- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Single-Gene Defects in United States
Total 3350 results
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SanofiBristol-Myers SquibbCompletedBlood Platelet Disorders | Congenital Heart DefectsUnited States, France, Canada, Germany, Italy, Belgium
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Mclean HospitalNational Institute on Drug Abuse (NIDA)UnknownPsychotropic Drugs EffectsUnited States
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Day One Biopharmaceuticals, Inc.RecruitingMelanoma | Colorectal Cancer | Solid Tumor | Non Small Cell Lung Cancer | Bladder Cancer | Thyroid Cancer, Papillary | Pilocytic Astrocytoma | Bladder Urothelial Carcinoma | Non-Small Cell Adenocarcinoma | MEK Mutation | RAS Mutation | Pancreatic Acinar Carcinoma | RAF Mutation | CRAF Gene Amplification | RAF1 Gene Amplification and other conditionsUnited States, Canada, Korea, Republic of, Spain, Australia, Belgium, France
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Joanne JeterNational Cancer Institute (NCI)Active, not recruitingLynch Syndrome | Colon Adenoma | Colon Carcinoma | MLH1 Gene Mutation | MSH2 Gene MutationUnited States
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University of MinnesotaWyeth is now a wholly owned subsidiary of Pfizer; Roche Pharma AG; Genzyme, a...CompletedCNI Side EffectsUnited States
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University of PennsylvaniaCompleted
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University of California, San FranciscoTakeda; Array BioPharmaTerminatedProgressive Disease | Stage IV Lung Cancer | Lung Non-Small Cell Carcinoma | ROS1 Gene Rearrangement | ALK Gene Rearrangement | Stage IIIB Lung Cancer | Stage IIIC Lung Cancer | Stage IVA Lung Cancer | Stage IVB Lung CancerUnited States
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Wills EyeCompleted
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Perfuse Therapeutics, Inc.Recruiting
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AllerganCompletedOcular Hypertension | Open-angle GlaucomaUnited States
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Spark TherapeuticsCompletedChoroideremia | CHM (Choroideremia) Gene MutationsUnited States
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The University of Texas Health Science Center at...Institut Straumann AGCompletedJaw, Edentulous, Partially | Acquired Absence of Single ToothUnited States
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Columbia UniversityRecruitingPrimary Open Angle GlaucomaUnited States
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University of MiamiNot yet recruitingObstructive Sleep Apnea | Patent Foramen OvaleUnited States
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Washington University School of MedicineCompleted
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Baxter Healthcare CorporationCompletedDura Defects | Pathological Processes in the Posterior FossaUnited States, Canada
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Duke UniversityRecruitingVisual Field Defect, PeripheralUnited States
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Ocular Therapeutix, Inc.CompletedOpen Angle Glaucoma and Ocular HypertensionUnited States
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Histogenics CorporationTerminatedArticular Cartilage Defects in the Knee JointUnited States, Canada
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The University of Texas Health Science Center at...ITI International Team for Implantology, SwitzerlandCompletedJaw, Edentulous, Partially | Acquired Absence of Single ToothUnited States
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University of PennsylvaniaTerminated
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Tyra Biosciences, IncRecruitingSolid Tumor | Intrahepatic Cholangiocarcinoma | Metastatic Cholangiocarcinoma | Locally Advanced CholangiocarcinomaUnited States
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Noveome Biotherapeutics, formerly StemnionCompletedPersistent Corneal Epithelial DefectUnited States
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University of California, Los AngelesNational Eye Institute (NEI)Active, not recruitingPrimary Open Angle Glaucoma | Chronic Angle Closure Glaucoma | Pseudoexfoliative GlaucomaUnited States
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CochlearCompletedSingle Sided DeafnessUnited States
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NRG OncologyNational Cancer Institute (NCI)Active, not recruitingGlioma | Oligoastrocytoma | Anaplastic Astrocytoma | Oligodendroglioma | Diffuse Astrocytoma | WHO Grade III Glioma | IDH2 Gene Mutation | IDH1 Gene Mutation | 1p/19q Co-deletionUnited States
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HemoSonics LLCCompleted
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Imara, Inc.Quintiles, Inc.CompletedSickle Cell Disease | Sickle Beta 0 Thalassemia | Sickle-Cell; Hb-SCUnited States
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SanofiBristol-Myers SquibbCompletedHeart Defects, CongenitalFrance, Canada, Brazil, Poland, Russian Federation, Germany, Italy, Netherlands, Portugal, Spain, Sweden, India, Malaysia, Singapore, Taiwan, Belgium, Mexico, Argentina, Denmark, Egypt, Finland, Hungary, Israel, Norway, Korea, Republic of, Hong Kong and more
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Qlaris Bio, Inc.RecruitingPrimary Open Angle Glaucoma of Both Eyes | Primary Open Angle Glaucoma (POAG) | Primary Open-Angle Glaucoma, Unspecified Eye | Ocular Hypertension (OHT)United States
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Annexon, Inc.CompletedOpen-angle GlaucomaUnited States
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Alcon ResearchTerminatedOcular Hypertension | Open-angle GlaucomaUnited States
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Alcon ResearchCompletedOcular Hypertension | Open-Angle GlaucomaUnited States
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Alcon ResearchCompletedOpen-angle GlaucomaUnited States
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University of Alabama at BirminghamNational Institute on Aging (NIA)Active, not recruiting
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Wills EyeCompletedPrimary Open-angle GlaucomaUnited States
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Glaukos CorporationCompletedGlaucoma Open-angleUnited States
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State University of New York at BuffaloCompletedDental Malocclusion | Crowding, Tooth | Angle Class II | Angle Class IUnited States
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Temple UniversityEli Lilly and CompanyWithdrawnCancer | Cognitive Late EffectsUnited States
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Daiichi Sankyo, Inc.CompletedFood Effects on PharmacokineticsUnited States
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Mclean HospitalTerminatedAOD Effects and ConsequencesUnited States
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Jazz PharmaceuticalsRecruitingBiliary Tract Cancer | HER2 Gene MutationUnited States, Puerto Rico
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University of South FloridaBoston Children's HospitalCompletedPTEN Gene MutationUnited States
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Institute of Child HealthCompletedRecurrent Neural Tube DefectsUnited Kingdom
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W.L.Gore & AssociatesActive, not recruitingHeart Defects, Congenital | Tetralogy of Fallot | Pulmonary Valve Insufficiency | Pulmonary Valve StenosisUnited States
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Glaukos CorporationCompletedPrimary Open-angle GlaucomaUnited States
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Alcon ResearchCompletedOcular Hypertension | Open-angle GlaucomaUnited States
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Alcon ResearchCompletedOcular Hypertension | Open-Angle GlaucomaUnited States
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Pharmaceutical Research NetworkCompleted