- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Refractive Errors
Total 4723 results
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Assistance Publique - Hôpitaux de ParisCompletedOculocerebrorenal SyndromeFrance
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National Center for Research Resources (NCRR)Icahn School of Medicine at Mount SinaiCompletedMetabolism, Inborn Errors | Leukodystrophy, Globoid Cell | Tay-Sachs Disease | Porphyria, ErythropoieticUnited States
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McGill University Health Centre/Research Institute...Children's Hospital and Medical Center, Omaha, NebraskaCompleted
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M.D. Anderson Cancer CenterNational Cancer Institute (NCI)Active, not recruitingWeight Loss | Advanced Malignant Solid Neoplasm | Recurrent Malignant Solid Neoplasm | Metastatic Malignant Solid Neoplasm | Cancer Fatigue | C-Reactive Protein MeasurementUnited States
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Crinetics Pharmaceuticals Inc.RecruitingCongenital Adrenal Hyperplasia | Classic Congenital Adrenal HyperplasiaBrazil, India, United States, Argentina, Italy, United Kingdom
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H. Lundbeck A/SRecruitingCongenital Adrenal HyperplasiaUnited Kingdom
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National Institutes of Health Clinical Center (CC)RecruitingCongenital Adrenal HyperplasiaUnited States
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University of British ColumbiaVancouver Coastal Health Research Institute; Genome British ColumbiaRecruitingAcute Coronary Syndrome | Familial Hypercholesterolemia | STEMI | NSTEMI - Non-ST Segment Elevation MI | Familial Hypercholesterolemia - Heterozygous | Familial Hypercholesterolemia Due to Genetic Defect of Apolipoprotein B | Familial Hypercholesterolemia Due to Heterozygous LDL Receptor Mutation and other conditionsCanada
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Adrenas Therapeutics IncRecruitingCongenital Adrenal HyperplasiaUnited States
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Baylor College of MedicineChildren's National Research InstituteRecruitingOrnithine Transcarbamylase Deficiency | Urea Cycle Disorder | Carbamyl Phosphate Synthetase Deficiency | Argininosuccinic Aciduria | Hyperargininemia | Citrullinemia 1 | ARGI Deficiency | ASL Deficiency | ASS Deficiency | NAGS DeficiencyUnited States
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Spruce BiosciencesTerminatedCongenital Adrenal HyperplasiaUnited States, Australia, Brazil, Canada, Denmark, Estonia, Germany, Ireland, Italy, Korea, Republic of, Latvia, Lithuania, Netherlands, Poland, Romania, Spain, Sweden, Switzerland, Turkey, United Kingdom
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Cellaion SATerminatedUrea Cycle Disorder | Crigler-Najjar Syndrome | Acute on Chronic Liver FailureBelgium, Spain, France, Bulgaria, Poland
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Eunice Kennedy Shriver National Institute of Child...CompletedCongenital Adrenal Hyperplasia (CAH)United States
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Neurocrine BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, Spain, Belgium, Austria, Bulgaria, Canada, Czechia, France, Germany, Greece, Israel, Italy, Netherlands, Poland, Portugal, Serbia, Sweden, United Kingdom
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ShireCompletedHunter SyndromeUnited States, United Kingdom, Canada
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Amicus TherapeuticsEngage Health Inc.CompletedFabry DiseaseUnited States
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VA Office of Research and DevelopmentCompletedChronic Kidney Diseases | GoutUnited States
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Diurnal LimitedCompletedCongenital Adrenal HyperplasiaFrance, United States, Japan
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Hospices Civils de LyonCompletedClassic Congenital Adrenal HyperplasiaFrance
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Mandos LLCTerminatedNiemann-Pick Type C DiseaseUnited States
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University Hospital, BordeauxCompletedChronic Pain | Fabry's DiseaseFrance
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Allena PharmaceuticalsTerminatedChronic Kidney Diseases | Hyperuricemia | GoutUnited States
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Centre Hospitalier Universitaire de NiceCompleted
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Wake Forest University Health SciencesCompletedCardiovascular Diseases | Diabetes | Metabolic Syndrome | Liver Fat | Cardiovascular Risk Factor | Diet Habit | Dietary Modification | High Cholesterol | Triglycerides High | Low-density-lipoprotein-type | HDL Cholesterol, Low Serum | High Blood Sugar | Intra-abdominal Fat | High Density Lipoprotein DeficiencyUnited States
