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Clinical Trials on Rigid Spine Muscular Dystrophy in Colombia
Total 48 results
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Cooperative International Neuromuscular Research...National Institutes of Health (NIH)CompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | Limb Girdle Muscular DystrophyUnited States
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The Duchenne RegistryParent Project Muscular DystrophyRecruiting
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Cooperative International Neuromuscular Research...Carolinas Medical Center lead study siteCompletedBecker Muscular Dystrophy | Limb-Girdle Muscular Dystrophy, Type 2A (Calpain-3 Deficiency) | Limb-Girdle Muscular Dystrophy, Type 2B (Miyoshi Myopathy, Dysferlin Deficiency) | Limb-Girdle Muscular Dystrophy, Type 2I (FKRP-deficiency)United States
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Wyeth is now a wholly owned subsidiary of PfizerCompletedBecker Muscular Dystrophy | Facioscapulohumeral Muscular Dystrophy | Limb-Girdle Muscular DystrophyUnited States
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Cooperative International Neuromuscular Research...National Institutes of Health (NIH)CompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | Limb Girdle Muscular DystrophyUnited States
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Children's National Research InstituteFoundation to Eradicate DuchenneActive, not recruitingDuchenne Muscular DystrophyUnited States
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Cooperative International Neuromuscular Research...Completed
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States
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Cooperative International Neuromuscular Research...United States Department of DefenseCompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | Limb Girdle Muscular DystrophyUnited States, Japan, Canada
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Santhera PharmaceuticalsSanthera PharmaceuticalsActive, not recruitingDuchenne Muscular DystrophyCanada
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Acceleron Pharma Inc. (a wholly owned subsidiary...Terminated
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Cooperative International Neuromuscular Research...Completed
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Cooperative International Neuromuscular Research...Washington University School of Medicine; Children's National Research Institute and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Australia, Italy
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States
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Children's Hospital of Eastern OntarioJesse's Journey-The Foundation for Gene and Cell TherapyCompletedDuchenne Muscular DystrophyCanada
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Cooperative International Neuromuscular Research...UnknownDuchenne Muscular DystrophyUnited States, Canada
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Cumberland PharmaceuticalsVanderbilt University Medical CenterRecruitingCardiomyopathy, Dilated | Duchenne Muscular Dystrophy CardiomyopathyUnited States
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular Dystrophy | DystrophinopathyUnited Kingdom, Canada, Germany, Spain, Sweden, Italy, Australia, Belgium, France, Israel
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Santhera PharmaceuticalsAvailableDuchenne Muscular DystrophyUnited States, Canada, Israel
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ItalfarmacoRecruitingDuchenne Muscular DystrophyCanada, Italy, France, Belgium, Germany, Netherlands, United Kingdom
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Sarepta Therapeutics, Inc.Completed
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Cooperative International Neuromuscular Research...aTyr Pharma, Inc.; Muscular Dystrophy Canada; FSHD Global Research Foundation; FSH...CompletedFacioscapulohumeral Muscular DystrophyUnited States, Canada, Australia, Sweden, United Kingdom
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Cooperative International Neuromuscular Research...UnknownBecker Muscular DystrophyUnited States, Canada, Italy, United Kingdom
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, Germany, Spain, Sweden, Canada, Italy, Australia, Belgium, France, Israel, United Kingdom
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Capricor Inc.RecruitingNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States
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PfizerTerminatedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Japan, Italy
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ReveraGen BioPharma, Inc.University of Pittsburgh; Newcastle University; European Union; Cooperative International...CompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, United Kingdom, Spain, Netherlands, Sweden, Czechia, Australia, Greece, Israel
