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Clinical Trials on Ryanodine Receptor 1-Related Myopathy in United States
Total 1656 results
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National Institute of Nursing Research (NINR)Not yet recruitingRyanodine Receptor 1-Related Myopathy | Ryanodine Receptor 1 Related DisordersUnited States
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Armgo Pharma, Inc.National Institute of Nursing Research (NINR); National Institute of Neurological... and other collaboratorsCompletedRYR-1 MyopathyUnited States
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Newcastle-upon-Tyne Hospitals NHS TrustRecruitingX-linked Myotubular Myopathy | Centronuclear Myopathy | Myotubular Myopathy | Myotubular Myopathy 1 | Myotubular (Centronuclear) Myopathy | Centronuclear Myopathy, X-LinkedUnited Kingdom
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Myotonic Dystrophy FoundationRecruitingMyotonic Dystrophy | Myotonic Dystrophy 1 | Steinert's Disease | Congenital Myotonic Dystrophy | PROMM (Proximal Myotonic Myopathy) | Steinert Disease | Dystrophia Myotonica 1 | Myotonic Dystrophy 2 | Dystrophia Myotonica | Dystrophia Myotonica 2 | Myotonia Dystrophica | Myotonic Dystrophy, Congenital | Myotonic... and other conditionsUnited States
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National Institute of Arthritis and Musculoskeletal...National Institutes of Health Clinical Center (CC)Completed
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Newcastle-upon-Tyne Hospitals NHS TrustRecruitingBethlem Myopathy | Ullrich Congenital Muscular Dystrophy 1, Digenic, Col6A1/Col6A2 | Ullrich Congenital Muscular Dystrophy 1, Autosomal Recessive | Ullrich Congenital Muscular Dystrophy 1, Autosomal Dominant | Bethlem Myopathy 1, Autosomal Recessive | UCMD | BTHLM1United Kingdom
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Mayo ClinicCompletedStroke | Immobilization | Myofacial Pain | Hyperthyroid MyopathyUnited States
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National Human Genome Research Institute (NHGRI)Therapeutics for Rare and Neglected Diseases (TRND)RecruitingGNE Myopathy | GNE Related DiseasesUnited States
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AstraZenecaCompletedAdvanced Solid Tumours With Androgen Receptor Pathway as a Potential FactorUnited Kingdom, United States
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMuscular Dystrophy | Myotonic Dystrophy Type 2 | Myotonic Dystrophy Type 1 | Myotonic Dystrophy | Facioscapulohumeral Muscular Dystrophy | Steinert's Disease | Congenital Myotonic Dystrophy | PROMM (Proximal Myotonic Myopathy) | Myotonic Muscular DystrophyUnited States
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Rhythm Pharmaceuticals, Inc.CompletedPro-opiomelanocortin (POMC), Proprotein Convertase Subtilisin/Kexin Type 1 (PCSK1) and Leptin Receptor (LepR) Gene MutationsUnited States, Israel, Canada, Germany, Greece, Italy, Portugal
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National Cancer Institute (NCI)Active, not recruitingHormone Receptor-Positive Breast | Gynecologic | Desmoid | Hormone Receptor-Positive NeoplasmsUnited States
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Eledon PharmaceuticalsWithdrawnBrittle Type 1 Diabetes MellitusUnited States
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Eddii, Inc.Completed
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NYU Langone HealthNational Heart, Lung, and Blood Institute (NHLBI)Recruiting
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Boston Children's HospitalCompletedType 1 Diabetes MellitusUnited States
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Vanderbilt University Medical CenterCompletedType 1 Diabetes MellitusUnited States
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Joslin Diabetes CenterNovo Nordisk A/STerminatedType 1 Diabetes MellitusUnited States
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Legacy Health SystemJuvenile Diabetes Research FoundationCompleted
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Vanderbilt University Medical CenterUniversity of ConnecticutCompletedType 1 Diabetes MellitusUnited States
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Massachusetts General HospitalBoston UniversityTerminatedType 1 Diabetes MellitusUnited States
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University of FloridaJuvenile Diabetes Research Foundation; National Institutes of Health (NIH)Completed
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Jaeb Center for Health ResearchThe Leona M. and Harry B. Helmsley Charitable Trust; Indiana University School...CompletedType 1 Diabetes MellitusUnited States
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Oregon Health and Science UniversityCompleted
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Boston Children's HospitalCompletedType 1 Diabetes MellitusUnited States
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Boston Children's HospitalCompleted
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Legacy Health SystemJuvenile Diabetes Research FoundationCompletedType 1 Diabetes MellitusUnited States
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University of Colorado, DenverThe Leona M. and Harry B. Helmsley Charitable Trust; Nova Immunotherapeutics...RecruitingType 1 Diabetes MellitusUnited States
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Sue BrownDexCom, Inc.; Roche Diagnostics GmbHTerminatedType 1 Diabetes MellitusUnited States
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University of Illinois at ChicagoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Loyola...CompletedType 1 Diabetes MellitusUnited States
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National Institute of Diabetes and Digestive and...CompletedDiabetes Mellitus Type 1United States
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University of Texas Southwestern Medical CenterUniversity of Massachusetts, WorcesterCompleted
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University of VirginiaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); DexCom... and other collaboratorsCompletedType 1 Diabetes MellitusUnited States
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Sansum Diabetes Research InstituteUniversity of Virginia; University of California, Santa BarbaraCompleted
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University of Colorado, DenverNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)CompletedType 1 Diabetes MellitusUnited States
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Medical College of WisconsinCompletedType 1 Diabetes MellitusUnited States
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University of VirginiaDexCom, Inc.CompletedType 1 Diabetes MellitusUnited States
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Nemours Children's ClinicCompletedType 1 Diabetes MellitusUnited States
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Massachusetts General HospitalTerminatedType 1 Diabetes MellitusUnited States
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Oregon Health and Science UniversityCompleted
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Montefiore Medical CenterCompleted
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University of MinnesotaJuvenile Diabetes Research FoundationTerminatedHypoglycemia | Type 1 Diabetes MellitusUnited States
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Creighton UniversityCompletedType 1 Diabetes, | BoneUnited States
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Emory UniversityThrasher Research FundCompleted
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National Institute of Diabetes and Digestive and...CompletedAdolescent Type 1 DiabetesUnited States
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Yale UniversityCompletedType 1 Diabetes MellitusUnited States
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Sansum Diabetes Research InstituteUniversity of California, Santa BarbaraCompletedType 1 Diabetes MellitusUnited States
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Halozyme TherapeuticsCompletedType 1 Diabetes MellitusUnited States
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University of FloridaNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Recruiting
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University of VirginiaTerminated