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Clinical Trials on Spastic Paraplegia, Hereditary
Total 3537 results
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National Taiwan University HospitalCompleted
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Masonic Cancer Center, University of MinnesotaWithdrawn
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Ascend Biopharmaceuticals LtdCompletedBasal Cell Nevus Syndrome | Skin Neoplasm | Nodular Basal Cell Carcinoma of SkinAustralia
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University of MinnesotaNo longer availableX-linked AdrenoleukodystrophyUnited States
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New York Medical CollegeTerminatedSarcoma | Neuroblastoma | Wilms' Tumor | Refractory Solid Tumor | Recurrent Solid TumorUnited States
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MedDay Pharmaceuticals SACompletedAdrenoleukodystrophy | Adrenomyeloneuropathy | AMNFrance, Germany, Spain
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University of Sao PauloUnknownFamilial Adenomatous PolyposisBrazil
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Novartis PharmaceuticalsCompletedTreatment for Basal Cell Carcinomas (BCCs) in Gorlin Syndrome PatientsAustria, Switzerland
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Children's Hospital Medical Center, CincinnatiNovartisCompletedTuberous Sclerosis | Subependymal Giant Cell AstrocytomaUnited States
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Eunice Kennedy Shriver National Institute of Child...Food and Drug Administration (FDA)TerminatedAdrenoleukodystrophy | AdrenomyeloneuropathyUnited States
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Academisch Medisch Centrum - Universiteit van Amsterdam...The Stop ALD FoundationCompletedAdrenomyeloneuropathy | X-linked AdrenoleukodystrophyNetherlands
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Hospital Infantil Universitario Niño Jesús, Madrid...Universitat Autonoma de Barcelona; Instituto de Investigación Sanitaria de... and other collaboratorsCompletedFanconi AnemiaSpain
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Cystinosis Research FoundationUnknownCystinosis | Nephropathic Cystinosis | Renal Fanconi SyndromeUnited States
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The Emmes Company, LLCNational Heart, Lung, and Blood Institute (NHLBI)TerminatedStudy of Parathyroid Hormone Following Sequential Cord Blood Transplantation From an Unrelated DonorLymphoma | Hodgkin Disease | Myelofibrosis | Anemia, Aplastic | Leukemia, Lymphocytic, Acute | Leukemia, Myelocytic, Acute | Leukemia, Myeloid, Chronic | Leukemia, Lymphocytic, ChronicUnited States
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Seattle Children's HospitalActive, not recruitingMelanoma | Soft Tissue Sarcoma | Carcinoma | Osteosarcoma | Ewing Sarcoma | Rhabdoid Tumor | Neuroblastoma | Retinoblastoma | Rhabdomyosarcoma | Wilms Tumor | Hepatoblastoma | Synovial Sarcoma | Desmoplastic Small Round Cell Tumor | Germ Cell Tumor | Pediatric Solid Tumor | Clear Cell Sarcoma | Malignant Peripheral Nerve Sheath...United States
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Rolfs Consulting und Verwaltungs-GmbH (RCV)Rhythm Pharmaceuticals, Inc.RecruitingCognitive Impairment | Hyperphagia | Obesity, Childhood | Bardet-Biedl Syndrome | Polydactyly | Retinopathy | Syndactyly | POMC DeficiencyGermany
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Masonic Cancer Center, University of MinnesotaRecruiting
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Assiut UniversityRecruitingBehcet's Disease With Multisystem InvolvementEgypt
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Assistance Publique - Hôpitaux de ParisBraintaleNot yet recruitingX-linked Adrenoleukodystrophy
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Minoryx Therapeutics, S.L.RecruitingCerebral Adrenoleukodystrophy (cALD)United States, Brazil, Argentina
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Poxel SANot yet recruiting
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West China HospitalRecruitingSarcoma | Lymphoma | Neuroblastoma | Wilms' Tumor | Teratoma | Germ Cell TumorChina
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Academisch Medisch Centrum - Universiteit van Amsterdam...IRCCS Azienda Ospedaliero-Universitaria di Bologna; Hospital Clinic of Barcelona and other collaboratorsRecruitingFamilial Adenomatous PolyposisNetherlands
