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Clinical Trials on Sanfilippo Disease Type A
Total 57717 results
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Bioverativ Therapeutics Inc.Swedish Orphan BiovitrumCompletedSevere Hemophilia AUnited States, Australia, New Zealand
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BayerTerminatedHemophilia A and BAustralia, United Kingdom, Taiwan, Japan, Korea, Republic of, Austria, Bulgaria, Hungary, Italy, France, New Zealand
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OctapharmaCompletedSevere Hemophilia AUnited States, Bulgaria
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PfizerCompletedHemophilia A or BUnited States, Chile, Croatia, Poland, South Africa, Switzerland
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Margaret RagniWithdrawn
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Beijing Children's HospitalUnknownHemophilia A With InhibitorChina
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Hampshire Hospitals NHS Foundation TrustUppsala University; University of Wales Cardiff United Kingdom (UK)CompletedSevere Haemophilia AUnited Kingdom
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Skane University HospitalCompleted
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Joanne Kurtzberg, MDThe Marcus FoundationRecruitingMucopolysaccharidosis II | Brain Diseases, Metabolic, Inborn | Adrenoleukodystrophy | Batten Disease | Leukodystrophy, Metachromatic | Leukodystrophy, Globoid Cell | Alpha-Mannosidosis | Tay-Sachs Disease | Pelizaeus-Merzbacher Disease | Sandhoff Disease | Neimann Pick Disease | Sanfilippo MucopolysaccharidosesUnited States
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Leiden University Medical CenterAndaluz Health ServiceCompletedDiabetes Mellitus | Health Behavior | Self Efficacy | Type2 Diabetes Mellitus | Type1 Diabetes MellitusNetherlands, Spain
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University Hospital, MontpellierCompletedResident of Languedoc-roussillon | Carrying a Chronic WoundFrance
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Novartis PharmaceuticalsActive, not recruitingCardiovascular Disease and Lipoprotein(a)China, Germany, United States, South Africa, Italy, Spain, Belgium, Czechia, Hungary, Japan, Taiwan, Netherlands, Australia, Austria, Canada, France, Israel, Switzerland, United Kingdom, Korea, Republic of, Argentina, Denmark, Greece, Romani... and more
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Tri-Service General HospitalRecruitingSevere Hemophilia A Without InhibitorTaiwan
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Institute of Hematology & Blood Diseases HospitalRecruiting
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Groupe Maladies hémorragiques de BretagneRecruitingDesmopressin | Hemophilia A, Mild | Factor VIIIFrance
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University of WashingtonGenentech, Inc.Recruiting
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Novo Nordisk A/SEnrolling by invitationHaemophilia AAustria, Spain, Bulgaria, Croatia, Estonia, Hungary, Italy, Lithuania, Portugal, Greece, Germany, Czechia, Slovenia, Switzerland, Slovakia
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Chulalongkorn UniversityCompletedSevere Hemophilia A Without InhibitorThailand
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Baxalta now part of ShireNo longer available
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The Hospital for Sick ChildrenUnity Health Toronto; Nationwide Children's Hospital; Canadian Hemophilia SocietyUnknown
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BayerCompletedVasomotor Symptoms as a Sex Hormone-dependent Disorder in Women and MenGermany
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University of NottinghamUnknownOld Age (Focus; Not a Recognized Condition)United Kingdom
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Assistance Publique Hopitaux De MarseilleCompletedPatient With Breast CancerFrance
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University of ValenciaBaxter Healthcare CorporationCompletedHemophilia A, CongenitalSpain
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Fondazione I.R.C.C.S. Istituto Neurologico Carlo...Not yet recruitingPatients With Radiological, Clinical and Anamnestic Picture Compatible With a New Diagnosis of Glioblastoma
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Novartis PharmaceuticalsRecruitingHyperlipoproteinemia (a)Germany
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Novo Nordisk A/SRecruitingHaemophilia A With or Without InhibitorsKorea, Republic of, India, China, Canada, Spain, Netherlands, South Africa, United States, Israel, Japan, Poland, United Kingdom, Italy, Lithuania, Portugal, Switzerland, Taiwan
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Zhang Lei, MDHenan Cancer Hospital; Qilu Hospital of Shandong University; Tianjin First Central... and other collaboratorsCompletedAcquired Hemophilia AChina
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Baxalta now part of ShireBaxalta Innovations GmbH, now part of ShireCompletedHemophilia A or B With InhibitorsCroatia, North Macedonia, Ukraine
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AryoGen Pharmed Co.CompletedHemophilia A or B With InhibitorIran, Islamic Republic of, Turkey
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Grifols Italia S.p.AThrombinoscopeUnknownSevere Hemophilia A With InhibitorItaly
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Merck Sharp & Dohme LLCCompleted
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Novo Nordisk A/SCompletedEpidemiological Study on Haemophilia Care and Orthopaedic Status in Developing Countries (HAEMOcare)Congenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia BIndia, Morocco, South Africa, Oman
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia BSpain
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UPECLIN HC FM Botucatu UnespCompletedHepatitis, Viral, Non-A, Non-B, Parenterally-TransmittedBrazil
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North-West University, South AfricaMedical Research Council, South Africa; National Research Foundation of South... and other collaboratorsCompletedMalnutrition | Vitamin A Status | Iron Status | Zinc StatusSouth Africa
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Baxalta now part of ShireBaxalta Innovations GmbH, now part of ShireCompletedAcquired Hemophilia AUnited States, Italy, United Kingdom, Germany, Austria, Netherlands, France
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Baxalta now part of ShireCompletedAcquired Hemophilia AUnited States, Canada, India, United Kingdom
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OPKO Health, Inc.CompletedHemophilia A or B With InhibitorsIsrael
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Peking Union Medical College HospitalUnknownAcquired Hemophilia AChina
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Georgetown UniversityGenentech, Inc.Terminated
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Hospital Universitario La PazUnknownSevere Haemophilia A With InhibitorsSpain
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Recoly N.V.CompletedHaemophilia ARussian Federation
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Skane University HospitalCompleted
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Evidation HealthUniversity of Washington; Biomedical Advanced Research and Development Authority and other collaboratorsCompletedRespiratory Tract Infections | Influenza A | Influenza Type B | Respiratory Viral Infection | Influenza -Like IllnessUnited States
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Nantes University HospitalRecruiting
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Novo Nordisk A/SWithdrawnHealthy | Congenital Bleeding Disorder | Haemophilia A With Inhibitors | Haemophilia B With Inhibitors | Haemophilia A | Haemophilia B
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Novo Nordisk A/SRecruitingHaemophilia A and B With and Without InhibitorsUnited States, Spain, Italy, Estonia, Thailand, Canada, India, Malaysia, United Kingdom, Turkey, South Africa, Lebanon, Bosnia and Herzegovina, Bulgaria, France, Greece, Japan, Lithuania, Norway, Poland, Romania, Russian Federation, Swede... and more