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Clinical Trials on Refractive Errors in Canada
Total 429 results
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Exsar CorporationThe Hospital for Sick Children; NYU Langone Health; University Hospitals Cleveland...WithdrawnG(M2) Ganglioside | Tay-Sachs Disease Ganglioside | Sandhoff Disease GangliosideUnited States, Canada
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Alexion Pharmaceuticals, Inc.RecruitingHypophosphatasiaUnited States, Japan, Germany, Turkey, Italy, India, Australia, France, United Kingdom, Argentina, Canada
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Novartis PharmaceuticalsCompletedIron Overload | Hereditary HemochromatosisUnited States, Germany, Italy, Australia, Canada, France
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Genzyme, a Sanofi CompanyBioMarin/Genzyme LLCCompletedMucopolysaccharidosis I | Hurler-Scheie Syndrome | Hurlers SyndromeUnited States, Canada, Germany
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InSightecActive, not recruitingParkinson's Disease | Movement Disorders | Tardive Dyskinesia | Dystonia | Essential Tremor | Huntington's Disease | Wilson's Disease | Holmes Tremor | Orofacial DyskinesiasCanada
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Cerenis Therapeutics, SATerminatedFamilial HypoalphalipoproteinemiaFrance, United States, Belgium, Canada, Israel, Italy, Netherlands
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Arrowhead PharmaceuticalsCompletedHypertriglyceridemia | Familial ChylomicronemiaAustralia, Canada, New Zealand
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The Hospital for Sick ChildrenChildren's Hospital of Philadelphia; Canadian Institutes of Health Research... and other collaboratorsRecruitingIdiopathic Infantile Hypercalcemia - Mild FormCanada
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SanofiRegeneron PharmaceuticalsCompletedHypercholesterolaemiaNorway, Russian Federation, Sweden, South Africa, Czechia, United States, Canada, France, Netherlands, Spain
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ShireCompleted
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Regeneron PharmaceuticalsSanofiCompletedHypercholesterolemia | Heterozygous Familial HypercholesterolemiaUnited States, Canada
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Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeUnited States, Canada, Sweden
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Inozyme PharmaRecruitingGeneralized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets | Ectonucleotide Pyrophosphatase/Phosphodiesterase1 DeficiencyUnited States, United Kingdom, Canada
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University of PennsylvaniaPassage Bio, Inc.RecruitingGM1 GangliosidosisUnited States, Turkey, Brazil, Canada, United Kingdom
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AVROBIOTerminatedGaucher DiseaseUnited States, Canada
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Novartis PharmaceuticalsCompletedHereditary HemochromatosisBelgium, France, Russian Federation, Romania, Slovakia, Spain, Switzerland
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McMaster Children's HospitalUnknownEpilepsy | Metabolic Acidosis | Tubular Acidosis; RenalCanada
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Aeglea BiotherapeuticsCompletedArginase I Deficiency | HyperargininemiaUnited States, Canada, United Kingdom, Portugal
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ModernaTX, Inc.RecruitingPropionic AcidemiaUnited States, Spain, Netherlands, France, United Kingdom, Australia, Canada, Italy
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Pacific Parkinson's Research CentreUniversity of British Columbia; Oregon Health and Science University; University... and other collaboratorsRecruitingParkinson Disease | Gaucher Disease | GBA Gene MutationUnited States, Canada
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REGENXBIO Inc.National Heart, Lung, and Blood Institute (NHLBI)TerminatedHomozygous Familial Hypercholesterolemia (HoFH)United States, Canada, Italy, Netherlands
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Dicerna Pharmaceuticals, Inc., a Novo Nordisk companyActive, not recruitingPrimary Hyperoxaluria Type 3United States, Germany, United Kingdom, Canada, Poland
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AlexionCompletedWolman Disease | Lysosomal Acid Lipase DeficiencyUnited States, Canada, United Kingdom, Italy, France
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Horizon Pharma Ireland, Ltd., Dublin IrelandCompletedUrea Cycle DisordersUnited States, Canada
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Agios Pharmaceuticals, Inc.RecruitingPediatric Pyruvate Kinase Deficiency | Pediatric Hemolytic AnemiaUnited States, Spain, Germany, Netherlands, Canada, France, Israel, Switzerland, Italy
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SunovionCompletedReactive Airways Disease (RAD)United States, Canada
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Ultragenyx Pharmaceutical IncActive, not recruitingGlycogen Storage Disease Type IA | Von Gierke's Disease (GSD Type Ia)Netherlands, United States, Canada, Spain