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Children's Oncology GroupNational Cancer Institute (NCI)RecruitingStage II Kidney Wilms Tumor | Stage III Kidney Wilms Tumor | Stage IV Kidney Wilms Tumor | Recurrent Kidney Wilms Tumor | Anaplastic Kidney Wilms TumorUnited States, Canada, Puerto Rico, Australia, New Zealand, Saudi Arabia
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National Cancer Institute (NCI)RecruitingNeurofibromatosis Type 1 | Low Grade Glioma | Visual Pathway GliomaUnited States, Canada, Puerto Rico
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Boston Children's HospitalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingIntellectual Disability | Tuberous Sclerosis | Autism DisorderUnited States
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, France, Germany, Italy, Netherlands, United Kingdom
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S.L.A. Pharma AGActive, not recruitingFamilial Adenomatous PolyposisItaly
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Vanderbilt UniversityNational Institute of Neurological Disorders and Stroke (NINDS)CompletedNeurofibromatosis Type 1 | Reading DisabilitiesUnited States
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University Hospital, ToursCompletedTuberous Sclerosis Complex | LymphangioleiomyomatosisFrance
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Rapamycin Holdings, Inc. dba Emtora BiosciencesLumaBridgeActive, not recruitingFamilial Adenomatous PolyposisUnited States
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Talaris Therapeutics Inc.Duke UniversityNo longer availableMetachromatic LeukodystrophyUnited States
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Stanford UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Hugo W. Moser... and other collaboratorsCompletedX-linked AdrenoleukodystrophyUnited States
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, Germany, Argentina, Australia, France, United Kingdom
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University of Puerto RicoNational Institutes of Health (NIH)CompletedFamilial Adenomatous PolyposisPuerto Rico
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Vanderbilt-Ingram Cancer CenterNational Cancer Institute (NCI)TerminatedFamilial Adenomatous Polyposis | Deep Fibromatosis/Desmoid TumorUnited States
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Shenzhen Geno-Immune Medical InstituteUnknown
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NeuroVia, Inc.WithdrawnX-Linked AdrenoleukodystrophyAustralia, Argentina, United Kingdom, Colombia, Chile, France, Russian Federation, Ukraine
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Academisch Medisch Centrum - Universiteit van Amsterdam...Completed
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Xinhua Hospital, Shanghai Jiao Tong University...UnknownLymphoma | Acute Myeloid Leukemia | Neuroblastoma | Retinoblastoma | Hepatoblastoma | Acute Lymphoid LeukemiaChina
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Rabin Medical CenterUnknown
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NYU Langone HealthWithdrawnEpilepsy | Tuberous Sclerosis | Dravet Syndrome | Focal Seizures | Lennox-Gastaut SyndromeUnited States
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Nantes University HospitalUniversité de NantesUnknownChronic Inflammatory Demyelinating Polyneuropathy | Anti-MAG Neuropathy | Charcot-Marie-Tooth Disease, Type IAFrance
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Masonic Cancer Center, University of MinnesotaWithdrawnCerebral Adrenoleukodystrophy
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National Cancer Institute (NCI)CompletedFamilial Adenomatous PolyposisUnited States, Puerto Rico
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Washington University School of MedicineCompletedNeurofibromatosis Type 1 | Pediatric Brain TumorUnited States
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The Cleveland ClinicOhio State University Comprehensive Cancer CenterCompletedFamilial Adenomatous PolyposisUnited States
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University Hospital, ToulouseCompleted
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FDA Office of Orphan Products DevelopmentHugo W. Moser Research Institute at Kennedy Krieger, Inc.Completed
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The University of Texas Health Science Center,...Society for Pediatric DermatologyCompletedTuberous Sclerosis | Neurofibromatoses | Neurofibroma | AngiofibromaUnited States