- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Pyruvate Metabolism, Inborn Errors
Total 4341 results
-
AmgenCompletedSevere Familial HypercholesterolemiaItaly, Czechia, United States, Israel, New Zealand, South Africa, France, Spain, Australia, Belgium, Canada, Netherlands, Hong Kong, Brazil, United Kingdom, Greece, Japan, Lebanon
-
LIB Therapeutics LLCMedpace, Inc.CompletedHeterozygous Familial HypercholesterolemiaUnited States, Israel, Norway, South Africa, Turkey
-
Innovent Biologics (Suzhou) Co. Ltd.CompletedHomozygous Familial HypercholesterolemiaChina
-
Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Australia, Austria, Netherlands, Taiwan, Ukraine
-
Novartis PharmaceuticalsCompletedA Study of Inclisiran in Participants With Homozygous Familial Hypercholesterolemia (HoFH) (ORION-5)Homozygous Familial HypercholesterolemiaHong Kong, Israel, Russian Federation, Serbia, South Africa, Taiwan, Turkey, Ukraine
-
Organon and CoTerminatedLipid Metabolism, Inborn Errors | Hypercholesterolemia, Familial
-
Korea United Pharm. Inc.Active, not recruiting
-
Pfizer's Upjohn has merged with Mylan to form Viatris...CompletedPediatric Heterozygous HypercholesterolemiaGreece, Norway, Canada
-
Regeneron PharmaceuticalsSanofiCompletedHypercholesterolemia | Heterozygous Familial HypercholesterolemiaUnited States, Canada
-
Regeneron PharmaceuticalsSanofiCompletedHeterozygous Familial HypercholesterolemiaUnited States, Germany
-
Laval UniversityAmgenCompleted
-
Akcea TherapeuticsIonis Pharmaceuticals, Inc.WithdrawnHomozygous Familial HypercholesterolemiaCanada
-
AmgenCompletedHomozygous Familial HypercholesterolemiaNew Zealand, South Africa, France, United States, Spain, Belgium, Czechia, Italy, Netherlands, Hong Kong, Canada, Lebanon
-
Aegerion Pharmaceuticals, Inc.CompletedFamilial Hypercholesterolemia - HomozygousJapan
-
Aegerion Pharmaceuticals, Inc.FDA Office of Orphan Products DevelopmentCompletedHomozygous Familial HypercholesterolemiaUnited States, Canada, Italy, South Africa
-
PfizerCompletedHeterozygous Familial HypercholesterolemiaCanada, Netherlands, United Kingdom, United States, Spain, Poland, Finland, Norway, South Africa, Italy, Bulgaria
-
Laval UniversityCompletedHomozygous Familial HypercholesterolemiaCanada
-
Regeneron PharmaceuticalsSanofiCompletedHeterozygous Familial HypercholesterolemiaUnited Kingdom, Netherlands, Czech Republic, Norway
-
Cerenis Therapeutics, SACompletedHomozygous Familial HypercholesterolemiaUnited States, Canada, Italy, Netherlands, United Kingdom
-
Aegerion Pharmaceuticals, Inc.University of Pennsylvania; Doris Duke Charitable FoundationCompletedHomozygous Familial HypercholesterolemiaUnited States
-
The University of Western AustraliaNational Health and Medical Research Council, AustraliaUnknownFamilial Hypercholesterolaemia | HypertriglyceridaemiaAustralia
-
HemoShear TherapeuticsTerminatedPropionic Acidemia | Methylmalonic AcidemiaUnited States, Saudi Arabia, Australia
-
Nicoline LøkkenCompleted
-
King Abdullah International Medical Research CenterCompletedPropionic Acidemia | Methylmalonic AcidemiaSaudi Arabia
-
Mendel TuchmanUniversity of Colorado, Denver; Children's Hospital of Philadelphia; University... and other collaboratorsTerminatedPropionic Acidemia | Methylmalonic AcidemiaUnited States
-
University Children's Hospital, ZurichRecruitingUrea Cycle DisordersSwitzerland
-
PTC TherapeuticsRecruitingPhenylketonuriaUnited States
-
First Affiliated Hospital Bengbu Medical CollegeRecruiting
-
Vitaflo International, LtdBirmingham Women's and Children's NHS Foundation TrustRecruiting
-
Jnana TherapeuticsRecruitingPhenylketonuriaUnited States, Australia
-
University Medical Centre LjubljanaNot yet recruitingPhenylketonurias | Nutritional and Metabolic Diseases
-
Applied Therapeutics, Inc.CompletedClassic GalactosemiaUnited States
-
SynlogicTerminatedPhenylketonuriaUnited States, Canada, Georgia, Turkey
-
University of Southern CaliforniaNational PKU AllianceActive, not recruitingPhenylketonuriasUnited States
-
Boston Children's HospitalBioMarin PharmaceuticalCompletedPhenylketonuriasUnited States
-
University of NebraskaCompleted
-
Homology Medicines, IncTerminated
-
University of Missouri-ColumbiaBioMarin PharmaceuticalEnrolling by invitationPhenylketonuriasUnited States
-
APR Applied Pharma Research s.a.Terminated
-
University Hospital Inselspital, BerneUniversity of ZurichCompleted
-
Applied Therapeutics, Inc.Active, not recruitingClassic GalactosemiaUnited States
-
University Hospitals Cleveland Medical CenterBioMarin PharmaceuticalCompleted
-
The University of Texas Medical Branch, GalvestonTerminated
-
Boston Children's HospitalBioMarin PharmaceuticalCompleted
-
NestléWithdrawn
-
Universidade do PortoBioMarin Pharmaceutical; Centro Hospitalar do PortoCompleted
-
University of British ColumbiaVitaflo International, LtdUnknown