- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Refractive Errors in United Kingdom
Total 2276 results
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Masonic Cancer Center, University of MinnesotaTerminatedSphingolipidoses | Niemann-Pick Disease, Type C | Krabbe Disease | Sly Syndrome | Fucosidosis | Aspartylglucosaminuria | Alpha Mannosidosis | Hurler's Syndrome | Maroteaux-Lamy Syndrome | Wolman's Disease | Niemann-Pick Disease Type BUnited States
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedCoronary Artery Disease | Heterozygous Familial HypercholesterolemiaUnited States, Canada
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Amicus TherapeuticsCompletedFabry DiseaseCanada, Belgium, United States, Australia, Netherlands
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National Institute of Diabetes and Digestive and...RecruitingPrimary Hyperparathyroidism | Pseudohypoparathyroidism | Parathyroid Cancer | Inheritable Bone Diseases | Multiple Endocrine Neoplasia, Type 1United States
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University of MinnesotaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Washington... and other collaboratorsRecruiting
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University of MinnesotaCompletedDisorders of Sex Development | Urogenital Abnormalities | Congenital Adrenal Hyperplasia | Genetic Diseases, Inborn | Hyperplasia | Adrenocortical Hyperfunction | Congenital Disorders | Hydrocortisone | Adrenal Hyperplasia | Steroid Metabolic Diseases, Inborn | Adrenal Gland DiseaseUnited States
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Oregon Health and Science UniversityTerminatedImmune System Diseases | Lipid Metabolism, Inborn Errors | Mevalonic Aciduria | Mevalonate Kinase Deficiency | Periodic Fever Syndromes, HereditaryUnited States
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University of MinnesotaGE HealthcareCompletedParkinson Disease | Gaucher Disease | Idiopathic Rapid Eye Movement Sleep DisorderUnited States
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University of Texas Southwestern Medical CenterWithdrawnHIV Infections | Cerebral Palsy | Crohn Disease | Hurler Syndrome | Juvenile Rheumatoid ArthritisUnited States
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bluebird bioTerminatedCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, United Kingdom, Argentina, Canada, Germany, Italy, Netherlands
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Horizon Pharma USA, Inc.CompletedCystinosisFrance, United States, Netherlands
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National Human Genome Research Institute (NHGRI)RecruitingHermansky-Pudlak Syndrome (HPS)United States
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Brigham and Women's HospitalUniversity of MichiganCompletedPrimary Aldosteronism | Primary Aldosteronism Due to Adrenal Hyperplasia (Bilateral)United States
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Baylor Research InstituteCompleted
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National Institute of Arthritis and Musculoskeletal...CompletedMyositis | Dermatomyositis | Polymyositis | Glycogen Storage Disease Type II | Glycogen Storage Disease Type VIIUnited States
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Revive Therapeutics, Ltd.Unknown
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Rady Children's Hospital, San DiegoCompletedAsthma | Reactive Airway DiseaseUnited States
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Baylor College of MedicineChildren's National Research InstituteRecruitingOrnithine Transcarbamylase Deficiency | Urea Cycle Disorder | Carbamyl Phosphate Synthetase Deficiency | Argininosuccinic Aciduria | Hyperargininemia | Citrullinemia 1 | ARGI Deficiency | ASL Deficiency | ASS Deficiency | NAGS DeficiencyUnited States
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National Institute of Diabetes and Digestive and...RecruitingLipodystrophyUnited States
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PRG Science & Technology Co., Ltd.Amarex Clinical ResearchCompletedHutchinson-Gilford Progeria Syndrome | Werner SyndromeUnited States
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National Human Genome Research Institute (NHGRI)Completed
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Eunice Kennedy Shriver National Institute of Child...RecruitingNiemann-Pick Disease Type C1 | Juvenile Neuronal Ceroid Lipofuscinosis | Smith-Lemli-Opitz Syndrome | Creatine Transporter DeficiencyUnited States
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Chiesi Farmaceutici S.p.A.Chiesi USA, Inc.AvailableFabry DiseaseUnited States
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Spruce BiosciencesCompletedCongenital Adrenal Hyperplasia | CAH - Congenital Adrenal Hyperplasia | CAH - 21-Hydroxylase DeficiencyUnited States
