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Clinical Trials on Spinal Muscular Atrophy 4 in United Kingdom
Total 1157 results
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Marco CapogrossoRoche-GenentechRecruitingSpinal Muscular Atrophy Type 3 | Spinal Muscular Atrophy Type 4United States
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Marco CapogrossoRoche-GenentechNot yet recruitingSpinal Muscular Atrophy | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy 4United States
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Great Ormond Street Hospital for Children NHS Foundation...RecruitingSpinal Muscular AtrophyUnited Kingdom
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Robert Jones and Agnes Hunt Orthopaedic and District...University Hospital Birmingham NHS Foundation TrustRecruitingSpinal Muscular AtrophyUnited Kingdom
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Great Ormond Street Hospital for Children NHS Foundation...CompletedSpinal Muscular AtrophyUnited Kingdom
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Newcastle UniversityRoche Pharma AG; Biogen; Adult SMA REACH; SMA REACH UKRecruiting
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University of OxfordHoffmann-La Roche; Oxford University Hospitals NHS Trust; Novartis Gene TherapiesRecruiting
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Hoffmann-La RocheAssociation Française contre les Myopathies (AFM), ParisCompletedSpinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type III Non AmbulantGermany, Italy, France, Belgium, Poland, Netherlands, United Kingdom
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Novartis Gene TherapiesCompletedSMAFrance, United Kingdom, Italy, Belgium
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Universidad Autonoma de MadridKing's College London; Centro Superior de Estudios Universitarios LasalleCompletedMuscle Atrophy | Intervertebral Disc Compression | Spine InjurySpain, United Kingdom
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Gillette Children's Specialty HealthcareUniversity of MinnesotaCompletedSpinal Muscular Dystrophy | Neuromuscular DisabilityUnited States
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University of NottinghamBiotechnology and Biological Sciences Research CouncilUnknownMuscular Atrophy | Immobility SyndromeUnited Kingdom
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University of ExeterCompleted
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Hoffmann-La RocheRecruitingSpinal Muscular Atrophy (SMA)Belgium, United States, Croatia, Japan, Netherlands, Spain, Canada, Poland, United Kingdom, Portugal, Italy, Australia
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Columbia UniversityMuscular Dystrophy Association; Stevens Institute of TechnologyCompletedDuchenne Muscular Dystrophy | Spinal Muscular Atrophy Type 3United States
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Novartis Gene TherapiesActive, not recruitingSMA | Spinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type I | Spinal Muscular Atrophy Type IIIUnited States, Belgium, France, Japan, United Kingdom, Italy, Taiwan, Australia, Canada
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University of BirminghamCompletedMuscle Disuse AtrophyUnited Kingdom
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Novartis PharmaceuticalsRecruitingSpinal Muscular Atrophy (SMA)Spain, Canada, Taiwan, Belgium, Japan, Italy, Singapore, United Kingdom, France, Australia, Denmark, United States
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Novartis Gene TherapiesPRA Health SciencesCompletedSpinal Muscular AtrophyUnited States, United Kingdom, Australia, Belgium, Canada, Japan
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Alcyone Therapeutics, IncBiogenRecruitingScoliosis | Spinal Muscular Atrophy | Spine DeformityUnited States
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Hoffmann-La RocheActive, not recruitingSpinal Muscular AtrophyBelgium, United States, United Kingdom, France, Poland, Italy, Switzerland, Netherlands, Germany
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Northwell HealthCompletedAdult Spinal Muscular AtrophyUnited States
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Hoffmann-La RocheTerminatedMuscular Atrophy, SpinalFrance, Turkey, Canada, United States, Italy, Netherlands, Sweden, Switzerland, United Kingdom
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University of BirminghamUniversity of Nottingham; Biotechnology and Biological Sciences Research CouncilCompletedSarcopenia | Muscle Loss | Prehabilitation | Disuse Atrophy | Protein MetabolismUnited Kingdom
