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Clinical Trials on Single-Gene Defects in South Africa
Total 316 results
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PfizerCompletedOcular Hypertension | Glaucoma | Open Angle GlaucomaUnited States
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ShireTakeda Development Center Americas, Inc.Completed
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bluebird bioEnrolling by invitationSickle Cell DiseaseUnited States, France
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Othera PharmaceuticalsCompletedOcular Hypertension | Glaucoma, Open-AngleUnited States
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SunovionCompleted
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Imara, Inc.TerminatedSickle Cell DiseaseUnited States, Oman, Italy, United Kingdom, Lebanon, Greece, Morocco, Tunisia, Ghana, Kenya, Netherlands, Senegal, Uganda
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AstraZenecaCompletedSickle Cell DiseaseUnited States, Italy, France, United Kingdom, Turkey, Egypt, Lebanon, Kenya
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University of PittsburghNational Heart, Lung, and Blood Institute (NHLBI); Boston Children's HospitalEnrolling by invitation
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AbbVieRecruitingOcular Hypertension | Open-angle GlaucomaUnited States, Japan
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHematologic Diseases | Anemia, Sickle CellUnited States
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Universitas SriwijayaActive, not recruitingCapecitabine | Hand and Foot Syndrome | Hand and Foot Skin ReactionIndonesia
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BrainswayCompletedMajor Depressive Disorder, Recurrent, Unspecified | Major Depressive Disorder, Single Episode, UnspecifiedUnited States, Canada, Germany, Israel
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AllerganCompletedGlaucoma | Open-Angle Ocular HypertensionSpain, United States, Singapore, Australia, Denmark, France, Poland, Russian Federation, Thailand
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AbbVieEnrolling by invitationOcular Hypertension | Open-Angle GlaucomaUnited States, Argentina, Belgium, Brazil, Canada, Colombia, Czechia, Denmark, Egypt, France, Germany, Hong Kong, Italy, Korea, Republic of, New Zealand, Peru, Philippines, Poland, Russian Federation, Singapore, South Africa, Spain, Thailan... and more
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Vifor (International) Inc.FortreaCompletedSickle Cell DiseaseUnited States, France, Greece, Lebanon, United Kingdom
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Santen Inc.Completed
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Aerie PharmaceuticalsCompletedPrimary Open Angle Glaucoma or Ocular HypertensionUnited States
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AbbVie (prior sponsor, Abbott)CompletedCognitive Deficits in SchizophreniaUnited States
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Dynavax Technologies CorporationCompletedHerpes Zoster | Vaccine-Preventable Diseases | ShinglesAustralia
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ApoPharmaTerminatedIron Overload | Sickle Cell Disease | Other AnemiasUnited States, United Kingdom, Egypt, Canada, Saudi Arabia
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Sound Pharmaceuticals, IncorporatedMedical University of South Carolina; Cystic Fibrosis FoundationEnrolling by invitation
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Sheffield Teaching Hospitals NHS Foundation TrustUniversity of SheffieldCompleted
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ShireCompletedBinge Eating DisorderUnited States
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ShireCompletedBinge Eating DisorderSpain, United States, Germany
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Turning Point Therapeutics, Inc.TerminatedNon-Small Cell Lung Cancer | NSCLC | Non Small Cell Lung Cancer | Advanced Solid Tumor | Metastatic Solid Tumor | ALK Gene MutationUnited States, Australia, Korea, Republic of
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Mark GladwinCompletedSickle Cell DiseaseUnited States
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Carelon ResearchTerminatedCongenital Heart Disease | Hypoplastic Left HeartUnited States, Canada
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Medical College of WisconsinNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsCompletedSickle Cell DiseaseUnited States
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Avera McKennan Hospital & University Health CenterTerminatedBreast Cancer | Breast TumorsUnited States
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Editas Medicine, Inc.RecruitingSickle Cell Disease | HemoglobinopathiesUnited States, Canada
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ActelionCompletedClinical Study Assessing the Efficacy and Safety of Macitentan in Fontan-palliated Subjects (RUBATO)Congenital Heart DiseaseUnited States, United Kingdom, Taiwan, Germany, France, Poland, China, Australia, Czechia, Canada, Denmark, New Zealand
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Sydney Local Health DistrictEnrolling by invitationClass III Malocclusion | UnderbiteAustralia
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Zynerba Pharmaceuticals, Inc.Completed22Q Deletion SyndromeUnited States, Australia
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PfizerPfizerRecruitingSickle Cell DiseaseUnited States
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Brigham and Women's HospitalUniversity of Chicago; University of Wisconsin, Madison; University of California... and other collaboratorsCompletedMedication Administered in Error | Adverse Drug EventsUnited States
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CephalonTerminatedFatigue | Chemotherapy Side EffectsUnited States
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University of MichiganMedical University of South Carolina; Emory University; Medical College of Wisconsin and other collaboratorsCompletedCongenital Heart Disease | Hypoplastic Left Heart Syndrome | Hypoplastic Right Heart Syndrome | d-Transposition of the Great ArteriesUnited States, Australia
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Abbott Medical DevicesCompleted
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ShireCompletedBinge Eating DisorderUnited States, Spain, Germany, Sweden
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PfizerTerminatedDilated Cardiomyopathy | Lamin A/C Gene MutationUnited States, Spain, Canada, Belgium, Italy, Argentina, Mexico, Netherlands, Norway, United Kingdom
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Carl Backes, MDChildren's Hospital of Philadelphia; National Heart, Lung, and Blood Institute... and other collaboratorsRecruitingCongenital Heart Disease (CHD)United States, Canada
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Medical College of WisconsinNational Heart, Lung, and Blood Institute (NHLBI); Dana-Farber Cancer Institute and other collaboratorsCompletedSickle Cell DiseaseUnited States
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PfizerPfizerAvailableSickle Cell DiseaseUnited States, Brazil
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Tenaya TherapeuticsMedical University of South Carolina; Johns Hopkins University; University of... and other collaboratorsRecruitingArrhythmogenic Right Ventricular CardiomyopathyUnited States, Italy, United Kingdom, France, Sweden, Germany
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ISTO Technologies, Inc.TerminatedDefect of Articular Cartilage | Articular Cartilage Disorder | Degeneration; Articular Cartilage | Chronic Cartilage Injury | Acute Cartilage InjuryUnited States
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ASH Research CollaborativeUniversity of Pennsylvania; American Society of HematologyActive, not recruiting
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Novartis PharmaceuticalsCompleted
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Novartis PharmaceuticalsRecruitingSickle Cell Disease (SCD)United States, Germany, Spain, Belgium, Italy, Lebanon, Brazil, Colombia, Oman, Switzerland, Turkey, United Kingdom, Canada, India, France
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Kevin WinthropMedical University of South Carolina; Mayo Clinic; University of Washington; National... and other collaboratorsNot yet recruitingOtotoxicity, Drug-InducedUnited States
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PfizerActive, not recruitingSickle Cell DiseaseUnited States, Oman, United Kingdom, France, Egypt, Ghana, Italy, Kenya, Nigeria, Saudi Arabia