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CENTOGENE GmbH RostockWithdrawnSplenomegaly | Hepatomegaly | Ceramidase Deficiency | Farber's LipogranulomatosisGermany, India, Egypt
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CENTOGENE GmbH RostockWithdrawnMuscle Weakness | Peripheral NeuropathyEgypt, Germany, India, Sri Lanka
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SanofiApproved for marketing
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisBrazil, France, Italy, United States, Germany, United Kingdom
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Idorsia Pharmaceuticals Ltd.CompletedGM2 Gangliosidosis | GM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff Disease | Gaucher Disease, Type 2 | AB Variant Gangliosidosis GM2United States, Spain, Germany, Italy, Belgium, Brazil, France, Portugal, Switzerland, United Kingdom
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ShireCompletedHunter Syndrome | Mucopolysaccharidosis II (MPS II)United States, France, United Kingdom, Germany, Sweden, Spain, Brazil, Canada, Italy, Romania
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Kobe UniversityBoehringer IngelheimActive, not recruitingInsulin Resistance - Type A | Insulin Resistance - Type B | Lipoatrophic Diabetes Mellitus | Insulin Resistance SyndromeJapan
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Cyprium Therapeutics, Inc.Eunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedMenkes Disease | Occipital Horn Syndrome | Unexplained Copper DeficiencyUnited States
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Enzyvant Therapeutics GmBHCompletedFarber Disease | Farber's Disease | Farber Lipogranulomatosis | Acid Ceramidase Deficiency | Ceramidase Deficiency | N-Laurylsphingosine Deacylase Deficiency | ASAH1 MutationUnited States, Egypt, Canada, Italy, Turkey, Argentina, Germany, India, Sweden
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University of AarhusUnknownGlycogen Storage Disease Type 2 | Dystrophia MyotonicaDenmark
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Genzyme, a Sanofi CompanyCompletedPompe Disease (Late-onset) | Glycogen Storage Disease Type II (GSD-II) | Acid Maltase Deficiency Disease | Glycogenosis 2United States, France, Netherlands
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1 | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States, United Kingdom, Spain, Italy, Brazil, Canada, Poland
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Baylor Research InstituteNational Institute of Neurological Disorders and Stroke (NINDS)Completed
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Genzyme, a Sanofi CompanyCompletedCerebroside Lipidosis Syndrome | Glucosylceramide Beta-Glucosidase Deficiency Disease | Gaucher Disease Type I | Clucocerebrosidase Deficiency Disease | Gaucher Disease, Non-Neuronopathic FormUnited States
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Shaare Zedek Medical CenterUnknownHepatitis C | Gaucher DiseaseIsrael
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ActelionCompleted
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University of British ColumbiaCanadian Institutes of Health Research (CIHR); AllerGen NCE Inc.RecruitingExposure to Pollution | Glucocorticoid ResistanceCanada
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National Taiwan University HospitalMinistry of Science and Technology, TaiwanUnknownAcute Disease | Congenital Metabolic DisorderTaiwan
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Oslo University HospitalAkershus University Hospital, Lørenskog, Norway; Koc University Hospital, Istanbul... and other collaboratorsCompletedDepression | Stress | Insomnia | Anxiety | Optimism | Interpersonal Disengagement | Professional Fulfillment | Work Exhaustion | Self-reported Medical Errors | Physician BurnoutTurkey
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European Georges Pompidou HospitalUnknownEmbolism | Pulmonary Embolism | Pulmonary Vascular Disorder | Pulmonary Embolism and Thrombosis | Diagnostic ErrorsFrance
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University Hospital Inselspital, BerneCompletedDumping Syndrome | Hypoglycemia, ReactiveSwitzerland
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Alnylam PharmaceuticalsCompletedAmyloidosis, Familial | Transthyretin AmyloidosisFrance, Germany, Italy, Portugal, Spain, Sweden, United Kingdom
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Mayo ClinicCompleted
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Catholic University of the Sacred HeartCompletedMorbid Obesity | Bariatric Surgery | Obesity With Complications | Reactive HypoglycemiaItaly