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Newcastle... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Germany, Italy
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Cooperative International Neuromuscular Research...United States Department of Defense; National Institutes of Health (NIH); U.S... and other collaboratorsUnknownDuchenne Muscular DystrophyUnited States, Canada, Australia, India, Israel, Argentina, Italy, Sweden
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PTC TherapeuticsParexel; Dohmen Life Science ServicesApproved for marketingDuchenne Muscular DystrophyUnited States
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ItalfarmacoSyneos HealthCompletedDuchenne Muscular DystrophyUnited States, Italy, Spain, Canada, Belgium, France, Germany, Israel, Netherlands, Serbia, United Kingdom
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PfizerTerminatedDuchenne Muscular DystrophyUnited States, Australia, Canada, United Kingdom, Japan, Bulgaria, Italy, Poland
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Sarepta Therapeutics, Inc.Active, not recruitingMuscular Dystrophy, DuchenneUnited States, Korea, Republic of, India, Slovenia, Turkey, United Kingdom, Germany, Switzerland, Spain, Czechia, France, Serbia, Taiwan, Netherlands, Mexico, Colombia, Denmark, New Zealand, Norway, Greece, Hungary, Ireland, Italy, Jo... and more
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ItalfarmacoCromsourceEnrolling by invitationDuchenne Muscular DystrophySpain, United States, Canada, Belgium, France, Israel, Italy, Netherlands, Serbia, Germany, United Kingdom
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GlaxoSmithKlineCompletedMuscular DystrophiesFrance, Denmark, Germany, Belgium, Spain, Turkey, Korea, Republic of, Brazil, Netherlands, Italy, Chile, Japan, Canada, Hungary, Russian Federation, Czechia, Poland, Norway, Argentina, Taiwan
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Eli Lilly and CompanyTerminatedMuscular Dystrophy, DuchenneGermany, United States, Spain, Belgium, France, Italy, Taiwan, Netherlands, Turkey, Korea, Republic of, Argentina, Canada, Japan, Puerto Rico, Russian Federation, United Kingdom
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BioMarin PharmaceuticalTerminatedMuscular DystrophiesUnited States, Canada
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States, Canada, Argentina, Australia, Israel, Italy
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Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Korea, Republic of, Italy, United Kingdom, Canada, Poland, Spain, France, Germany, Belgium, Australia, Czechia, Serbia, Greece, Argentina, Bulgaria, Denmark, Hungary, India, Ireland, Israel, Mexico, Russian Federation, ...
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GlaxoSmithKlineTerminatedMuscular DystrophiesFrance, Bulgaria, Denmark, Germany, Belgium, Canada, Spain, Turkey, United Kingdom, Korea, Republic of, Brazil, Netherlands, Italy, Japan, Czech Republic, Chile, Israel, Hungary, Russian Federation, Australia, Poland, Norway, Argentina and more
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PTC TherapeuticsEnrolling by invitationDuchenne Muscular DystrophyUnited States, Canada
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Children's National Research InstituteActive, not recruitingGenetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Dystrophies | Cardiac FibrosisUnited States
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Escuela NeijingCompletedAge-related Macular Degeneration | Stargardt Disease | Macular DystrophyColombia
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CENTOGENE GmbH RostockCompletedScoliosis | Muscular Atrophy | Duchenne Muscular Dystrophy | Lordosis | Muscular Weakness | Increased Lordosis/Scoliosis | Hyporeflexia | Red-Green Color BlindnessEgypt, India, Albania, Pakistan, Georgia, Lebanon, Romania, Sri Lanka
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PTC TherapeuticsTerminatedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Germany, Brazil, Bulgaria, Chile, Czechia, Poland, Sweden, Switzerland, Turkey
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Brazil, Chile, Czechia, Sweden, Switzerland, Turkey, Germany, Poland
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Foundation Fighting BlindnessRecruitingRetinitis Pigmentosa | Choroideremia | Usher Syndrome | Batten Disease | Leber Congenital Amaurosis | Goldmann-Favre Syndrome | Kearns-Sayre Syndrome | Retinal Disease | Bardet-Biedl Syndrome | Stargardt Disease | Cone Dystrophy | Retinoschisis | Achromatopsia | Gyrate Atrophy | Eye Diseases Hereditary | Bassen-Kornzweig... and other conditionsUnited States