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Clinical Trials on Respiration; Insufficient or Poor, Newborn
Total 7038 results
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bluebird bioCenter for International Blood and Marrow Transplant ResearchRecruitingCerebral Adrenoleukodystrophy (CALD)United States
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Poxel SANot yet recruiting
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Masonic Cancer Center, University of MinnesotaRecruitingCerebral Adrenoleukodystrophy | Adrenoleukodystrophy | ALD (Adrenoleukodystrophy)United States
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Cellaion SATerminatedUrea Cycle Disorder | Crigler-Najjar Syndrome | Acute on Chronic Liver FailureBelgium, Spain, France, Bulgaria, Poland
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Onofre, Aurora Pujol, M.D.Completed
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Radboud University Medical CenterActive, not recruitingTurner Syndrome | Premature Ovarian Failure | Fertility Preservation | Live Birth | Ovarian Tissue CryopreservationNetherlands
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Hugo W. Moser Research Institute at Kennedy Krieger...TerminatedAdrenoleukodystrophyUnited States
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Onofre, Aurora Pujol, M.D.Instituto de Salud Carlos III; Fundacion Hesperia; ELA España AssociationCompletedAdrenomyeloneuropathy | X-linked AdrenoleukodystrophySpain
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Onofre, Aurora Pujol, M.D.Ministerio de Sanidad, Servicios Sociales e Igualdad; Fundacion HesperiaCompleted
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Hugo W. Moser Research Institute at Kennedy Krieger...European Leukodystrophy AssociationCompletedX-linked AdrenoleukodystrophyUnited States
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Nemours Children's ClinicEli Lilly and CompanyCompletedHypogonadism | Turner Syndrome | Premature Ovarian FailureUnited States
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Gilead SciencesCompletedHIV Infections | Renal Impairment | Fanconi Syndrome | Kidney DiseaseCanada, United States
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Beijing Tiantan HospitalRecruiting
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McGill University Health Centre/Research Institute...RecruitingCoronary Artery Disease | Aortic Valve Stenosis | Myocarditis | Dilated Cardiomyopathy | Congenital Heart Disease | Hypertrophic Cardiomyopathy | Pericardial Effusion | Aortic Valve Regurgitation | Vascular Anomaly | Infiltrative CardiomyopathyCanada
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Beth Israel Deaconess Medical CenterBrigham and Women's HospitalRecruitingAortic Valve Disease | Aortic Valve Insufficiency | Aortic Aneurysm | Aortic Diseases | Aortic Valve Calcification | Calcific Aortic Stenosis | Calcific Aortic Stenosis - Bicuspid Valve | Aortic Valve Cusp Abnormality | Aortic Valve Disease MixedUnited States
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Minoryx Therapeutics, S.L.Active, not recruitingAdrenoleukodystrophySpain, United States, Hungary, France, Germany, Italy, Netherlands, United Kingdom
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Nemours Children's ClinicGenentech, Inc.CompletedHypogonadism | Turner Syndrome | Premature Ovarian FailureUnited States, Chile
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National Taiwan University HospitalCompleted
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Masonic Cancer Center, University of MinnesotaWithdrawn
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University of MinnesotaNo longer availableX-linked AdrenoleukodystrophyUnited States
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MedDay Pharmaceuticals SACompletedAdrenoleukodystrophy | Adrenomyeloneuropathy | AMNFrance, Germany, Spain
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Amicus TherapeuticsCompleted
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Eunice Kennedy Shriver National Institute of Child...Food and Drug Administration (FDA)TerminatedAdrenoleukodystrophy | AdrenomyeloneuropathyUnited States
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Academisch Medisch Centrum - Universiteit van Amsterdam...The Stop ALD FoundationCompletedAdrenomyeloneuropathy | X-linked AdrenoleukodystrophyNetherlands
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Paul SzabolcsRecruitingCongenital Bone Marrow Failure Syndromes | Inflammatory Conditions | Primary Immunodeficiency (PID) | Inherited Metabolic Disorders (IMD) | Hereditary Anemias | Systemic Juvenile Idiopathic Arthritis (sJIA)United States
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University of ValenciaHospital Universitario La Fe; Hospital General Universitario de Valencia; Hospital...CompletedAsthma | Type 1 Diabetes | Allergic Rhinitis | Cystic Fibrosis | Pulmonary Disease | Atopic Dermatitis | Food Allergy | Allergic Asthma | Rhinoconjunctivitis | Primary Ciliary Dyskinesia | Short StatureSpain
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National Cancer Institute (NCI)RecruitingFanconi Anemia | Inherited Bone Marrow Failure SyndromeUnited States
