- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Refractive Errors in United Kingdom
Total 2276 results
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National Institute of Arthritis and Musculoskeletal...CompletedIchthyosis | Ichthyosis, X-Linked | Ichthyosis, Lamellar | Darier Disease | Hailey-Hailey Disease | Hyperkeratosis, Epidermolytic | KeratodermaUnited States
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University of California, IrvineCompletedMuscle Weakness | Pompe DiseaseUnited States
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Lysosomal and Rare Disorders Research and Treatment...UnknownParkinson Disease | Gaucher DiseaseUnited States
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National Institute of Neurological Disorders and...CompletedFabry DiseaseUnited States
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National Institute of Neurological Disorders and...Completed
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Diurnal LimitedNational Institutes of Health (NIH)CompletedCongenital Adrenal Hyperplasia | Adrenal Insufficiency | Endocrine DiseaseUnited States
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O & O Alpan LLCCompletedFabry DiseaseUnited States
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Ohio State UniversityGenzyme, a Sanofi CompanyCompleted
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National Institute of Neurological Disorders and...Completed
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National Institute of Neurological Disorders and...Completed
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Horizon Pharma Rheumatology LLCCompletedRefractory Chronic GoutUnited States
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Ionis Pharmaceuticals, Inc.CompletedAmyloidosis | Familial Amyloid Polyneuropathy | FAP | TTR | TransthyretinUnited States, Spain, Argentina, Brazil, France, Germany, Italy, Portugal, United Kingdom
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Rocket Pharmaceuticals Inc.RecruitingDanon DiseaseUnited States
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REGENXBIO Inc.Withdrawn
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Horizon Pharma Ireland, Ltd., Dublin IrelandCompletedUrea Cycle DisordersUnited States, Canada
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Rocket Pharmaceuticals Inc.Active, not recruitingDanon DiseaseUnited States
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National Institute of Neurological Disorders and...National Institute of Neurological Disorders and Stroke@@@Shire Human Genetic...Completed
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Acid Maltase Deficiency Disease | Glycogenosis 2 | Pompe DiseaseUnited States
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Cyclo Therapeutics, Inc.RecruitingNiemann-Pick Disease, Type C1United States, Spain, Israel, Taiwan, Brazil, Germany, Australia, Poland, Turkey, Italy, United Kingdom
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Patricia I. Dickson, M.D.The Ryan FoundationTerminatedMucopolysaccharidosis I | Scheie Syndrome | Lysosomal Storage Disease | Spinal Cord Compression | Hurler-Scheie SyndromeFinland, United States
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BioMarin PharmaceuticalApproved for marketingMorquio A Syndrome | MPS IVA | Mucopolysaccharidosis IVAUnited States, Puerto Rico
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University of South FloridaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedArthritis, Reactive | Reiter DiseaseUnited States, Canada
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Neurocrine BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, United Kingdom, France, Greece, Italy, Spain, Belgium, Canada, Germany, Poland
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Astellas Gene TherapiesRecruitingPompe Disease (Late-onset)United States, Spain, France, Taiwan, Italy
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, Germany, Argentina, Australia, France, United Kingdom
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Duke UniversityRecruiting
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University of California, San FranciscoRecruitingSphingolipidoses | Enzyme DeficiencyUnited States
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University of NebraskaUniversity of Colorado, Denver; University of Pittsburgh; Children's Hospital...Completed
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National Institutes of Health Clinical Center (CC)Eunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedAdrenal Insufficiency | Congenital Adrenal Hyperplasia (CAH) | Excess AndrogenUnited States
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II | Pompe Disease Infantile-OnsetUnited States, France, South Africa
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National Human Genome Research Institute (NHGRI)TerminatedCitrullinemia | Argininosuccinic Aciduria | Hyperargininemia | Ornithine Carbamoyltransferase Deficiency | Carbamoyl-Phosphate Synthase I Deficiency | N-Acetylglutamate Synthase DeficiencyUnited States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedParkinson's Disease | Gaucher's DiseaseUnited States
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Ionis Pharmaceuticals, Inc.CompletedAmyloidosis | Familial Amyloid Polyneuropathy | FAP | TTR | TransthyretinNew Zealand, United States, Spain, Argentina, Brazil, France, Germany, Italy, Portugal, United Kingdom
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Amicus TherapeuticsCompletedGaucher Disease | Gaucher Disease, Type 1 | Type 1 Gaucher DiseaseUnited States
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Horizon Pharma Ireland, Ltd., Dublin IrelandCompletedUrea Cycle DisordersUnited States, Canada
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ArmaGen, IncCompletedMucopolysaccharidosis IIUnited States, Germany, Philippines
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Spruce BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, Australia, Brazil, Estonia, Germany, Korea, Republic of, Latvia, Lithuania, Poland, Romania, Spain, Sweden, Turkey, Canada, Italy, United Kingdom
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Horizon Therapeutics, LLCCompletedUrea Cycle DisorderUnited States, Canada
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University of UtahGenzyme, a Sanofi CompanyCompletedFabry DiseaseUnited States
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Georgetown UniversityCompletedEnd Stage Renal Disease | HyperhomocysteinemiaUnited States
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Horizon Pharma USA, Inc.Completed
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NeuroVia, Inc.WithdrawnX-Linked AdrenoleukodystrophyAustralia, Argentina, United Kingdom, Colombia, Chile, France, Russian Federation, Ukraine
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Monica E. KleinmanSchering-PloughCompletedProgeria | Hutchinson-Gilford SyndromeUnited States
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University of RochesterRecruitingBatten Disease | Neuronal Ceroid Lipofuscinosis | Neuronal Ceroid Lipofuscinosis CLN6 | Neuronal Ceroid Lipofuscinosis CLN3 | Neuronal Ceroid Lipofuscinosis CLN5 | Neuronal Ceroid Lipofuscinosis CLN1 | Neuronal Ceroid Lipofuscinosis CLN2 | Neuronal Ceroid Lipofuscinosis CLN7 | Neuronal Ceroid Lipofuscinosis... and other conditionsUnited States
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Ultragenyx Pharmaceutical IncKyowa Kirin Co., Ltd.Active, not recruitingX-linked Hypophosphatemia | Hypophosphatemic RicketsUnited States, Brazil, Argentina, Canada, Chile, Colombia
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Pompe DiseaseUnited States
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Eunice Kennedy Shriver National Institute of Child...RecruitingLysosomal Storage Disease | Cholesterol MetabolismUnited States
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Office of Rare Diseases (ORD)UnknownAdrenal Hyperplasia, CongenitalUnited States, Brazil, France
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Cedars-Sinai Medical CenterNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsUnknown