Myeloid Leukemia (AML) | Acute Myeloid Leukemia With FMS-like Tyrosine Kinase (FLT3) MutationUnited States
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American Regent, Inc.WithdrawnIron Deficiency, AnaemiaUnited States
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Weill Medical College of Cornell UniversityTerminated
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Montefiore Medical CenterCompleted
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Winthrop University HospitalCompleted
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Winthrop University HospitalCompletedVitamin D Deficiency | PostmenopausalUnited States
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Cornell UniversityCompletedIron Deficiency (Without Anemia)United States
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Cornell UniversityInstituto Nacional de Salud Publica, MexicoCompletedIron Deficiency (Without Anemia)United States
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Rochester General HospitalCompletedSecondary Immune Deficiency DisorderUnited States
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NYU Langone HealthCompletedVitamin D DeficiencyUnited States
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Pharmacosmos A/SCompletedIron Deficiency Anemia | Iron Deficiency AnaemiaUnited States