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Pompe Disease | Glycogenesis 2 Acid Maltase DeficiencyUnited States, Canada, Australia
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University of Colorado, DenverRecruitingHearing Loss | Smith-Lemli-Opitz Syndrome | Cone-Rod DystrophyUnited States
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Baylor Research InstituteShireUnknownQuality of Life | Renal Insufficiency | Cardiac EventUnited States
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Eunice Kennedy Shriver National Institute of Child...CompletedObesity | Hyperandrogenism | Polycystic Ovarian Syndrome | Oligomenorrhea | Adrenal HyperplasiaUnited States
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Baylor College of MedicineChildren's Hospital of Philadelphia; Children's Hospital Colorado; Seattle Children... and other collaboratorsRecruitingOrnithine Transcarbamylase Deficiency | Urea Cycle Disorder | Argininosuccinic Aciduria | Hyperargininemia | Citrullinemia 1 | ARGI Deficiency | ASL Deficiency | ASS DeficiencyUnited States
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PfizerCompletedTransthyretin Amyloidosis Cardiomyopathy (ATTR-CM)Italy, Romania, France, Australia, Austria, Portugal, Slovakia, Slovenia, Spain, United Kingdom
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bluebird bioActive, not recruitingCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, Argentina, Australia, Brazil, France, Germany, Netherlands, United Kingdom, Italy
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University of Texas Southwestern Medical CenterEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsSuspendedCongenital Adrenal HyperplasiaUnited States
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Radnor Registry Research, IncAmerican Regent, Inc.CompletedSoft Tissue Injuries | Dysmenorrhea | Fractures | Gouty Arthritis | Ureteral ColicUnited States
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TakedaTakeda Development Center Americas, Inc.RecruitingHunter Syndrome | Mucopolysaccharidosis (MPS)United States
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University of ChicagoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedKrabbe Disease | Mucopolysaccharidosis Type II (MPS II) | Mucopolysaccharidosis Type I (MPS I) | Mucopolysaccharidosis Type III (MPS III) | Mucopolysaccharidosis Type VI (MPS VI)United States
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MED-LIFE DISCOVERIES LPUnknown
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ShireCompletedFabry DiseaseCanada, United States
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Wake Forest University Health SciencesCompletedCardiovascular Diseases | Diabetes | Metabolic Syndrome | Liver Fat | Cardiovascular Risk Factor | Diet Habit | Dietary Modification | High Cholesterol | Triglycerides High | Low-density-lipoprotein-type | HDL Cholesterol, Low Serum | High Blood Sugar | Intra-abdominal Fat | High Density Lipoprotein DeficiencyUnited States
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Eunice Kennedy Shriver National Institute of Child...RecruitingCongenital Adrenal Hyperplasia (CAH) | Familial Male-Limited Precocious Puberty (FMPP)United States
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National Human Genome Research Institute (NHGRI)RecruitingPulmonary Fibrosis | Healthy Volunteers | Hermansky-Pudlak Syndrome (HPS)United States
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Completed
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Adrenas Therapeutics IncRecruitingCongenital Adrenal HyperplasiaUnited States
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University of Alabama at BirminghamCompletedProteinuria | Fabry DiseaseUnited States, Slovenia
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Ironwood Pharmaceuticals, Inc.Medpace, Inc.TerminatedGout | Chronic Kidney Disease (CKD)United States, Hungary, Poland, Czechia
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Caleb NelsonOtsuka America PharmaceuticalCompleted
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ShireNo longer available
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O & O Alpan LLCUnknownLysosomal Storage DisordersUnited States
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Genzyme, a Sanofi CompanyTerminatedGlycogenosis 2 | Glycogen Storage Disease Type II (GSD II) | Acid Maltase Deficiency | Pompe Disease (Infantile-Onset)United States, Taiwan, Germany
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University of NebraskaRecruiting
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St. Jude Children's Research HospitalRecruitingMucopolysaccharidosis I | Severe Combined Immunodeficiency | Neuroblastoma | Neoplasm | Malignancy, HematologicUnited States