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Clinical Trials on Sphingolipidoses in France
Total 81 results
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LYSOGENETerminatedGM1 GangliosidosisUnited Kingdom, United States, France
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Assistance Publique - Hôpitaux de ParisCompletedGaucher DiseaseFrance
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SanofiCompletedGaucher Disease | SplenomegalyFrance
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University Hospital, Clermont-FerrandUnknown
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CEN BiotechTakeda; BioClinica, Inc.Completed
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Nantes University HospitalCompletedPatients With Gaucher's DiseaseFrance
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Groupe Hospitalier Diaconesses Croix Saint-SimonTerminated
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Assistance Publique - Hôpitaux de ParisShire; Zymenex A/S; European Leukodystrophy AssociationCompletedMetachromatic LeukodystrophyFrance
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Assistance Publique - Hôpitaux de ParisUnknown
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University Hospital, RouenUnknownAnderson-Fabry DiseaseFrance
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University Hospital, BordeauxUnknown
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University Hospital, CaenUnknownCardiomyopathiesFrance
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SanofiRecruitingAcid Sphingomyelinase Deficiency (ASMD)France
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Institut National de la Santé Et de la Recherche...Assistance Publique - Hôpitaux de Paris; European Leukodystrophy AssociationActive, not recruitingMetachromatic LeukodystrophyFrance
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Rennes University HospitalCompleted
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Assistance Publique - Hôpitaux de ParisEuropean Leukodystrophy AssociationCompletedLate Infantile Metachromatic LeukodystrophyFrance
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University Hospital, AngersRecruiting
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Hospital St. Joseph, Marseille, FranceCompleted
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University Hospital, BordeauxCompletedPain | Fabry's DiseaseFrance
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ShireCompletedMetachromatic Leukodystrophy (MLD)Australia, Denmark, Japan, France, Germany
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Amicus TherapeuticsCompletedFabry DiseaseFrance, United Kingdom
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Centre Hospitalier Universitaire de NiceUnknown
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Assistance Publique - Hôpitaux de ParisShire International GmbHCompleted
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University Hospital, MontpellierRecruiting
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Hospices Civils de LyonUnknownEnd Stage Renal Disease | Fabry Disease | Renal DialysisFrance
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Amicus Therapeutics France SASCompleted
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ShireTakeda Development Center Americas, Inc.Active, not recruitingMetachromatic Leukodystrophy (MLD)Denmark, Germany, Japan, Australia, France, Brazil, Czechia
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseUnited States, France, Poland, United Kingdom
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University Hospital, GrenobleTerminatedPsychiatric Adults PatientsFrance
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Amicus Therapeutics France SASCompletedFabry Disease | Anderson Fabry DiseaseFrance
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Forge Biologics, IncRecruitingKrabbe DiseaseUnited States
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Genzyme, a Sanofi CompanyCompletedGaucher DiseaseUnited States, Sweden, India, Netherlands, Austria, Japan, China, Serbia, France, Croatia, Australia, Portugal, Canada, Brazil, Greece, Romania, Russian Federation
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Amicus TherapeuticsCompletedFabry DiseaseUnited States, Australia, France, United Kingdom, Brazil, Canada
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Assistance Publique - Hôpitaux de ParisRecruitingAdrenoleukodystrophy | Adrenomyeloneuropathy | Metachromatic Leukodystrophy | Adult-Onset Leukoencephalopathy With Axonal Spheroids and Pigmented GliaFrance
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Azafaros A.G.Active, not recruitingGM1 Gangliosidosis | Tay-Sachs Disease | Sandhoff DiseaseUnited States, Brazil, France, Germany, Italy, United Kingdom
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseFrance, Poland, United States, Russian Federation, United Kingdom
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University Hospital, BordeauxCompletedChronic Pain | Fabry's DiseaseFrance
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Genzyme, a Sanofi CompanyCompletedFabry DiseaseFrance, Poland, United States, Russian Federation, United Kingdom
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Amicus TherapeuticsTerminatedFabry DiseaseUnited Kingdom, United States, Australia, Brazil, France
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CENTOGENE GmbH RostockCompletedFabry Disease | Anderson-Fabry Disease | Fabry´s DiseaseArgentina, Belgium, Croatia, Czechia, Denmark, France, Germany, United Kingdom
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ActelionCompletedGaucher Disease Type 1United States, Taiwan, Canada, Spain, Australia, France, Brazil, Hungary, Czechia, Germany, Italy, Netherlands, United Kingdom
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Genzyme, a Sanofi CompanyActive, not recruitingTay-Sachs Disease | Sandhoff DiseaseUnited States, Argentina, Czechia, Portugal, Russian Federation, Turkey, United Kingdom, Brazil, France, Germany, Italy, Japan, Spain
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisBrazil, France, Italy, United States, Germany, United Kingdom
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AVROBIOTerminatedFabry DiseaseAustralia, Brazil
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CENTOGENE GmbH RostockShire Human Genetic Therapies, Inc.CompletedFabry Disease | Cerebrovascular AccidentAustria, Croatia, France, Germany, Poland, Portugal, Georgia
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SanofiRecruitingGaucher's Disease Type IIIUnited States, Germany, Hungary, France, China, Japan, Canada, Argentina, Italy, Turkey
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Amicus TherapeuticsApproved for marketingPhysician Initiated Expanded Access Request for Migalastat in Individual Patients With Fabry DiseaseFabry DiseaseUnited States, Australia
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1United States, France, Germany, Italy, Brazil, Australia, Argentina, Canada, Egypt, Russian Federation, Spain, United Kingdom
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Genzyme, a Sanofi CompanyCompletedSphingomyelin LipidosisUnited States, Belgium, Brazil, France, Germany, Italy, United Kingdom