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Scholar Rock, Inc.Active, not recruitingNeuromuscular Diseases | Neuromuscular Manifestations | Atrophy | Muscular Atrophy | Spinal Muscular Atrophy | Muscular Atrophy, Spinal | Spinal Muscular Atrophy Type 3 | SMA | Anti-myostatin | Spinal Muscular Atrophy Type IIUnited States, Spain, Belgium, Germany, Netherlands, Poland, Italy, France, United Kingdom
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalBelgium, United Kingdom, Germany, France, Italy, Netherlands, Poland
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Scholar Rock, Inc.Active, not recruitingNeuromuscular Diseases | Neuromuscular Manifestations | Atrophy | Muscular Atrophy | Spinal Muscular Atrophy | Muscular Atrophy, Spinal | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type 2 | Anti-myostatinUnited States, Germany, Belgium, Spain, United Kingdom, Netherlands, France, Italy, Poland
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Natera, Inc.WithdrawnGenetic Testing | Spinal Muscular Atrophy (SMA) | Carrier ScreeningUnited States
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Nationwide Children's HospitalNovartisActive, not recruitingSpinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type IUnited States
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WestatNational Institute of Neurological Disorders and Stroke (NINDS)TerminatedSpinal Muscular Atrophy Type II | Spinal Muscular Atrophy Type IIIUnited States
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Hoffmann-La RocheCompletedMuscular Atrophy, SpinalBelgium, United States, China, Spain, Japan, Canada, France, Poland, Brazil, Croatia, Italy, Russian Federation, Turkey, Germany, Serbia, United Kingdom
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BiogenActive, not recruitingSpinal Muscular AtrophyUnited States, Taiwan, Israel, Australia, Qatar, United Kingdom, Turkey, Italy, Germany, Argentina, Canada
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Washington University School of MedicineActive, not recruitingSpinal Muscular Atrophy | Spinal Muscular Atrophy Type 3 | Spinal Muscular Atrophy Type IIUnited States, Canada
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Columbia UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedSpinal Muscular Atrophy Type 3 | Mitochondrial MyopathyUnited States
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Ohio State UniversityMassachusetts General Hospital; National Institute of Neurological Disorders... and other collaboratorsCompletedSpinal Muscular Atrophy (SMA)United States
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Novartis Gene TherapiesCompletedGene Therapy | SMA - Spinal Muscular AtrophyUnited States
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Scholar Rock, Inc.CompletedNeuromuscular Diseases | Neuromuscular Manifestations | Atrophy | Muscular Atrophy | Spinal Muscular Atrophy | Muscular Atrophy, Spinal | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type 2United States, Spain, Italy, Netherlands
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BiogenTerminatedSpinal Muscular AtrophyKorea, Republic of, United States, Spain, Canada, Germany, Australia, Japan, Sweden, Belgium, France, Italy, Turkey, United Kingdom
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Novartis PharmaceuticalsCompletedSpinal Muscular AtrophyTaiwan, Belgium, Canada, United States, Australia, France, Italy, Portugal, United Kingdom
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Novartis Gene TherapiesActive, not recruitingSpinal Muscular Atrophy 1United States
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Novartis Gene TherapiesCompletedSpinal Muscular Atrophy 1United States
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Stanford UniversityCompletedMuscular Atrophy, SpinalUnited States
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BiogenCompletedSpinal Muscular AtrophyUnited States, Spain, Germany, United Kingdom, Australia, Japan, Canada, Belgium, France, Hong Kong, Italy, Korea, Republic of, Sweden, Turkey
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AveXis, Inc.United BioSource, LLCRecruitingSpinal Muscular Atrophy (SMA)Japan, United States, Korea, Republic of, Israel, Greece, Ireland, Portugal, Russian Federation, Taiwan
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Novartis PharmaceuticalsCompleted
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NYU Langone HealthWinthrop University HospitalWithdrawnSpinal Muscular AtrophyUnited States
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Hoffmann-La RocheCompletedSpinal Muscular AtrophyUnited States
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National Institute of Neurological Disorders and...Completed
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Columbia UniversityCompletedSpinal Muscular AtrophyUnited States
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Ohio State UniversityCure SMAActive, not recruitingSpinal Muscular AtrophyUnited States