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Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | LAL-Deficiency | Cholesterol Ester Storage Disease (CESD)France, United Kingdom, United States, Canada, Czechia
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Agios Pharmaceuticals, Inc.Active, not recruitingPediatric Pyruvate Kinase Deficiency | Pediatric Hemolytic AnemiaUnited States, Spain, Denmark, Turkey, Netherlands, Czechia, United Kingdom, Germany, Canada, Switzerland
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Alexion Pharmaceuticals, Inc.RecruitingHypophosphatasiaItaly, Spain, Israel, Korea, Republic of, Belgium, Germany, United States, China, France, Taiwan, Austria, Japan, India, Australia, Argentina, Poland, Turkey, Brazil, Thailand, United Kingdom, Canada, Slovakia, Czechia
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Alexion Pharmaceuticals, Inc.Not yet recruitingHypophosphatasiaUnited States, Taiwan, Thailand, Vietnam, United Kingdom, Korea, Republic of, Israel, Italy, Australia, Turkey, France, Poland, Germany, Spain, Belgium, China, Canada, Brazil, Argentina, Mexico
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SanofiRegeneron PharmaceuticalsCompletedHypercholesterolaemiaNetherlands, United States, Canada, Russian Federation, South Africa
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Agios Pharmaceuticals, Inc.Active, not recruitingPyruvate Kinase DeficiencyUnited States, Spain, Japan, Canada, United Kingdom, Korea, Republic of, Ireland, Thailand, Italy, Turkey, Denmark, Brazil, France, Germany, Netherlands, Switzerland
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Origin BiosciencesCompletedMolybdenum Cofactor Deficiency | Isolated Sulfite Oxidase DeficiencySpain, Israel, United States, United Kingdom, Canada, Netherlands, Germany, Saudi Arabia, Tunisia, Japan, Italy, Malaysia, Poland, Turkey
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PfizerTerminatedHyperlipoproteinemia Type IIICanada, United States
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Inozyme PharmaRecruitingGeneralized Arterial Calcification of Infancy | Autosomal Recessive Hypophosphatemic Rickets | Ectonucleotide Pyrophosphatase/phosphodiesterase1 DeficiencyUnited States, United Kingdom, Canada, France, Germany
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BioMarin PharmaceuticalCompletedPhenylketonuria (PKU)United States, Turkey, Canada, France, Germany, Italy, United Kingdom
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PfizerCompletedGaucher DiseaseUnited Kingdom, Canada, Israel, United States, Australia, Spain
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Canadian Fabry Research ConsortiumNova Scotia Health AuthorityRecruiting
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PfizerCompletedGaucher DiseaseUnited States, Chile, United Kingdom, Israel, Canada, Spain, South Africa, Italy
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Mark BatshawEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsTerminatedUrea Cycle DisordersUnited States, Canada
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Korea, Republic of, Canada, Japan, France, Denmark
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Regeneron PharmaceuticalsSanofiCompletedHomozygous Familial HypercholesterolemiaUnited States, South Africa, Canada, Greece, Japan, Ukraine, Austria, Czechia, France, Germany, Italy, Taiwan, Turkey
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Agios Pharmaceuticals, Inc.CompletedAnemia, Hemolytic | Pyruvate Kinase DeficiencyUnited States, Spain, Switzerland, Turkey, Germany, France, United Kingdom, Japan, Netherlands, Brazil, Canada, Czechia, Denmark, Italy, Korea, Republic of, Thailand
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Alexion Pharmaceuticals, Inc.Enrolling by invitationHypophosphatasia (HPP)United States, Italy, Russian Federation, Spain, United Kingdom, Germany, Canada, France, Saudi Arabia, Poland, Australia
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Agios Pharmaceuticals, Inc.RecruitingPyruvate Kinase DeficiencyUnited States, Germany, Spain, Italy, United Kingdom, Czechia, France, Canada, Korea, Republic of, Netherlands, Turkey, Portugal, Denmark, Ireland, Switzerland, Thailand
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AmgenCompletedHomozygous Familial HypercholesterolemiaNew Zealand, South Africa, France, United States, Spain, Belgium, Czechia, Italy, Netherlands, Hong Kong, Canada, Lebanon
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Novartis PharmaceuticalsCompletedTransfusional Hemosiderosis | Transfusional Iron OverloadTaiwan, Turkey, Egypt, United Kingdom, Thailand, Canada, China, Italy, Cyprus, Lebanon, United Arab Emirates
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Novartis PharmaceuticalsTerminatedFamilial Chylomicronemia Syndrome (FCS) (HLP Type I)South Africa, Germany, United Kingdom, France, United States, Canada, Netherlands
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedMetabolic Diseases | Congenital Abnormalities | Infant, Newborn, Diseases | Genetic Diseases, Inborn | Dyslipidemias | Metabolism, Inborn Errors | Lipid Metabolism Disorders | Hypercholesterolemia | Hyperlipidemias | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Hyperlipoproteinemia Type II | Metabolic... and other conditionsUnited States, Taiwan, Brazil, Canada, South Africa, United Kingdom, Singapore