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Shirley Ryan AbilityLabNorthwestern University; University of Illinois at Chicago; Ann & Robert H Lurie... and other collaboratorsRecruitingPremature Birth | Intraventricular Hemorrhage | Bronchopulmonary Dysplasia | Hypoxic-Ischemic Encephalopathy | Motor DelayUnited States
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Children's Hospital of Fudan UniversityShanghai High-risk Infants Early Intervention CenterTerminatedCerebral Infarction | Hypoxic-Ischemic Encephalopathy | Periventricular Leukomalacia | Kernicterus | Bilirubin Encephalopathy | Hypoglycemia, Neonatal | Intraventricular Hemorrhage NeonatalChina
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University of North Carolina, Chapel HillNational Institutes of Health (NIH); National Center for Research Resources... and other collaboratorsCompletedCystic Fibrosis | Primary Ciliary Dyskinesia | Kartagener Syndrome | PseudohypoaldosteronismUnited States, Canada
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Université de MontréalWithdrawnGlaucoma | Cataract | Astigmatism | Myopia | Retinopathy of Prematurity | Retinoblastoma | Hyperopia | Amblyopia | Xerophthalmia | TrachomaHaiti
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National Human Genome Research Institute (NHGRI)CompletedCancer | Myelofibrosis | Pulmonary Fibrosis | Gaucher Disease | Hermansky-Pudlak Syndrome (HPS)United States
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Centre Hospitalier Universitaire DijonUnknownHeart Failure | Multiple Sclerosis | Hemophilia | Chronic Respiratory Failure | Horton's Disease | Chronic Coronary Syndrome | AMD and Macular Edema | Malignant HemopathyFrance
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Altoosi University CollegeBabylon UniversityUnknownCerebral Palsy | Cancer | HIV/AIDS | Muscular Dystrophy | Cystic Fibrosis | Cardiac Anomaly | Batten's DiseaseIraq
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Synspira, Inc.TerminatedLung Diseases | Cystic Fibrosis | Pulmonary Disease | Antibiotic Resistant Infection | Respiratory Tract Disease | Cystic Fibrosis Pulmonary Exacerbation | Lung Inflammation | Burkholderia Infections | Lung Infection | Multi-antibiotic Resistance | Pulmonary Inflammation | Lung Infection Pseudomonal | Cystic Fibrosis... and other conditionsUnited Kingdom
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Eunice Kennedy Shriver National Institute of Child...RecruitingTurner Syndrome | Galactosemia | Ovarian Disfunction | Post-menarcheal Adolescents | Variations in Sex Characteristics | Differences in Sex DevelopmentUnited States
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RFM Renal Treatment ServicesUnknownChronic Kidney Disease | Left Ventricular Hypertrophy | Renal OsteodystrophyTurkey
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SwanBio Therapeutics, Inc.RecruitingAMN | AMN Gene Mutation | X-ALDNetherlands, United States
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Leipzig University Medical CenterRecruitingX-linked AdrenoleukodystrophyGermany
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Leipzig University Medical CenterEuropean Leukodystrophy AssociationCompletedX-linked AdrenoleukodystrophyGermany
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bluebird bioActive, not recruitingCerebral Adrenoleukodystrophy (CALD) | Adrenoleukodystrophy (ALD) | X-Linked Adrenoleukodystrophy (X-ALD)United States, Argentina, Australia, Brazil, France, Germany, Netherlands, United Kingdom, Italy
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NeuroVia, Inc.UnknownX-Linked AdrenoleukodystrophyUnited States
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Minoryx Therapeutics, S.L.RecruitingX-linked AdrenoleukodystrophyFrance
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Massachusetts General HospitalEuropean Leukodystrophy AssociationRecruitingRestless Legs Syndrome | AdrenoleukodystrophyUnited States, Netherlands
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Viking Therapeutics, Inc.RecruitingAdrenomyeloneuropathy Form (AMN) of X-linked Adrenoleukodystrophy (X-ALD)United States, France, Germany, Italy, United Kingdom
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Haukeland University HospitalCompletedUltradian Subcutaneous Hydrocortisone Infusion in Addison Disease and Congenital Adrenal HyperplasiaAddison Disease | Adrenal Hyperplasia CongenitalNorway
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Genetic Disease InvestigatorsCompletedVenous Insufficiency | Postural Orthostatic Tachycardia Syndrome | Dysautonomia | Ehlers Danlos Syndrome | External HydrocephalusUnited States
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Minoryx Therapeutics, S.L.Active, not recruitingCerebral AdrenoleukodystrophySpain, Germany, France, Argentina
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Baylor Research InstituteShireUnknownQuality of Life | Renal Insufficiency | Cardiac EventUnited States
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Thomas S. ScanlanWithdrawnAdrenomyeloneuropathy | X-Linked AdrenoleukodystrophyUnited States